Duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinoma

Abstract Mutation of the Duchenne muscular dystrophy (DMD) gene causes neuromuscular disorders, but increasing evidence has implicated DMD in the development and progression of several major cancer types. This study investigates the prognostic and biological significance of DMD expression in head an...

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Main Authors: Leanne Jones, Sonika Divakar, Lewis Collins, Wael Hamarneh, Phillip Ameerally, Karen Anthony, Lee Machado
Format: Article
Language:English
Published: Nature Portfolio 2025-03-01
Series:Scientific Reports
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Online Access:https://doi.org/10.1038/s41598-025-94221-9
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author Leanne Jones
Sonika Divakar
Lewis Collins
Wael Hamarneh
Phillip Ameerally
Karen Anthony
Lee Machado
author_facet Leanne Jones
Sonika Divakar
Lewis Collins
Wael Hamarneh
Phillip Ameerally
Karen Anthony
Lee Machado
author_sort Leanne Jones
collection DOAJ
description Abstract Mutation of the Duchenne muscular dystrophy (DMD) gene causes neuromuscular disorders, but increasing evidence has implicated DMD in the development and progression of several major cancer types. This study investigates the prognostic and biological significance of DMD expression in head and neck squamous cell carcinoma (HNSCC). Analysis of The Cancer Genome Atlas (TCGA) data revealed that high DMD expression correlates with improved overall (median survival difference: 22 months, p = 0.0083) and progression-free (p = 0.0237) survival. The Dp71ab transcript is most strongly associated with better outcomes (median overall survival: 42 months, p = 0.0007). Notably, DMD expression levels stratify HPV-positive patients, identifying a DMD low/HPV-positive subgroup with poor outcomes. Immunohistochemical analysis of 50 HNSCC tissue cases confirmed dystrophin localisation in the nucleus and cytoplasm, with high nuclear expression linked to longer overall survival (mean difference: 31 months, p = 0.0497). Functional assays in HNSCC cells showed that Dp71ab overexpression disrupts nuclear morphology and reduces proliferation. Differential gene expression analysis additionally identified 388 upregulated and 30 downregulated genes, with pathways linked to muscle processes, ribosome biogenesis and non-coding RNA regulation. These findings highlight DMD as a potential biomarker and/or therapeutic target in HNSCC, warranting further mechanistic studies of Dp71 isoforms.
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spelling doaj-art-d6536e6672b846c1aa2c2480dc844dae2025-08-20T03:40:45ZengNature PortfolioScientific Reports2045-23222025-03-0115111210.1038/s41598-025-94221-9Duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinomaLeanne Jones0Sonika Divakar1Lewis Collins2Wael Hamarneh3Phillip Ameerally4Karen Anthony5Lee Machado6Centre for Physical Activity and Life Sciences, University of NorthamptonCentre for Physical Activity and Life Sciences, University of NorthamptonCentre for Physical Activity and Life Sciences, University of NorthamptonNorthampton General Hospital NHS TrustMaxillofacial Department, Northampton General Hospital NHS TrustCentre for Physical Activity and Life Sciences, University of NorthamptonCentre for Physical Activity and Life Sciences, University of NorthamptonAbstract Mutation of the Duchenne muscular dystrophy (DMD) gene causes neuromuscular disorders, but increasing evidence has implicated DMD in the development and progression of several major cancer types. This study investigates the prognostic and biological significance of DMD expression in head and neck squamous cell carcinoma (HNSCC). Analysis of The Cancer Genome Atlas (TCGA) data revealed that high DMD expression correlates with improved overall (median survival difference: 22 months, p = 0.0083) and progression-free (p = 0.0237) survival. The Dp71ab transcript is most strongly associated with better outcomes (median overall survival: 42 months, p = 0.0007). Notably, DMD expression levels stratify HPV-positive patients, identifying a DMD low/HPV-positive subgroup with poor outcomes. Immunohistochemical analysis of 50 HNSCC tissue cases confirmed dystrophin localisation in the nucleus and cytoplasm, with high nuclear expression linked to longer overall survival (mean difference: 31 months, p = 0.0497). Functional assays in HNSCC cells showed that Dp71ab overexpression disrupts nuclear morphology and reduces proliferation. Differential gene expression analysis additionally identified 388 upregulated and 30 downregulated genes, with pathways linked to muscle processes, ribosome biogenesis and non-coding RNA regulation. These findings highlight DMD as a potential biomarker and/or therapeutic target in HNSCC, warranting further mechanistic studies of Dp71 isoforms.https://doi.org/10.1038/s41598-025-94221-9DMDDystrophinHNSCCCancerHeadNeck cancer
spellingShingle Leanne Jones
Sonika Divakar
Lewis Collins
Wael Hamarneh
Phillip Ameerally
Karen Anthony
Lee Machado
Duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinoma
Scientific Reports
DMD
Dystrophin
HNSCC
Cancer
Head
Neck cancer
title Duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinoma
title_full Duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinoma
title_fullStr Duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinoma
title_full_unstemmed Duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinoma
title_short Duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinoma
title_sort duchenne muscular dystrophy gene product expression is associated with survival in head and neck squamous cell carcinoma
topic DMD
Dystrophin
HNSCC
Cancer
Head
Neck cancer
url https://doi.org/10.1038/s41598-025-94221-9
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