The Rising Era of Immune Checkpoint Inhibitors in Myelodysplastic Syndromes

Myelodysplastic syndromes (MDS) are a heterogeneous group of diseases characterized by ineffective hematopoiesis and a wide spectrum of manifestations ranging from indolent and asymptomatic cytopenias to acute myeloid leukemia (AML). MDS result from genetic and epigenetic derangements in clonal cell...

Full description

Saved in:
Bibliographic Details
Main Authors: Nora Chokr, Rima Patel, Kapil Wattamwar, Samer Chokr
Format: Article
Language:English
Published: Wiley 2018-01-01
Series:Advances in Hematology
Online Access:http://dx.doi.org/10.1155/2018/2458679
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849684830445371392
author Nora Chokr
Rima Patel
Kapil Wattamwar
Samer Chokr
author_facet Nora Chokr
Rima Patel
Kapil Wattamwar
Samer Chokr
author_sort Nora Chokr
collection DOAJ
description Myelodysplastic syndromes (MDS) are a heterogeneous group of diseases characterized by ineffective hematopoiesis and a wide spectrum of manifestations ranging from indolent and asymptomatic cytopenias to acute myeloid leukemia (AML). MDS result from genetic and epigenetic derangements in clonal cells and their surrounding microenvironments. Studies have shown associations between MDS and other autoimmune diseases. Several immune mechanisms have been identified in MDS, suggesting that immune dysregulation might be at least partially implicated in its pathogenesis. This has led to rigorous investigations on the role of immunomodulatory drugs as potential treatment options. Epigenetic modification via immune check point inhibition, while well established as a treatment method for advanced solid tumors, is a new approach being considered in hematologic malignancies including high risk MDS. Several trials are looking at the efficacy of these agents in MDS, as frontline therapy and in relapse, both as monotherapy and in combination with other drugs. In this review, we explore the utility of immune checkpoint inhibitors in MDS and current research evaluating their efficacy.
format Article
id doaj-art-bd3b53acfef940e8b0d428a6cf056560
institution DOAJ
issn 1687-9104
1687-9112
language English
publishDate 2018-01-01
publisher Wiley
record_format Article
series Advances in Hematology
spelling doaj-art-bd3b53acfef940e8b0d428a6cf0565602025-08-20T03:23:19ZengWileyAdvances in Hematology1687-91041687-91122018-01-01201810.1155/2018/24586792458679The Rising Era of Immune Checkpoint Inhibitors in Myelodysplastic SyndromesNora Chokr0Rima Patel1Kapil Wattamwar2Samer Chokr3Department of Internal Medicine, Yale School of Medicine, New Haven, CT, USATufts Medical Center, Boston, MA, USADepartment of Internal Medicine, Yale School of Medicine, New Haven, CT, USAMedical University of Varna, Varna, BulgariaMyelodysplastic syndromes (MDS) are a heterogeneous group of diseases characterized by ineffective hematopoiesis and a wide spectrum of manifestations ranging from indolent and asymptomatic cytopenias to acute myeloid leukemia (AML). MDS result from genetic and epigenetic derangements in clonal cells and their surrounding microenvironments. Studies have shown associations between MDS and other autoimmune diseases. Several immune mechanisms have been identified in MDS, suggesting that immune dysregulation might be at least partially implicated in its pathogenesis. This has led to rigorous investigations on the role of immunomodulatory drugs as potential treatment options. Epigenetic modification via immune check point inhibition, while well established as a treatment method for advanced solid tumors, is a new approach being considered in hematologic malignancies including high risk MDS. Several trials are looking at the efficacy of these agents in MDS, as frontline therapy and in relapse, both as monotherapy and in combination with other drugs. In this review, we explore the utility of immune checkpoint inhibitors in MDS and current research evaluating their efficacy.http://dx.doi.org/10.1155/2018/2458679
spellingShingle Nora Chokr
Rima Patel
Kapil Wattamwar
Samer Chokr
The Rising Era of Immune Checkpoint Inhibitors in Myelodysplastic Syndromes
Advances in Hematology
title The Rising Era of Immune Checkpoint Inhibitors in Myelodysplastic Syndromes
title_full The Rising Era of Immune Checkpoint Inhibitors in Myelodysplastic Syndromes
title_fullStr The Rising Era of Immune Checkpoint Inhibitors in Myelodysplastic Syndromes
title_full_unstemmed The Rising Era of Immune Checkpoint Inhibitors in Myelodysplastic Syndromes
title_short The Rising Era of Immune Checkpoint Inhibitors in Myelodysplastic Syndromes
title_sort rising era of immune checkpoint inhibitors in myelodysplastic syndromes
url http://dx.doi.org/10.1155/2018/2458679
work_keys_str_mv AT norachokr therisingeraofimmunecheckpointinhibitorsinmyelodysplasticsyndromes
AT rimapatel therisingeraofimmunecheckpointinhibitorsinmyelodysplasticsyndromes
AT kapilwattamwar therisingeraofimmunecheckpointinhibitorsinmyelodysplasticsyndromes
AT samerchokr therisingeraofimmunecheckpointinhibitorsinmyelodysplasticsyndromes
AT norachokr risingeraofimmunecheckpointinhibitorsinmyelodysplasticsyndromes
AT rimapatel risingeraofimmunecheckpointinhibitorsinmyelodysplasticsyndromes
AT kapilwattamwar risingeraofimmunecheckpointinhibitorsinmyelodysplasticsyndromes
AT samerchokr risingeraofimmunecheckpointinhibitorsinmyelodysplasticsyndromes