P413: A rare and treatable cause for unexplained white matter lesions: Partial biotinidase deficiency

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Bibliographic Details
Main Authors: Sammie Lai, Madeleine Franchi, Garciela Gallo, Philip Aldana, Pamela Trapane, Fernando Galan
Format: Article
Language:English
Published: Elsevier 2025-01-01
Series:Genetics in Medicine Open
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774425013196
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author Sammie Lai
Madeleine Franchi
Garciela Gallo
Philip Aldana
Pamela Trapane
Fernando Galan
author_facet Sammie Lai
Madeleine Franchi
Garciela Gallo
Philip Aldana
Pamela Trapane
Fernando Galan
author_sort Sammie Lai
collection DOAJ
format Article
id doaj-art-ceea25187483480085442e1c8fd4de21
institution DOAJ
issn 2949-7744
language English
publishDate 2025-01-01
publisher Elsevier
record_format Article
series Genetics in Medicine Open
spelling doaj-art-ceea25187483480085442e1c8fd4de212025-08-20T03:14:01ZengElsevierGenetics in Medicine Open2949-77442025-01-01310328010.1016/j.gimo.2025.103280P413: A rare and treatable cause for unexplained white matter lesions: Partial biotinidase deficiencySammie Lai0Madeleine Franchi1Garciela Gallo2Philip Aldana3Pamela Trapane4Fernando Galan5Mayo Clinic FloridaUF JacksonvilleUF JacksonvilleUF JacksonvilleUF JacksonvilleNemours Children's Healthhttp://www.sciencedirect.com/science/article/pii/S2949774425013196
spellingShingle Sammie Lai
Madeleine Franchi
Garciela Gallo
Philip Aldana
Pamela Trapane
Fernando Galan
P413: A rare and treatable cause for unexplained white matter lesions: Partial biotinidase deficiency
Genetics in Medicine Open
title P413: A rare and treatable cause for unexplained white matter lesions: Partial biotinidase deficiency
title_full P413: A rare and treatable cause for unexplained white matter lesions: Partial biotinidase deficiency
title_fullStr P413: A rare and treatable cause for unexplained white matter lesions: Partial biotinidase deficiency
title_full_unstemmed P413: A rare and treatable cause for unexplained white matter lesions: Partial biotinidase deficiency
title_short P413: A rare and treatable cause for unexplained white matter lesions: Partial biotinidase deficiency
title_sort p413 a rare and treatable cause for unexplained white matter lesions partial biotinidase deficiency
url http://www.sciencedirect.com/science/article/pii/S2949774425013196
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