Machine learning-driven multi-targeted drug discovery in colon cancer using biomarker signatures

Abstract Computational oncology advances multi-targeted therapies for Colon Cancer (CC) by leveraging molecular data and identifying potential drug candidates. However, challenges persist in understanding CC molecular pathways and identifying essential genes. This research integrates biomarker signa...

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Main Authors: Tingting Liu, Lifan Zhong, Xizhe Sun, Zhijiang He, Witiao Lv, Liyun Deng, Yanfei Chen
Format: Article
Language:English
Published: Nature Portfolio 2025-08-01
Series:npj Precision Oncology
Online Access:https://doi.org/10.1038/s41698-025-01058-6
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author Tingting Liu
Lifan Zhong
Xizhe Sun
Zhijiang He
Witiao Lv
Liyun Deng
Yanfei Chen
author_facet Tingting Liu
Lifan Zhong
Xizhe Sun
Zhijiang He
Witiao Lv
Liyun Deng
Yanfei Chen
author_sort Tingting Liu
collection DOAJ
description Abstract Computational oncology advances multi-targeted therapies for Colon Cancer (CC) by leveraging molecular data and identifying potential drug candidates. However, challenges persist in understanding CC molecular pathways and identifying essential genes. This research integrates biomarker signatures from high-dimensional gene expression, mutation data, and protein interaction networks. The research study employs Adaptive Bacterial Foraging (ABF) optimization to refine search parameters, maximizing the predictive accuracy of therapeutic outcomes. The CatBoost algorithm efficiently classifies patients based on molecular profiles and predicts drug responses. The ABF-CatBoost integration facilitates a multi-targeted therapeutic approach, addressing drug resistance by analyzing mutation patterns, adaptive resistance mechanisms, and conserved binding sites. External validation datasets assess predictive accuracy and generalizability. The results demonstrated that the proposed system outperformed traditional Machine Learning models, such as Support Vector Machine and Random Forest, in terms of accuracy (98.6%), specificity (0.984), sensitivity (0.979), and F1-score (0.978). The model predicts toxicity risks, metabolism pathways, and drug efficacy profiles, ensuring safer and more effective treatments. The artificial intelligence model personalizes therapy by leveraging patient-specific molecular profiles, optimizing drug selection and dosage while minimizing side effects. By altering the biomarker selection and pathway analysis components, this computational framework is modified for other cancers, expanding its application and impact in personalized cancer treatment. It also improves precision medicine in CC therapy, speeding up drug discovery and improving therapeutic outcomes.
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spelling doaj-art-bfcf222629f74c40ae374bec4642f6df2025-08-24T11:05:52ZengNature Portfolionpj Precision Oncology2397-768X2025-08-019111310.1038/s41698-025-01058-6Machine learning-driven multi-targeted drug discovery in colon cancer using biomarker signaturesTingting Liu0Lifan Zhong1Xizhe Sun2Zhijiang He3Witiao Lv4Liyun Deng5Yanfei Chen6Hainan Pharmaceutical Research and Development Science and Technology Park, Hainan Medical University, HaikouHainan Pharmaceutical Research and Development Science and Technology Park, Hainan Medical University, HaikouHainan Pharmaceutical Research and Development Science and Technology Park, Hainan Medical University, HaikouDepartment of Orthopedics, Hainan Provincial Corps Hospital of Chinese People’s Armed Police Force, HaikouSchool of Pharmacy, Hainan Medical University, HaikouSchool of Pharmacy, Hainan Medical University, HaikouHainan Pharmaceutical Research and Development Science and Technology Park, Hainan Medical University, HaikouAbstract Computational oncology advances multi-targeted therapies for Colon Cancer (CC) by leveraging molecular data and identifying potential drug candidates. However, challenges persist in understanding CC molecular pathways and identifying essential genes. This research integrates biomarker signatures from high-dimensional gene expression, mutation data, and protein interaction networks. The research study employs Adaptive Bacterial Foraging (ABF) optimization to refine search parameters, maximizing the predictive accuracy of therapeutic outcomes. The CatBoost algorithm efficiently classifies patients based on molecular profiles and predicts drug responses. The ABF-CatBoost integration facilitates a multi-targeted therapeutic approach, addressing drug resistance by analyzing mutation patterns, adaptive resistance mechanisms, and conserved binding sites. External validation datasets assess predictive accuracy and generalizability. The results demonstrated that the proposed system outperformed traditional Machine Learning models, such as Support Vector Machine and Random Forest, in terms of accuracy (98.6%), specificity (0.984), sensitivity (0.979), and F1-score (0.978). The model predicts toxicity risks, metabolism pathways, and drug efficacy profiles, ensuring safer and more effective treatments. The artificial intelligence model personalizes therapy by leveraging patient-specific molecular profiles, optimizing drug selection and dosage while minimizing side effects. By altering the biomarker selection and pathway analysis components, this computational framework is modified for other cancers, expanding its application and impact in personalized cancer treatment. It also improves precision medicine in CC therapy, speeding up drug discovery and improving therapeutic outcomes.https://doi.org/10.1038/s41698-025-01058-6
spellingShingle Tingting Liu
Lifan Zhong
Xizhe Sun
Zhijiang He
Witiao Lv
Liyun Deng
Yanfei Chen
Machine learning-driven multi-targeted drug discovery in colon cancer using biomarker signatures
npj Precision Oncology
title Machine learning-driven multi-targeted drug discovery in colon cancer using biomarker signatures
title_full Machine learning-driven multi-targeted drug discovery in colon cancer using biomarker signatures
title_fullStr Machine learning-driven multi-targeted drug discovery in colon cancer using biomarker signatures
title_full_unstemmed Machine learning-driven multi-targeted drug discovery in colon cancer using biomarker signatures
title_short Machine learning-driven multi-targeted drug discovery in colon cancer using biomarker signatures
title_sort machine learning driven multi targeted drug discovery in colon cancer using biomarker signatures
url https://doi.org/10.1038/s41698-025-01058-6
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AT zhijianghe machinelearningdrivenmultitargeteddrugdiscoveryincoloncancerusingbiomarkersignatures
AT witiaolv machinelearningdrivenmultitargeteddrugdiscoveryincoloncancerusingbiomarkersignatures
AT liyundeng machinelearningdrivenmultitargeteddrugdiscoveryincoloncancerusingbiomarkersignatures
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