Bortezomib promotes the TRAIL-mediated killing of resistant rhabdomyosarcoma by ErbB2/Her2-targeted CAR-NK-92 cells via DR5 upregulation

Treatment resistance and immune escape are hallmarks of metastatic rhabdomyosarcoma (RMS), underscoring the urgent medical need for therapeutic agents against this disease entity as a key challenge in pediatric oncology. Chimeric antigen receptor (CAR)-based immunotherapies, such as the ErbB2 (Her2)...

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Main Authors: Catrin Heim, Leonie Hartig, Nadine Weinelt, Laura M. Moser, Emilia Salzmann-Manrique, Michael Merker, Winfried S. Wels, Torsten Tonn, Peter Bader, Jan-Henning Klusmann, Sjoerd J.L. van Wijk, Eva Rettinger
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Language:English
Published: Elsevier 2024-06-01
Series:Molecular Therapy: Oncology
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Online Access:http://www.sciencedirect.com/science/article/pii/S2950329924000444
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author Catrin Heim
Leonie Hartig
Nadine Weinelt
Laura M. Moser
Emilia Salzmann-Manrique
Michael Merker
Winfried S. Wels
Torsten Tonn
Peter Bader
Jan-Henning Klusmann
Sjoerd J.L. van Wijk
Eva Rettinger
author_facet Catrin Heim
Leonie Hartig
Nadine Weinelt
Laura M. Moser
Emilia Salzmann-Manrique
Michael Merker
Winfried S. Wels
Torsten Tonn
Peter Bader
Jan-Henning Klusmann
Sjoerd J.L. van Wijk
Eva Rettinger
author_sort Catrin Heim
collection DOAJ
description Treatment resistance and immune escape are hallmarks of metastatic rhabdomyosarcoma (RMS), underscoring the urgent medical need for therapeutic agents against this disease entity as a key challenge in pediatric oncology. Chimeric antigen receptor (CAR)-based immunotherapies, such as the ErbB2 (Her2)-CAR-engineered natural killer (NK) cell line NK-92/5.28.z, provide antitumor cytotoxicity primarily through CAR-mediated cytotoxic granule release and thereafter—even in cases with low surface antigen expression or tumor escape—by triggering intrinsic NK cell-mediated apoptosis induction via additional ligand/receptors. In this study, we showed that bortezomib increased susceptibility toward apoptosis in clinically relevant RMS cell lines RH30 and RH41, and patient-derived RMS tumor organoid RMS335, by upregulation of the tumor necrosis factor-related apoptosis-inducing ligand (TRAIL) receptor DR5 in these metastatic, relapsed/refractory (r/r) RMS tumors. Subsequent administration of NK-92/5.28.z cells significantly enhanced antitumor activity in vitro. Applying recombinant TRAIL instead of NK-92/5.28.z cells confirmed that the synergistic antitumor effects of the combination treatment were mediated via TRAIL. Western blot analyses indicated that the combination treatment with bortezomib and NK-92/5.28.z cells increased apoptosis by interacting with the nuclear factor κB, JNK, and caspase pathways. Overall, bortezomib pretreatment can sensitize r/r RMS tumors to CAR- and, by upregulating DR5, TRAIL-mediated cytotoxicity of NK-92/5.28.z cells.
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spelling doaj-art-cfcc688602004da1992f3e649b5c4ffd2025-08-20T02:32:49ZengElsevierMolecular Therapy: Oncology2950-32992024-06-0132220080210.1016/j.omton.2024.200802Bortezomib promotes the TRAIL-mediated killing of resistant rhabdomyosarcoma by ErbB2/Her2-targeted CAR-NK-92 cells via DR5 upregulationCatrin Heim0Leonie Hartig1Nadine Weinelt2Laura M. Moser3Emilia Salzmann-Manrique4Michael Merker5Winfried S. Wels6Torsten Tonn7Peter Bader8Jan-Henning Klusmann9Sjoerd J.L. van Wijk10Eva Rettinger11Goethe University Frankfurt, Department of Pediatrics, Division of Stem Cell Transplantation and Immunology, 60590 Frankfurt am Main, Germany; Goethe University Frankfurt, Department of Pediatrics, 60590 Frankfurt am Main, GermanyGoethe University Frankfurt, Department of Pediatrics, Division of Stem Cell Transplantation and Immunology, 60590 Frankfurt am Main, Germany; Goethe University Frankfurt, Department of Pediatrics, 60590 Frankfurt am Main, GermanyInstitute for Experimental Paediatric Haematology and Oncology (EPOH), 60528 Frankfurt am Main, GermanyGoethe University Frankfurt, Department of Pediatrics, Division of Stem Cell Transplantation and Immunology, 60590 Frankfurt am Main, Germany; German Cancer Consortium (DKTK), partner site Frankfurt am Main, a partnership between DKFZ and University Hospital and Georg-Speyer-Haus, Frankfurt am Main, Germany; Frankfurt Cancer Institute (FCI), 60596 Frankfurt am Main, Germany; Universitäres Centrum für Tumorerkrankungen (UCT) Frankfurt Marburg, 60590 Frankfurt am Main, Germany; Goethe University Frankfurt, Department of Pediatrics, 60590 Frankfurt am Main, GermanyGoethe University Frankfurt, Department of Pediatrics, Division of Stem Cell Transplantation and Immunology, 60590 Frankfurt am Main, Germany; Goethe University Frankfurt, Department of Pediatrics, 60590 Frankfurt am Main, GermanyGoethe University Frankfurt, Department of Pediatrics, Division of Stem Cell Transplantation and Immunology, 60590 Frankfurt am Main, Germany; Universitäres Centrum für Tumorerkrankungen (UCT) Frankfurt Marburg, 60590 Frankfurt am Main, Germany; Goethe University Frankfurt, Department of Pediatrics, 60590 Frankfurt am Main, GermanyGerman Cancer Consortium (DKTK), partner site Frankfurt am Main, a partnership between DKFZ and University Hospital and Georg-Speyer-Haus, Frankfurt am Main, Germany; Frankfurt Cancer Institute (FCI), 60596 Frankfurt am Main, Germany; Georg-Speyer-Haus, Institute for Tumor Biology and Experimental Therapy, 60596 Frankfurt am Main, GermanyDRK-Blutspendedienst Baden-Württemberg/Hessen gemeinnützige GmbH, 60505 Frankfurt am Main, GermanyGoethe University Frankfurt, Department of Pediatrics, Division of Stem Cell Transplantation and Immunology, 60590 Frankfurt am Main, Germany; Universitäres Centrum für Tumorerkrankungen (UCT) Frankfurt Marburg, 60590 Frankfurt am Main, Germany; Goethe University Frankfurt, Department of Pediatrics, 60590 Frankfurt am Main, GermanyGerman Cancer Consortium (DKTK), partner site Frankfurt am Main, a partnership between DKFZ and University Hospital and Georg-Speyer-Haus, Frankfurt am Main, Germany; Frankfurt Cancer Institute (FCI), 60596 Frankfurt am Main, Germany; Universitäres Centrum für Tumorerkrankungen (UCT) Frankfurt Marburg, 60590 Frankfurt am Main, Germany; Goethe University Frankfurt, Department of Pediatrics, 60590 Frankfurt am Main, GermanyInstitute for Experimental Paediatric Haematology and Oncology (EPOH), 60528 Frankfurt am Main, Germany; German Cancer Consortium (DKTK), partner site Frankfurt am Main, a partnership between DKFZ and University Hospital and Georg-Speyer-Haus, Frankfurt am Main, Germany; Universitäres Centrum für Tumorerkrankungen (UCT) Frankfurt Marburg, 60590 Frankfurt am Main, GermanyGoethe University Frankfurt, Department of Pediatrics, Division of Stem Cell Transplantation and Immunology, 60590 Frankfurt am Main, Germany; German Cancer Consortium (DKTK), partner site Frankfurt am Main, a partnership between DKFZ and University Hospital and Georg-Speyer-Haus, Frankfurt am Main, Germany; Frankfurt Cancer Institute (FCI), 60596 Frankfurt am Main, Germany; Universitäres Centrum für Tumorerkrankungen (UCT) Frankfurt Marburg, 60590 Frankfurt am Main, Germany; Corresponding author: Eva Rettinger, Goethe University Frankfurt, Department of Pediatrics, Division of Stem Cell Transplantation, Immunology and Intensive Care Medicine, 60590 Frankfurt am Main, Germany.Treatment resistance and immune escape are hallmarks of metastatic rhabdomyosarcoma (RMS), underscoring the urgent medical need for therapeutic agents against this disease entity as a key challenge in pediatric oncology. Chimeric antigen receptor (CAR)-based immunotherapies, such as the ErbB2 (Her2)-CAR-engineered natural killer (NK) cell line NK-92/5.28.z, provide antitumor cytotoxicity primarily through CAR-mediated cytotoxic granule release and thereafter—even in cases with low surface antigen expression or tumor escape—by triggering intrinsic NK cell-mediated apoptosis induction via additional ligand/receptors. In this study, we showed that bortezomib increased susceptibility toward apoptosis in clinically relevant RMS cell lines RH30 and RH41, and patient-derived RMS tumor organoid RMS335, by upregulation of the tumor necrosis factor-related apoptosis-inducing ligand (TRAIL) receptor DR5 in these metastatic, relapsed/refractory (r/r) RMS tumors. Subsequent administration of NK-92/5.28.z cells significantly enhanced antitumor activity in vitro. Applying recombinant TRAIL instead of NK-92/5.28.z cells confirmed that the synergistic antitumor effects of the combination treatment were mediated via TRAIL. Western blot analyses indicated that the combination treatment with bortezomib and NK-92/5.28.z cells increased apoptosis by interacting with the nuclear factor κB, JNK, and caspase pathways. Overall, bortezomib pretreatment can sensitize r/r RMS tumors to CAR- and, by upregulating DR5, TRAIL-mediated cytotoxicity of NK-92/5.28.z cells.http://www.sciencedirect.com/science/article/pii/S2950329924000444MT: Regular Issuechimeric antigen receptorimmunotherapybortezomibTRAILrhabdomyosarcoma
spellingShingle Catrin Heim
Leonie Hartig
Nadine Weinelt
Laura M. Moser
Emilia Salzmann-Manrique
Michael Merker
Winfried S. Wels
Torsten Tonn
Peter Bader
Jan-Henning Klusmann
Sjoerd J.L. van Wijk
Eva Rettinger
Bortezomib promotes the TRAIL-mediated killing of resistant rhabdomyosarcoma by ErbB2/Her2-targeted CAR-NK-92 cells via DR5 upregulation
Molecular Therapy: Oncology
MT: Regular Issue
chimeric antigen receptor
immunotherapy
bortezomib
TRAIL
rhabdomyosarcoma
title Bortezomib promotes the TRAIL-mediated killing of resistant rhabdomyosarcoma by ErbB2/Her2-targeted CAR-NK-92 cells via DR5 upregulation
title_full Bortezomib promotes the TRAIL-mediated killing of resistant rhabdomyosarcoma by ErbB2/Her2-targeted CAR-NK-92 cells via DR5 upregulation
title_fullStr Bortezomib promotes the TRAIL-mediated killing of resistant rhabdomyosarcoma by ErbB2/Her2-targeted CAR-NK-92 cells via DR5 upregulation
title_full_unstemmed Bortezomib promotes the TRAIL-mediated killing of resistant rhabdomyosarcoma by ErbB2/Her2-targeted CAR-NK-92 cells via DR5 upregulation
title_short Bortezomib promotes the TRAIL-mediated killing of resistant rhabdomyosarcoma by ErbB2/Her2-targeted CAR-NK-92 cells via DR5 upregulation
title_sort bortezomib promotes the trail mediated killing of resistant rhabdomyosarcoma by erbb2 her2 targeted car nk 92 cells via dr5 upregulation
topic MT: Regular Issue
chimeric antigen receptor
immunotherapy
bortezomib
TRAIL
rhabdomyosarcoma
url http://www.sciencedirect.com/science/article/pii/S2950329924000444
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