Patients with Papillary Renal Cancer and Germline Duplication of <i>MET</i> Exons 5-21

Hereditary papillary renal carcinoma (HPRC) is a rare monogenic hereditary disease in the group of hereditary cancer syndromes. Clinically, HPRC results in the development of multiple papillary renal cell carcinomas of the kidneys in young adults. HPRC is caused by point activating mutations in the...

Full description

Saved in:
Bibliographic Details
Main Authors: Dmitry S. Mikhaylenko, Natalya B. Kuryakova, Fatima M. Bostanova, Viktoria V. Zabnenkova, Oksana P. Ryzhkova, Ilya V. Volodin, Dmitry V. Zaletaev, Dmitry V. Pustoshilov, Sergey I. Kutsev, Vladimir V. Strelnikov
Format: Article
Language:English
Published: MDPI AG 2025-05-01
Series:Biomedicines
Subjects:
Online Access:https://www.mdpi.com/2227-9059/13/6/1329
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849432821799583744
author Dmitry S. Mikhaylenko
Natalya B. Kuryakova
Fatima M. Bostanova
Viktoria V. Zabnenkova
Oksana P. Ryzhkova
Ilya V. Volodin
Dmitry V. Zaletaev
Dmitry V. Pustoshilov
Sergey I. Kutsev
Vladimir V. Strelnikov
author_facet Dmitry S. Mikhaylenko
Natalya B. Kuryakova
Fatima M. Bostanova
Viktoria V. Zabnenkova
Oksana P. Ryzhkova
Ilya V. Volodin
Dmitry V. Zaletaev
Dmitry V. Pustoshilov
Sergey I. Kutsev
Vladimir V. Strelnikov
author_sort Dmitry S. Mikhaylenko
collection DOAJ
description Hereditary papillary renal carcinoma (HPRC) is a rare monogenic hereditary disease in the group of hereditary cancer syndromes. Clinically, HPRC results in the development of multiple papillary renal cell carcinomas of the kidneys in young adults. HPRC is caused by point activating mutations in the <i>MET</i> gene encoding a transmembrane tyrosine kinase receptor. Until now, all detected germline mutations in HPRC patients were missense variants leading to a constitutive activation of the tyrosine kinase domain. We describe, for the first time, unrelated patients with clinical features similar to HPRC and without <i>MET</i> pathogenic missense variants but harboring an extended heterozygous duplication ~101.4 kb in length (chr7:116740252-116841718) in 7q31.2 determined using whole-genome sequencing (WGS). This duplication results in an additional copy of the <i>MET</i> gene fragment, including exons 5-21. The duplicated exons encode most of the receptor domains. According to the American College of Medical Genetics and Genomics (ACMG) criteria, this duplication is classified as variant of uncertain significance (VUS) at present, but it is not excluded that this duplication may represent an activating mutation. Perhaps, further segregation analysis and functional studies will allow us to more accurately resolve the pathogenicity and diagnostic significance of this germline CNV.
format Article
id doaj-art-c7dfe5fc4dcb462999bc44ac0fe02f67
institution Kabale University
issn 2227-9059
language English
publishDate 2025-05-01
publisher MDPI AG
record_format Article
series Biomedicines
spelling doaj-art-c7dfe5fc4dcb462999bc44ac0fe02f672025-08-20T03:27:15ZengMDPI AGBiomedicines2227-90592025-05-01136132910.3390/biomedicines13061329Patients with Papillary Renal Cancer and Germline Duplication of <i>MET</i> Exons 5-21Dmitry S. Mikhaylenko0Natalya B. Kuryakova1Fatima M. Bostanova2Viktoria V. Zabnenkova3Oksana P. Ryzhkova4Ilya V. Volodin5Dmitry V. Zaletaev6Dmitry V. Pustoshilov7Sergey I. Kutsev8Vladimir V. Strelnikov9Research Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, RussiaResearch Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, RussiaResearch Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, RussiaResearch Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, RussiaResearch Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, RussiaResearch Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, RussiaResearch Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, Russia“Biotech Campus” LLC., Mikluho-Maklaya st., 117437 Moscow, RussiaResearch Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, RussiaResearch Centre for Medical Genetics, Moskvorechie st., 1, 115522 Moscow, RussiaHereditary papillary renal carcinoma (HPRC) is a rare monogenic hereditary disease in the group of hereditary cancer syndromes. Clinically, HPRC results in the development of multiple papillary renal cell carcinomas of the kidneys in young adults. HPRC is caused by point activating mutations in the <i>MET</i> gene encoding a transmembrane tyrosine kinase receptor. Until now, all detected germline mutations in HPRC patients were missense variants leading to a constitutive activation of the tyrosine kinase domain. We describe, for the first time, unrelated patients with clinical features similar to HPRC and without <i>MET</i> pathogenic missense variants but harboring an extended heterozygous duplication ~101.4 kb in length (chr7:116740252-116841718) in 7q31.2 determined using whole-genome sequencing (WGS). This duplication results in an additional copy of the <i>MET</i> gene fragment, including exons 5-21. The duplicated exons encode most of the receptor domains. According to the American College of Medical Genetics and Genomics (ACMG) criteria, this duplication is classified as variant of uncertain significance (VUS) at present, but it is not excluded that this duplication may represent an activating mutation. Perhaps, further segregation analysis and functional studies will allow us to more accurately resolve the pathogenicity and diagnostic significance of this germline CNV.https://www.mdpi.com/2227-9059/13/6/1329hereditary papillary renal cancergene <i>MET</i>germline duplicationnext generation sequencing
spellingShingle Dmitry S. Mikhaylenko
Natalya B. Kuryakova
Fatima M. Bostanova
Viktoria V. Zabnenkova
Oksana P. Ryzhkova
Ilya V. Volodin
Dmitry V. Zaletaev
Dmitry V. Pustoshilov
Sergey I. Kutsev
Vladimir V. Strelnikov
Patients with Papillary Renal Cancer and Germline Duplication of <i>MET</i> Exons 5-21
Biomedicines
hereditary papillary renal cancer
gene <i>MET</i>
germline duplication
next generation sequencing
title Patients with Papillary Renal Cancer and Germline Duplication of <i>MET</i> Exons 5-21
title_full Patients with Papillary Renal Cancer and Germline Duplication of <i>MET</i> Exons 5-21
title_fullStr Patients with Papillary Renal Cancer and Germline Duplication of <i>MET</i> Exons 5-21
title_full_unstemmed Patients with Papillary Renal Cancer and Germline Duplication of <i>MET</i> Exons 5-21
title_short Patients with Papillary Renal Cancer and Germline Duplication of <i>MET</i> Exons 5-21
title_sort patients with papillary renal cancer and germline duplication of i met i exons 5 21
topic hereditary papillary renal cancer
gene <i>MET</i>
germline duplication
next generation sequencing
url https://www.mdpi.com/2227-9059/13/6/1329
work_keys_str_mv AT dmitrysmikhaylenko patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT natalyabkuryakova patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT fatimambostanova patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT viktoriavzabnenkova patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT oksanapryzhkova patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT ilyavvolodin patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT dmitryvzaletaev patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT dmitryvpustoshilov patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT sergeyikutsev patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521
AT vladimirvstrelnikov patientswithpapillaryrenalcancerandgermlineduplicationofimetiexons521