European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience

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Bibliographic Details
Main Authors: A. T. van der Ploeg, M. Ую Kruijshaar, A. Toscano, P. Laforet, C. Angelini, R. H. Lachmann, S. I. Pascual Pascual, M. Roberts, K. Rosler, T. Stulnig, P. A. van Doorn, P.Y. K. Van den Bergh, J. Vissing, B. Schoser
Format: Article
Language:Russian
Published: ABV-press 2019-01-01
Series:Нервно-мышечные болезни
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Online Access:https://nmb.abvpress.ru/jour/article/view/301
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ISSN:2222-8721
2413-0443