Launching a novel preclinical infrastructure: comparative oncology trials consortium directed therapeutic targeting of TNFalpha to cancer vasculature.

<h4>Background</h4>Under the direction and sponsorship of the National Cancer Institute, we report on the first pre-clinical trial of the Comparative Oncology Trials Consortium (COTC). The COTC is a novel infrastructure to integrate cancers that naturally develop in pet dogs into the dev...

Full description

Saved in:
Bibliographic Details
Main Authors: Melissa C Paoloni, Anita Tandle, Christina Mazcko, Engy Hanna, Stefan Kachala, Amy Leblanc, Shelley Newman, David Vail, Carolyn Henry, Douglas Thamm, Karin Sorenmo, Amin Hajitou, Renata Pasqualini, Wadih Arap, Chand Khanna, Steven K Libutti
Format: Article
Language:English
Published: Public Library of Science (PLoS) 2009-01-01
Series:PLoS ONE
Online Access:https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0004972&type=printable
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850240769092222976
author Melissa C Paoloni
Anita Tandle
Christina Mazcko
Engy Hanna
Stefan Kachala
Amy Leblanc
Shelley Newman
David Vail
Carolyn Henry
Douglas Thamm
Karin Sorenmo
Amin Hajitou
Renata Pasqualini
Wadih Arap
Chand Khanna
Steven K Libutti
author_facet Melissa C Paoloni
Anita Tandle
Christina Mazcko
Engy Hanna
Stefan Kachala
Amy Leblanc
Shelley Newman
David Vail
Carolyn Henry
Douglas Thamm
Karin Sorenmo
Amin Hajitou
Renata Pasqualini
Wadih Arap
Chand Khanna
Steven K Libutti
author_sort Melissa C Paoloni
collection DOAJ
description <h4>Background</h4>Under the direction and sponsorship of the National Cancer Institute, we report on the first pre-clinical trial of the Comparative Oncology Trials Consortium (COTC). The COTC is a novel infrastructure to integrate cancers that naturally develop in pet dogs into the development path of new human drugs. Trials are designed to address questions challenging in conventional preclinical models and early phase human trials. Large animal spontaneous cancer models can be a valuable addition to successful studies of cancer biology and novel therapeutic drug, imaging and device development.<h4>Methodology/principal findings</h4>Through this established infrastructure, the first trial of the COTC (COTC001) evaluated a targeted AAV-phage vector delivering tumor necrosis factor (RGD-A-TNF) to alphaV integrins on tumor endothelium. Trial progress and data was reviewed contemporaneously using a web-enabled electronic reporting system developed for the consortium. Dose-escalation in cohorts of 3 dogs (n = 24) determined an optimal safe dose (5x10(12) transducing units intravenous) of RGD-A-TNF. This demonstrated selective targeting of tumor-associated vasculature and sparing of normal tissues assessed via serial biopsy of both tumor and normal tissue. Repetitive dosing in a cohort of 14 dogs, at the defined optimal dose, was well tolerated and led to objective tumor regression in two dogs (14%), stable disease in six (43%), and disease progression in six (43%) via Response Evaluation Criteria in Solid Tumors (RECIST).<h4>Conclusions/significance</h4>The first study of the COTC has demonstrated the utility and efficiency of the established infrastructure to inform the development of new cancer drugs within large animal naturally occurring cancer models. The preclinical evaluation of RGD-A-TNF within this network provided valuable and necessary data to complete the design of first-in-man studies.
format Article
id doaj-art-c5b6037943c7447f9f8bb2f08c0dda5e
institution OA Journals
issn 1932-6203
language English
publishDate 2009-01-01
publisher Public Library of Science (PLoS)
record_format Article
series PLoS ONE
spelling doaj-art-c5b6037943c7447f9f8bb2f08c0dda5e2025-08-20T02:00:46ZengPublic Library of Science (PLoS)PLoS ONE1932-62032009-01-0143e497210.1371/journal.pone.0004972Launching a novel preclinical infrastructure: comparative oncology trials consortium directed therapeutic targeting of TNFalpha to cancer vasculature.Melissa C PaoloniAnita TandleChristina MazckoEngy HannaStefan KachalaAmy LeblancShelley NewmanDavid VailCarolyn HenryDouglas ThammKarin SorenmoAmin HajitouRenata PasqualiniWadih ArapChand KhannaSteven K Libutti<h4>Background</h4>Under the direction and sponsorship of the National Cancer Institute, we report on the first pre-clinical trial of the Comparative Oncology Trials Consortium (COTC). The COTC is a novel infrastructure to integrate cancers that naturally develop in pet dogs into the development path of new human drugs. Trials are designed to address questions challenging in conventional preclinical models and early phase human trials. Large animal spontaneous cancer models can be a valuable addition to successful studies of cancer biology and novel therapeutic drug, imaging and device development.<h4>Methodology/principal findings</h4>Through this established infrastructure, the first trial of the COTC (COTC001) evaluated a targeted AAV-phage vector delivering tumor necrosis factor (RGD-A-TNF) to alphaV integrins on tumor endothelium. Trial progress and data was reviewed contemporaneously using a web-enabled electronic reporting system developed for the consortium. Dose-escalation in cohorts of 3 dogs (n = 24) determined an optimal safe dose (5x10(12) transducing units intravenous) of RGD-A-TNF. This demonstrated selective targeting of tumor-associated vasculature and sparing of normal tissues assessed via serial biopsy of both tumor and normal tissue. Repetitive dosing in a cohort of 14 dogs, at the defined optimal dose, was well tolerated and led to objective tumor regression in two dogs (14%), stable disease in six (43%), and disease progression in six (43%) via Response Evaluation Criteria in Solid Tumors (RECIST).<h4>Conclusions/significance</h4>The first study of the COTC has demonstrated the utility and efficiency of the established infrastructure to inform the development of new cancer drugs within large animal naturally occurring cancer models. The preclinical evaluation of RGD-A-TNF within this network provided valuable and necessary data to complete the design of first-in-man studies.https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0004972&type=printable
spellingShingle Melissa C Paoloni
Anita Tandle
Christina Mazcko
Engy Hanna
Stefan Kachala
Amy Leblanc
Shelley Newman
David Vail
Carolyn Henry
Douglas Thamm
Karin Sorenmo
Amin Hajitou
Renata Pasqualini
Wadih Arap
Chand Khanna
Steven K Libutti
Launching a novel preclinical infrastructure: comparative oncology trials consortium directed therapeutic targeting of TNFalpha to cancer vasculature.
PLoS ONE
title Launching a novel preclinical infrastructure: comparative oncology trials consortium directed therapeutic targeting of TNFalpha to cancer vasculature.
title_full Launching a novel preclinical infrastructure: comparative oncology trials consortium directed therapeutic targeting of TNFalpha to cancer vasculature.
title_fullStr Launching a novel preclinical infrastructure: comparative oncology trials consortium directed therapeutic targeting of TNFalpha to cancer vasculature.
title_full_unstemmed Launching a novel preclinical infrastructure: comparative oncology trials consortium directed therapeutic targeting of TNFalpha to cancer vasculature.
title_short Launching a novel preclinical infrastructure: comparative oncology trials consortium directed therapeutic targeting of TNFalpha to cancer vasculature.
title_sort launching a novel preclinical infrastructure comparative oncology trials consortium directed therapeutic targeting of tnfalpha to cancer vasculature
url https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0004972&type=printable
work_keys_str_mv AT melissacpaoloni launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT anitatandle launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT christinamazcko launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT engyhanna launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT stefankachala launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT amyleblanc launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT shelleynewman launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT davidvail launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT carolynhenry launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT douglasthamm launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT karinsorenmo launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT aminhajitou launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT renatapasqualini launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT wadiharap launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT chandkhanna launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature
AT stevenklibutti launchinganovelpreclinicalinfrastructurecomparativeoncologytrialsconsortiumdirectedtherapeutictargetingoftnfalphatocancervasculature