Sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis - perforinopathy: case based review

Systemic juvenile idiopathic arthritis is a subtype of juvenile idiopathic arthritis and characterized by arthritis and many systemic features like fever, rash, hepatosplenomegaly, lymphadenopathy and serositis. Macrophage activation syndrome is the most dreadful complication of systemic juvenile i...

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Main Authors: Mustafa Çakan, Nuray Aktay-Ayaz, Hakan Gemici, Agageldi Annayev, Agop Çıtak, Arzu Akçay, Gülyüz Öztürk
Format: Article
Language:English
Published: Hacettepe University Institute of Child Health 2018-10-01
Series:The Turkish Journal of Pediatrics
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Online Access:https://turkjpediatr.org/article/view/911
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author Mustafa Çakan
Nuray Aktay-Ayaz
Hakan Gemici
Agageldi Annayev
Agop Çıtak
Arzu Akçay
Gülyüz Öztürk
author_facet Mustafa Çakan
Nuray Aktay-Ayaz
Hakan Gemici
Agageldi Annayev
Agop Çıtak
Arzu Akçay
Gülyüz Öztürk
author_sort Mustafa Çakan
collection DOAJ
description Systemic juvenile idiopathic arthritis is a subtype of juvenile idiopathic arthritis and characterized by arthritis and many systemic features like fever, rash, hepatosplenomegaly, lymphadenopathy and serositis. Macrophage activation syndrome is the most dreadful complication of systemic juvenile idiopathic arthritis and can cause mortality and morbidity if not recognized and treated early and aggressively. Hemophagocytic lymphohistiocytosis (HLH) is characterized by diminished or absent activities of natural killer cells and cytotoxic T lymphocytes leading to cytokine storm and uncontrolled activation of T cells and macrophages. Primary (familial) HLH is a group of autosomal recessive disorders caused by mutations in the perforin and other related genes and distinctive for onset during early infancy and high rate of mortality. Secondary HLH may be caused by infectious, oncologic and rheumatologic disorders. The term Perforinopathy is used to describe cases with classical familial HLH and also for cases with familial HLH gene mutations but not following a classical familial HLH course. Herein we report a case of chronic perforinopathy in which clinical symptoms started with systemic juvenile idiopathic arthritis and severe macrophage activation syndrome that needed plasma exchange and extracorporeal membrane oxygenation during acute period and ongoing interleukin-1 blockage for sustained hyperferritinemia.
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publishDate 2018-10-01
publisher Hacettepe University Institute of Child Health
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spelling doaj-art-d53e39f20f614c14abaab4d1f7e7895a2025-08-20T02:01:51ZengHacettepe University Institute of Child HealthThe Turkish Journal of Pediatrics0041-43012791-64212018-10-0160510.24953/turkjped.2018.05.022Sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis - perforinopathy: case based reviewMustafa Çakan0Nuray Aktay-Ayaz1Hakan Gemici2Agageldi Annayev3Agop Çıtak4Arzu Akçay5Gülyüz Öztürk6Clinics of Pediatric Rheumatology, Kanuni Sultan Süleyman Research and Training Hospital.Clinics of Pediatric Rheumatology, Kanuni Sultan Süleyman Research and Training Hospital.Clinics of Pediatrics, Kanuni Sultan Süleyman Research and Training Hospital, Kanuni Sultan Süleyman Research and Training Hospital.Department of Pediatrics, Acıbadem University Atakent Hospital, Istanbul, Turkey.Department of Pediatrics, Acıbadem University Atakent Hospital, Istanbul, Turkey.Department of Pediatric Hematology and Oncology, Acıbadem University Atakent Hospital, Istanbul, Turkey.Department of Pediatric Hematology and Oncology, Acıbadem University Atakent Hospital, Istanbul, Turkey. Systemic juvenile idiopathic arthritis is a subtype of juvenile idiopathic arthritis and characterized by arthritis and many systemic features like fever, rash, hepatosplenomegaly, lymphadenopathy and serositis. Macrophage activation syndrome is the most dreadful complication of systemic juvenile idiopathic arthritis and can cause mortality and morbidity if not recognized and treated early and aggressively. Hemophagocytic lymphohistiocytosis (HLH) is characterized by diminished or absent activities of natural killer cells and cytotoxic T lymphocytes leading to cytokine storm and uncontrolled activation of T cells and macrophages. Primary (familial) HLH is a group of autosomal recessive disorders caused by mutations in the perforin and other related genes and distinctive for onset during early infancy and high rate of mortality. Secondary HLH may be caused by infectious, oncologic and rheumatologic disorders. The term Perforinopathy is used to describe cases with classical familial HLH and also for cases with familial HLH gene mutations but not following a classical familial HLH course. Herein we report a case of chronic perforinopathy in which clinical symptoms started with systemic juvenile idiopathic arthritis and severe macrophage activation syndrome that needed plasma exchange and extracorporeal membrane oxygenation during acute period and ongoing interleukin-1 blockage for sustained hyperferritinemia. https://turkjpediatr.org/article/view/911hyperferritinemiamacrophage activation syndromeperforin A91Vperforinopathysystemic juvenile idiopathic arthritis
spellingShingle Mustafa Çakan
Nuray Aktay-Ayaz
Hakan Gemici
Agageldi Annayev
Agop Çıtak
Arzu Akçay
Gülyüz Öztürk
Sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis - perforinopathy: case based review
The Turkish Journal of Pediatrics
hyperferritinemia
macrophage activation syndrome
perforin A91V
perforinopathy
systemic juvenile idiopathic arthritis
title Sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis - perforinopathy: case based review
title_full Sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis - perforinopathy: case based review
title_fullStr Sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis - perforinopathy: case based review
title_full_unstemmed Sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis - perforinopathy: case based review
title_short Sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis - perforinopathy: case based review
title_sort sustained hyperferritinemia in a child with macrophage activation syndrome secondary to systemic juvenile idiopathic arthritis perforinopathy case based review
topic hyperferritinemia
macrophage activation syndrome
perforin A91V
perforinopathy
systemic juvenile idiopathic arthritis
url https://turkjpediatr.org/article/view/911
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