Sotorasib resistance in KRAS G12C-mutant invasive mucinous adenocarcinoma with implications for VEGF-A

Abstract Invasive mucinous adenocarcinoma (IMA) is a rare subtype of lung adenocarcinoma with a poor prognosis. Compared to non-small cell lung cancer, IMA more frequently harbors KRAS mutations in the order p.G12V, p.G12D, and p.G12C. This report describes a patient with a KRAS p.G12C-mutant IMA tr...

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Main Authors: Hiraku Yanada, Ryohei Yoshida, Ryotaro Kida, Kiichi Nitanai, Maya Ikeda, Kazunori Nagasue, Taeka Naraoka, Masashi Ueda, Takashi Watanabe, Ryota Shigaki, Yasuhiro Umekage, Yoshinori Minami, Toshihiro Nagato, Manami Hayashi, Sayaka Yuzawa, Mishie Tanino, Takaaki Sasaki
Format: Article
Language:English
Published: Nature Portfolio 2025-05-01
Series:npj Precision Oncology
Online Access:https://doi.org/10.1038/s41698-025-00953-2
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author Hiraku Yanada
Ryohei Yoshida
Ryotaro Kida
Kiichi Nitanai
Maya Ikeda
Kazunori Nagasue
Taeka Naraoka
Masashi Ueda
Takashi Watanabe
Ryota Shigaki
Yasuhiro Umekage
Yoshinori Minami
Toshihiro Nagato
Manami Hayashi
Sayaka Yuzawa
Mishie Tanino
Takaaki Sasaki
author_facet Hiraku Yanada
Ryohei Yoshida
Ryotaro Kida
Kiichi Nitanai
Maya Ikeda
Kazunori Nagasue
Taeka Naraoka
Masashi Ueda
Takashi Watanabe
Ryota Shigaki
Yasuhiro Umekage
Yoshinori Minami
Toshihiro Nagato
Manami Hayashi
Sayaka Yuzawa
Mishie Tanino
Takaaki Sasaki
author_sort Hiraku Yanada
collection DOAJ
description Abstract Invasive mucinous adenocarcinoma (IMA) is a rare subtype of lung adenocarcinoma with a poor prognosis. Compared to non-small cell lung cancer, IMA more frequently harbors KRAS mutations in the order p.G12V, p.G12D, and p.G12C. This report describes a patient with a KRAS p.G12C-mutant IMA treated with sotorasib. To date, no studies have investigated the therapeutic efficacy or resistance mechanisms of sotorasib in IMA. The patient was treated with carboplatin and pemetrexed, followed by sotorasib upon disease progression. While the primary lung lesions responded well, metastatic thoracic lymph node lesions continued to increase. A pathological autopsy was performed with the family’s consent to investigate potential resistance mechanisms. RNA sequencing and additional analyses revealed increased VEGF-A expression in metastatic lymph node lesions, suggesting a role in sotorasib resistance. These findings provide insights into the potential molecular mechanisms underlying treatment resistance in KRAS p.G12C-mutant IMA.
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spelling doaj-art-d730aad7f527446c8ab6a6a8a81ab4e82025-08-20T02:39:04ZengNature Portfolionpj Precision Oncology2397-768X2025-05-01911610.1038/s41698-025-00953-2Sotorasib resistance in KRAS G12C-mutant invasive mucinous adenocarcinoma with implications for VEGF-AHiraku Yanada0Ryohei Yoshida1Ryotaro Kida2Kiichi Nitanai3Maya Ikeda4Kazunori Nagasue5Taeka Naraoka6Masashi Ueda7Takashi Watanabe8Ryota Shigaki9Yasuhiro Umekage10Yoshinori Minami11Toshihiro Nagato12Manami Hayashi13Sayaka Yuzawa14Mishie Tanino15Takaaki Sasaki16Department of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityDepartment of Pathology, Asahikawa Medical UniversityDepartment of Diagnostic Pathology, Asahikawa Medical University HospitalDepartment of Diagnostic Pathology, Asahikawa Medical University HospitalDepartment of Diagnostic Pathology, Asahikawa Medical University HospitalDepartment of Internal Medicine, Division of Respiratory Medicine and Neurology, Asahikawa Medical UniversityAbstract Invasive mucinous adenocarcinoma (IMA) is a rare subtype of lung adenocarcinoma with a poor prognosis. Compared to non-small cell lung cancer, IMA more frequently harbors KRAS mutations in the order p.G12V, p.G12D, and p.G12C. This report describes a patient with a KRAS p.G12C-mutant IMA treated with sotorasib. To date, no studies have investigated the therapeutic efficacy or resistance mechanisms of sotorasib in IMA. The patient was treated with carboplatin and pemetrexed, followed by sotorasib upon disease progression. While the primary lung lesions responded well, metastatic thoracic lymph node lesions continued to increase. A pathological autopsy was performed with the family’s consent to investigate potential resistance mechanisms. RNA sequencing and additional analyses revealed increased VEGF-A expression in metastatic lymph node lesions, suggesting a role in sotorasib resistance. These findings provide insights into the potential molecular mechanisms underlying treatment resistance in KRAS p.G12C-mutant IMA.https://doi.org/10.1038/s41698-025-00953-2
spellingShingle Hiraku Yanada
Ryohei Yoshida
Ryotaro Kida
Kiichi Nitanai
Maya Ikeda
Kazunori Nagasue
Taeka Naraoka
Masashi Ueda
Takashi Watanabe
Ryota Shigaki
Yasuhiro Umekage
Yoshinori Minami
Toshihiro Nagato
Manami Hayashi
Sayaka Yuzawa
Mishie Tanino
Takaaki Sasaki
Sotorasib resistance in KRAS G12C-mutant invasive mucinous adenocarcinoma with implications for VEGF-A
npj Precision Oncology
title Sotorasib resistance in KRAS G12C-mutant invasive mucinous adenocarcinoma with implications for VEGF-A
title_full Sotorasib resistance in KRAS G12C-mutant invasive mucinous adenocarcinoma with implications for VEGF-A
title_fullStr Sotorasib resistance in KRAS G12C-mutant invasive mucinous adenocarcinoma with implications for VEGF-A
title_full_unstemmed Sotorasib resistance in KRAS G12C-mutant invasive mucinous adenocarcinoma with implications for VEGF-A
title_short Sotorasib resistance in KRAS G12C-mutant invasive mucinous adenocarcinoma with implications for VEGF-A
title_sort sotorasib resistance in kras g12c mutant invasive mucinous adenocarcinoma with implications for vegf a
url https://doi.org/10.1038/s41698-025-00953-2
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