Unveiling Clinical and Genetic Distinctions in Pure‐Apical Versus Distal‐Dominant Apical Hypertrophic Cardiomyopathy

Background Original apical hypertrophic cardiomyopathy was characterized by left ventricular hypertrophy confined to the apex below the papillary muscle level. In contrast, apical hypertrophic cardiomyopathy in Western countries often includes hypertrophy extending to the midventricular septum. Reco...

Full description

Saved in:
Bibliographic Details
Main Authors: Kenta Sugiura, Toru Kubo, Shunsuke Inoue, Seitaro Nomura, Takanobu Yamada, Takashige Tobita, Yuki Kuramoto, Yohei Miyashita, Yoshihiro Asano, Yuri Ochi, Kazuya Miyagawa, Yuichi Baba, Tatsuya Noguchi, Takayoshi Hirota, Naohito Yamasaki, Hiroyuki Morita, Issei Komuro, Hiroaki Kitaoka
Format: Article
Language:English
Published: Wiley 2025-03-01
Series:Journal of the American Heart Association: Cardiovascular and Cerebrovascular Disease
Subjects:
Online Access:https://www.ahajournals.org/doi/10.1161/JAHA.124.038208
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850123483859648512
author Kenta Sugiura
Toru Kubo
Shunsuke Inoue
Seitaro Nomura
Takanobu Yamada
Takashige Tobita
Yuki Kuramoto
Yohei Miyashita
Yoshihiro Asano
Yuri Ochi
Kazuya Miyagawa
Yuichi Baba
Tatsuya Noguchi
Takayoshi Hirota
Naohito Yamasaki
Hiroyuki Morita
Issei Komuro
Hiroaki Kitaoka
author_facet Kenta Sugiura
Toru Kubo
Shunsuke Inoue
Seitaro Nomura
Takanobu Yamada
Takashige Tobita
Yuki Kuramoto
Yohei Miyashita
Yoshihiro Asano
Yuri Ochi
Kazuya Miyagawa
Yuichi Baba
Tatsuya Noguchi
Takayoshi Hirota
Naohito Yamasaki
Hiroyuki Morita
Issei Komuro
Hiroaki Kitaoka
author_sort Kenta Sugiura
collection DOAJ
description Background Original apical hypertrophic cardiomyopathy was characterized by left ventricular hypertrophy confined to the apex below the papillary muscle level. In contrast, apical hypertrophic cardiomyopathy in Western countries often includes hypertrophy extending to the midventricular septum. Recognizing these phenotypic differences is essential as they may influence the clinical prognosis. The aim of this study was to delineate the clinical and genetic disparities between the pure‐apical form, according to the original definition, and the distal‐dominant form, in which hypertrophy extends to the ventricular septum without basal septal hypertrophy. Methods A retrospective analysis was conducted for 111 consecutive patients with apical hypertrophic cardiomyopathy with assessment of hypertrophic cardiomyopathy–related adverse events including hypertrophic cardiomyopathy–related death, heart failure admission, embolic stroke admission, and sustained ventricular tachycardia with hemodynamic instability or appropriate implantable cardioverter‐defibrillator discharge. Genetic testing for hypertrophic cardiomyopathy‐associated genes was performed in 72 patients. Results Among the patients, 60 were classified as pure‐apical form, and 51 were classified as distal‐dominant form. The median age at diagnosis was 63 years, with a predominance of men in both groups. Over a follow‐up period of 11.0 years, the incidence of hypertrophic cardiomyopathy–related adverse events was significantly higher in the distal‐dominant group than in the pure‐apical group (log‐rank, P<0.001). The detection rate of pathogenic or likely pathogenic variants was also significantly higher in the distal‐dominant group than in the pure‐apical group (26% versus 3%; P=0.005). Conclusions Distinct clinical and genetic profiles of the 2 apical hypertrophic cardiomyopathy phenotypes warrant their recognition and differentiation in clinical practice due to distinct prognoses and genetic backgrounds.
format Article
id doaj-art-d3e922dcf8264c2e8167b3fa5263d661
institution OA Journals
issn 2047-9980
language English
publishDate 2025-03-01
publisher Wiley
record_format Article
series Journal of the American Heart Association: Cardiovascular and Cerebrovascular Disease
spelling doaj-art-d3e922dcf8264c2e8167b3fa5263d6612025-08-20T02:34:35ZengWileyJournal of the American Heart Association: Cardiovascular and Cerebrovascular Disease2047-99802025-03-0114610.1161/JAHA.124.038208Unveiling Clinical and Genetic Distinctions in Pure‐Apical Versus Distal‐Dominant Apical Hypertrophic CardiomyopathyKenta Sugiura0Toru Kubo1Shunsuke Inoue2Seitaro Nomura3Takanobu Yamada4Takashige Tobita5Yuki Kuramoto6Yohei Miyashita7Yoshihiro Asano8Yuri Ochi9Kazuya Miyagawa10Yuichi Baba11Tatsuya Noguchi12Takayoshi Hirota13Naohito Yamasaki14Hiroyuki Morita15Issei Komuro16Hiroaki Kitaoka17Department of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanDepartment of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanDepartment of Cardiovascular Medicine, Graduate School of Medicine The University of Tokyo JapanDepartment of Cardiovascular Medicine, Graduate School of Medicine The University of Tokyo JapanDepartment of Cardiovascular Medicine, Graduate School of Medicine The University of Tokyo JapanDepartment of Cardiology Tokyo Women’s Medical University Tokyo JapanDepartment of Cardiovascular Medicine Osaka University Graduate School of Medicine Suita JapanDepartment of Cardiovascular Medicine Osaka University Graduate School of Medicine Suita JapanDepartment of Cardiovascular Medicine Osaka University Graduate School of Medicine Suita JapanDepartment of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanDepartment of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanDepartment of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanDepartment of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanDepartment of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanDepartment of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanDepartment of Cardiovascular Medicine, Graduate School of Medicine The University of Tokyo JapanDepartment of Frontier Cardiovascular Science The University of Tokyo Graduate School of Medicine Tokyo JapanDepartment of Cardiology and Geriatrics, Kochi Medical School Kochi University Kochi JapanBackground Original apical hypertrophic cardiomyopathy was characterized by left ventricular hypertrophy confined to the apex below the papillary muscle level. In contrast, apical hypertrophic cardiomyopathy in Western countries often includes hypertrophy extending to the midventricular septum. Recognizing these phenotypic differences is essential as they may influence the clinical prognosis. The aim of this study was to delineate the clinical and genetic disparities between the pure‐apical form, according to the original definition, and the distal‐dominant form, in which hypertrophy extends to the ventricular septum without basal septal hypertrophy. Methods A retrospective analysis was conducted for 111 consecutive patients with apical hypertrophic cardiomyopathy with assessment of hypertrophic cardiomyopathy–related adverse events including hypertrophic cardiomyopathy–related death, heart failure admission, embolic stroke admission, and sustained ventricular tachycardia with hemodynamic instability or appropriate implantable cardioverter‐defibrillator discharge. Genetic testing for hypertrophic cardiomyopathy‐associated genes was performed in 72 patients. Results Among the patients, 60 were classified as pure‐apical form, and 51 were classified as distal‐dominant form. The median age at diagnosis was 63 years, with a predominance of men in both groups. Over a follow‐up period of 11.0 years, the incidence of hypertrophic cardiomyopathy–related adverse events was significantly higher in the distal‐dominant group than in the pure‐apical group (log‐rank, P<0.001). The detection rate of pathogenic or likely pathogenic variants was also significantly higher in the distal‐dominant group than in the pure‐apical group (26% versus 3%; P=0.005). Conclusions Distinct clinical and genetic profiles of the 2 apical hypertrophic cardiomyopathy phenotypes warrant their recognition and differentiation in clinical practice due to distinct prognoses and genetic backgrounds.https://www.ahajournals.org/doi/10.1161/JAHA.124.038208apical hypertrophic cardiomyopathy (ApHCM)geneticshypertrophic cardiomyopathy (HCM)phenotypeprognosis
spellingShingle Kenta Sugiura
Toru Kubo
Shunsuke Inoue
Seitaro Nomura
Takanobu Yamada
Takashige Tobita
Yuki Kuramoto
Yohei Miyashita
Yoshihiro Asano
Yuri Ochi
Kazuya Miyagawa
Yuichi Baba
Tatsuya Noguchi
Takayoshi Hirota
Naohito Yamasaki
Hiroyuki Morita
Issei Komuro
Hiroaki Kitaoka
Unveiling Clinical and Genetic Distinctions in Pure‐Apical Versus Distal‐Dominant Apical Hypertrophic Cardiomyopathy
Journal of the American Heart Association: Cardiovascular and Cerebrovascular Disease
apical hypertrophic cardiomyopathy (ApHCM)
genetics
hypertrophic cardiomyopathy (HCM)
phenotype
prognosis
title Unveiling Clinical and Genetic Distinctions in Pure‐Apical Versus Distal‐Dominant Apical Hypertrophic Cardiomyopathy
title_full Unveiling Clinical and Genetic Distinctions in Pure‐Apical Versus Distal‐Dominant Apical Hypertrophic Cardiomyopathy
title_fullStr Unveiling Clinical and Genetic Distinctions in Pure‐Apical Versus Distal‐Dominant Apical Hypertrophic Cardiomyopathy
title_full_unstemmed Unveiling Clinical and Genetic Distinctions in Pure‐Apical Versus Distal‐Dominant Apical Hypertrophic Cardiomyopathy
title_short Unveiling Clinical and Genetic Distinctions in Pure‐Apical Versus Distal‐Dominant Apical Hypertrophic Cardiomyopathy
title_sort unveiling clinical and genetic distinctions in pure apical versus distal dominant apical hypertrophic cardiomyopathy
topic apical hypertrophic cardiomyopathy (ApHCM)
genetics
hypertrophic cardiomyopathy (HCM)
phenotype
prognosis
url https://www.ahajournals.org/doi/10.1161/JAHA.124.038208
work_keys_str_mv AT kentasugiura unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT torukubo unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT shunsukeinoue unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT seitaronomura unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT takanobuyamada unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT takashigetobita unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT yukikuramoto unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT yoheimiyashita unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT yoshihiroasano unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT yuriochi unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT kazuyamiyagawa unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT yuichibaba unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT tatsuyanoguchi unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT takayoshihirota unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT naohitoyamasaki unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT hiroyukimorita unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT isseikomuro unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy
AT hiroakikitaoka unveilingclinicalandgeneticdistinctionsinpureapicalversusdistaldominantapicalhypertrophiccardiomyopathy