Identification of a new lesch-nyhan syndrome mutation (HPRT BRASIL) and analysis of potentially heterozygous females

The mutation in the hypoxanthine-guanine phosphoribosyltransferase (HPRT) gene has been determined in two brothers affected with Lesch-Nyhan syndrome. Female members of the family who are at risk for being heterozygous carriers of the HPRT mutation were also studied to determine whether they carry t...

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Main Authors: PATRICK O'NEILL, LUCY TROMBLEY, MARY GUNDEL, TIMOTHY HUNTER, JANICE A. NICKLAS, MARA LUCIA S. FERREIRA, MARIA JULIA BUGALLO, ANTÔNIO CARLOS FARIAS, ALFREDO LOHR, MERI DIAMANTOPOULOS, SALMO RASKIN
Format: Article
Language:English
Published: Thieme Revinter Publicações 1999-12-01
Series:Arquivos de Neuro-Psiquiatria
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Online Access:http://www.scielo.br/scielo.php?script=sci_arttext&pid=S0004-282X1999000600001&tlng=en
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author PATRICK O'NEILL
LUCY TROMBLEY
MARY GUNDEL
TIMOTHY HUNTER
JANICE A. NICKLAS
MARA LUCIA S. FERREIRA
MARIA JULIA BUGALLO
ANTÔNIO CARLOS FARIAS
ALFREDO LOHR
MERI DIAMANTOPOULOS
SALMO RASKIN
author_facet PATRICK O'NEILL
LUCY TROMBLEY
MARY GUNDEL
TIMOTHY HUNTER
JANICE A. NICKLAS
MARA LUCIA S. FERREIRA
MARIA JULIA BUGALLO
ANTÔNIO CARLOS FARIAS
ALFREDO LOHR
MERI DIAMANTOPOULOS
SALMO RASKIN
author_sort PATRICK O'NEILL
collection DOAJ
description The mutation in the hypoxanthine-guanine phosphoribosyltransferase (HPRT) gene has been determined in two brothers affected with Lesch-Nyhan syndrome. Female members of the family who are at risk for being heterozygous carriers of the HPRT mutation were also studied to determine whether they carry the mutation. DNA sequencing revealed that the boys' mother is heterozygous for the mutation in her somatic cells, but that three maternal aunts are not heterozygous. Such carrier information is important for the future pregnancy plans of at-risk females. The mutation, an A-->T transversion at cDNA base 590 (590A-->T), results in an amino acid change of glutamic acid to valine at codon 197, and has not been reported previously in a Lesch-Nyhan syndrome male. This mutation is designated HPRT Brasil.
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spelling doaj-art-d6d2f52759fd4dcab0ca9fed9d6c8d852025-08-20T02:04:01ZengThieme Revinter PublicaçõesArquivos de Neuro-Psiquiatria1678-42271999-12-0157490791110.1590/S0004-282X1999000600001Identification of a new lesch-nyhan syndrome mutation (HPRT BRASIL) and analysis of potentially heterozygous femalesPATRICK O'NEILL0LUCY TROMBLEY1MARY GUNDEL2TIMOTHY HUNTER3JANICE A. NICKLAS4MARA LUCIA S. FERREIRA5MARIA JULIA BUGALLO6ANTÔNIO CARLOS FARIAS7ALFREDO LOHR8MERI DIAMANTOPOULOS9SALMO RASKIN10University of VermontUniversity of VermontUniversity of VermontUniversity of VermontUniversity of VermontHospital Pequeno PríncipeHospital Pequeno PríncipeHospital Pequeno PríncipeHospital Pequeno PríncipeHospital Pequeno PríncipeHospital Pequeno PríncipeThe mutation in the hypoxanthine-guanine phosphoribosyltransferase (HPRT) gene has been determined in two brothers affected with Lesch-Nyhan syndrome. Female members of the family who are at risk for being heterozygous carriers of the HPRT mutation were also studied to determine whether they carry the mutation. DNA sequencing revealed that the boys' mother is heterozygous for the mutation in her somatic cells, but that three maternal aunts are not heterozygous. Such carrier information is important for the future pregnancy plans of at-risk females. The mutation, an A-->T transversion at cDNA base 590 (590A-->T), results in an amino acid change of glutamic acid to valine at codon 197, and has not been reported previously in a Lesch-Nyhan syndrome male. This mutation is designated HPRT Brasil.http://www.scielo.br/scielo.php?script=sci_arttext&pid=S0004-282X1999000600001&tlng=enLesch-Nyhan syndromeDNAHPRT
spellingShingle PATRICK O'NEILL
LUCY TROMBLEY
MARY GUNDEL
TIMOTHY HUNTER
JANICE A. NICKLAS
MARA LUCIA S. FERREIRA
MARIA JULIA BUGALLO
ANTÔNIO CARLOS FARIAS
ALFREDO LOHR
MERI DIAMANTOPOULOS
SALMO RASKIN
Identification of a new lesch-nyhan syndrome mutation (HPRT BRASIL) and analysis of potentially heterozygous females
Arquivos de Neuro-Psiquiatria
Lesch-Nyhan syndrome
DNA
HPRT
title Identification of a new lesch-nyhan syndrome mutation (HPRT BRASIL) and analysis of potentially heterozygous females
title_full Identification of a new lesch-nyhan syndrome mutation (HPRT BRASIL) and analysis of potentially heterozygous females
title_fullStr Identification of a new lesch-nyhan syndrome mutation (HPRT BRASIL) and analysis of potentially heterozygous females
title_full_unstemmed Identification of a new lesch-nyhan syndrome mutation (HPRT BRASIL) and analysis of potentially heterozygous females
title_short Identification of a new lesch-nyhan syndrome mutation (HPRT BRASIL) and analysis of potentially heterozygous females
title_sort identification of a new lesch nyhan syndrome mutation hprt brasil and analysis of potentially heterozygous females
topic Lesch-Nyhan syndrome
DNA
HPRT
url http://www.scielo.br/scielo.php?script=sci_arttext&pid=S0004-282X1999000600001&tlng=en
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