Successful treatment of an anti-MDA5 antibody-positive Juvenile Dermatomyositis patient with refractory interstitial lung disease using tofacitinib
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| Format: | Article |
| Language: | English |
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BMC
2025-02-01
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| Series: | Pediatric Rheumatology Online Journal |
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| Online Access: | https://doi.org/10.1186/s12969-024-01044-5 |
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| author | Valentina Natoli Serena Palmeri Ana Isabel Rebollo-Giménez Caterina Matucci-Cerinic Paola Bocca Roberta Caorsi Stefano Volpi Riccardo Papa Alessandro Consolaro Marco Gattorno Angelo Ravelli Silvia Rosina |
| author_facet | Valentina Natoli Serena Palmeri Ana Isabel Rebollo-Giménez Caterina Matucci-Cerinic Paola Bocca Roberta Caorsi Stefano Volpi Riccardo Papa Alessandro Consolaro Marco Gattorno Angelo Ravelli Silvia Rosina |
| author_sort | Valentina Natoli |
| collection | DOAJ |
| format | Article |
| id | doaj-art-bc8f7efeb0824486b629760a9b5da21f |
| institution | OA Journals |
| issn | 1546-0096 |
| language | English |
| publishDate | 2025-02-01 |
| publisher | BMC |
| record_format | Article |
| series | Pediatric Rheumatology Online Journal |
| spelling | doaj-art-bc8f7efeb0824486b629760a9b5da21f2025-08-20T02:01:35ZengBMCPediatric Rheumatology Online Journal1546-00962025-02-012311510.1186/s12969-024-01044-5Successful treatment of an anti-MDA5 antibody-positive Juvenile Dermatomyositis patient with refractory interstitial lung disease using tofacitinibValentina Natoli0Serena Palmeri1Ana Isabel Rebollo-Giménez2Caterina Matucci-Cerinic3Paola Bocca4Roberta Caorsi5Stefano Volpi6Riccardo Papa7Alessandro Consolaro8Marco Gattorno9Angelo Ravelli10Silvia Rosina11Università degli Studi di Genova, Dipartimento di Neuroscienze, Riabilitazione, Oftalmologia, Genetica e Scienze Materno-Infantili (DiNOGMI)Università degli Studi di Genova, Dipartimento di Neuroscienze, Riabilitazione, Oftalmologia, Genetica e Scienze Materno-Infantili (DiNOGMI)Università degli Studi di Genova, Dipartimento di Neuroscienze, Riabilitazione, Oftalmologia, Genetica e Scienze Materno-Infantili (DiNOGMI)Università degli Studi di Genova, Dipartimento di Neuroscienze, Riabilitazione, Oftalmologia, Genetica e Scienze Materno-Infantili (DiNOGMI)IRCCS Istituto Giannina Gaslini, Paediatric Rheumatology and Autoinflammatory Diseases UnitIRCCS Istituto Giannina Gaslini, Paediatric Rheumatology and Autoinflammatory Diseases UnitUniversità degli Studi di Genova, Dipartimento di Neuroscienze, Riabilitazione, Oftalmologia, Genetica e Scienze Materno-Infantili (DiNOGMI)IRCCS Istituto Giannina Gaslini, Paediatric Rheumatology and Autoinflammatory Diseases UnitUniversità degli Studi di Genova, Dipartimento di Neuroscienze, Riabilitazione, Oftalmologia, Genetica e Scienze Materno-Infantili (DiNOGMI)IRCCS Istituto Giannina Gaslini, Paediatric Rheumatology and Autoinflammatory Diseases UnitUniversità degli Studi di Genova, Dipartimento di Neuroscienze, Riabilitazione, Oftalmologia, Genetica e Scienze Materno-Infantili (DiNOGMI)IRCCS Istituto Giannina Gaslini, Paediatric Rheumatology and Autoinflammatory Diseases Unithttps://doi.org/10.1186/s12969-024-01044-5Juvenile dermatomyositisAnti-MDA5 antibodiesInterstitial lung diseaseTofacitinibJAK inhibitorsType I IFN gene signature |
| spellingShingle | Valentina Natoli Serena Palmeri Ana Isabel Rebollo-Giménez Caterina Matucci-Cerinic Paola Bocca Roberta Caorsi Stefano Volpi Riccardo Papa Alessandro Consolaro Marco Gattorno Angelo Ravelli Silvia Rosina Successful treatment of an anti-MDA5 antibody-positive Juvenile Dermatomyositis patient with refractory interstitial lung disease using tofacitinib Pediatric Rheumatology Online Journal Juvenile dermatomyositis Anti-MDA5 antibodies Interstitial lung disease Tofacitinib JAK inhibitors Type I IFN gene signature |
| title | Successful treatment of an anti-MDA5 antibody-positive Juvenile Dermatomyositis patient with refractory interstitial lung disease using tofacitinib |
| title_full | Successful treatment of an anti-MDA5 antibody-positive Juvenile Dermatomyositis patient with refractory interstitial lung disease using tofacitinib |
| title_fullStr | Successful treatment of an anti-MDA5 antibody-positive Juvenile Dermatomyositis patient with refractory interstitial lung disease using tofacitinib |
| title_full_unstemmed | Successful treatment of an anti-MDA5 antibody-positive Juvenile Dermatomyositis patient with refractory interstitial lung disease using tofacitinib |
| title_short | Successful treatment of an anti-MDA5 antibody-positive Juvenile Dermatomyositis patient with refractory interstitial lung disease using tofacitinib |
| title_sort | successful treatment of an anti mda5 antibody positive juvenile dermatomyositis patient with refractory interstitial lung disease using tofacitinib |
| topic | Juvenile dermatomyositis Anti-MDA5 antibodies Interstitial lung disease Tofacitinib JAK inhibitors Type I IFN gene signature |
| url | https://doi.org/10.1186/s12969-024-01044-5 |
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