Establishment of a transgene-free iPS cell line (SDCHi002-A) from a young patient bearing a NPRL3 mutation and suffering from Epilepsy

Epilepsy affects ∼ 65 million people worldwide. In this study, peripheral blood mononuclear cells were isolated from a young patient patient bearing a Nitrogen Perntease Regulator Like 3 Protein (NPRL3) mutation and suffering from Epilepsy verified by clinical and genetic diagnosis. Induced pluripot...

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Main Authors: Song Su, Ying Ren, Hongwei Zhang, Yi Liu, Yong Liu, Zilong Li, Tong Zhang, Fang Fang
Format: Article
Language:English
Published: Elsevier 2024-12-01
Series:Stem Cell Research
Online Access:http://www.sciencedirect.com/science/article/pii/S1873506124002721
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author Song Su
Ying Ren
Hongwei Zhang
Yi Liu
Yong Liu
Zilong Li
Tong Zhang
Fang Fang
author_facet Song Su
Ying Ren
Hongwei Zhang
Yi Liu
Yong Liu
Zilong Li
Tong Zhang
Fang Fang
author_sort Song Su
collection DOAJ
description Epilepsy affects ∼ 65 million people worldwide. In this study, peripheral blood mononuclear cells were isolated from a young patient patient bearing a Nitrogen Perntease Regulator Like 3 Protein (NPRL3) mutation and suffering from Epilepsy verified by clinical and genetic diagnosis. Induced pluripotent stem cells (iPSCs) were established by a non-integrative method, using plasmids carrying OCT4, SOX2, KLF4, BCL-XL and C-MYC. The established iPSCs presented typical pluripotent cells morphology, normal karyotype, and potential to differentiate into three germ layers. Our approach offers a useful model to explore pathogenesis and therapy of Epilepsy.
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institution DOAJ
issn 1873-5061
language English
publishDate 2024-12-01
publisher Elsevier
record_format Article
series Stem Cell Research
spelling doaj-art-bbaf87bfe7f846e88840eb9ddc78b82a2025-08-20T02:49:53ZengElsevierStem Cell Research1873-50612024-12-018110357410.1016/j.scr.2024.103574Establishment of a transgene-free iPS cell line (SDCHi002-A) from a young patient bearing a NPRL3 mutation and suffering from EpilepsySong Su0Ying Ren1Hongwei Zhang2Yi Liu3Yong Liu4Zilong Li5Tong Zhang6Fang Fang7Epilepsy Center, Children’s Hospital Affiliated to Shandong University, Jinan, Shandong 250022, China; Epilepsy Center, Jinan Children’s Hospital, Jinan, Shandong 250022, ChinaEpilepsy Center, Children’s Hospital Affiliated to Shandong University, Jinan, Shandong 250022, China; Epilepsy Center, Jinan Children’s Hospital, Jinan, Shandong 250022, ChinaEpilepsy Center, Children’s Hospital Affiliated to Shandong University, Jinan, Shandong 250022, China; Epilepsy Center, Jinan Children’s Hospital, Jinan, Shandong 250022, ChinaEpilepsy Center, Children’s Hospital Affiliated to Shandong University, Jinan, Shandong 250022, China; Epilepsy Center, Jinan Children’s Hospital, Jinan, Shandong 250022, ChinaEpilepsy Center, Children’s Hospital Affiliated to Shandong University, Jinan, Shandong 250022, China; Epilepsy Center, Jinan Children’s Hospital, Jinan, Shandong 250022, ChinaEpilepsy Center, Children’s Hospital Affiliated to Shandong University, Jinan, Shandong 250022, China; Epilepsy Center, Jinan Children’s Hospital, Jinan, Shandong 250022, ChinaEpilepsy Center, Children’s Hospital Affiliated to Shandong University, Jinan, Shandong 250022, China; Epilepsy Center, Jinan Children’s Hospital, Jinan, Shandong 250022, ChinaDepartment of Neurology, Beijing Children’s Hospital, National Center for Children’s Health, Capital Medical University, Beijing 100045, China; Corresponding author.Epilepsy affects ∼ 65 million people worldwide. In this study, peripheral blood mononuclear cells were isolated from a young patient patient bearing a Nitrogen Perntease Regulator Like 3 Protein (NPRL3) mutation and suffering from Epilepsy verified by clinical and genetic diagnosis. Induced pluripotent stem cells (iPSCs) were established by a non-integrative method, using plasmids carrying OCT4, SOX2, KLF4, BCL-XL and C-MYC. The established iPSCs presented typical pluripotent cells morphology, normal karyotype, and potential to differentiate into three germ layers. Our approach offers a useful model to explore pathogenesis and therapy of Epilepsy.http://www.sciencedirect.com/science/article/pii/S1873506124002721
spellingShingle Song Su
Ying Ren
Hongwei Zhang
Yi Liu
Yong Liu
Zilong Li
Tong Zhang
Fang Fang
Establishment of a transgene-free iPS cell line (SDCHi002-A) from a young patient bearing a NPRL3 mutation and suffering from Epilepsy
Stem Cell Research
title Establishment of a transgene-free iPS cell line (SDCHi002-A) from a young patient bearing a NPRL3 mutation and suffering from Epilepsy
title_full Establishment of a transgene-free iPS cell line (SDCHi002-A) from a young patient bearing a NPRL3 mutation and suffering from Epilepsy
title_fullStr Establishment of a transgene-free iPS cell line (SDCHi002-A) from a young patient bearing a NPRL3 mutation and suffering from Epilepsy
title_full_unstemmed Establishment of a transgene-free iPS cell line (SDCHi002-A) from a young patient bearing a NPRL3 mutation and suffering from Epilepsy
title_short Establishment of a transgene-free iPS cell line (SDCHi002-A) from a young patient bearing a NPRL3 mutation and suffering from Epilepsy
title_sort establishment of a transgene free ips cell line sdchi002 a from a young patient bearing a nprl3 mutation and suffering from epilepsy
url http://www.sciencedirect.com/science/article/pii/S1873506124002721
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