Real-World Evidence and Managed Entry Agreements

Introduction: Real-World Data (RWD) are data relating to patient health status and/or the delivery of health care routinely collected from a variety of sources such as Electronic Health Records (EHRs), data from product and disease Registries, patient generated data, etc. Real-World Evidence (RWE)...

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Main Authors: Silvia Adami, Cosetta Bianchi, Elisa Crovato, Gianluca Trifirò
Format: Article
Language:English
Published: AboutScience Srl 2025-07-01
Series:Global & Regional Health Technology Assessment
Subjects:
Online Access:https://journals.aboutscience.eu/index.php/grhta/article/view/3563
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author Silvia Adami
Cosetta Bianchi
Elisa Crovato
Gianluca Trifirò
author_facet Silvia Adami
Cosetta Bianchi
Elisa Crovato
Gianluca Trifirò
author_sort Silvia Adami
collection DOAJ
description Introduction: Real-World Data (RWD) are data relating to patient health status and/or the delivery of health care routinely collected from a variety of sources such as Electronic Health Records (EHRs), data from product and disease Registries, patient generated data, etc. Real-World Evidence (RWE) is the clinical evidence about the usage and potential benefits and/or risks of a medical product derived from the analysis of Real-World Data. This document illustrates the results of a discussion of a multi-disciplinary expert Panel on the role of RWE with specific regard to both the post-marketing (re)evaluation of the benefit-risk profile of drugs in the real-world setting and the management of uncertainty about efficacy and safety at the time of their marketing, through Managed Entry Agreements (MEAs). Method: The debate took place during the 7th edition of the Seminari di Mogliano Veneto, attended by experts working in different organizations. Results: The experts have emphasized the need (i) to introduce outcome-based MEA for drugs with high uncertainty in outcomes and a high impact on spending, (ii) to evaluate the opportunity to define any secondary objectives in order to be able to carry out additional evaluations when establishing a new Registry, and (iii) to use other data sources through linkage and interoperability of the information systems involved (e.g., administrative databases, disease Registries). The Panel also agreed on a general need to define guidelines at national level on how to generate RWE to support the various regulatory processes including evaluation for the purposes of applying MEA and price renegotiation.
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spelling doaj-art-ba57e2ac7ef1423282d30bd4f09f7f8a2025-08-20T03:50:16ZengAboutScience SrlGlobal & Regional Health Technology Assessment2284-24032283-57332025-07-0112110.33393/grhta.2025.3563Real-World Evidence and Managed Entry AgreementsSilvia Adami0Cosetta Bianchi1Elisa Crovato2Gianluca Trifirò3Direzione Farmaceutico-Protesica-Dispositivi Medici, Regione del Veneto - ItalyDephaforum s.r.l., Milano - ItalyMarket Access Chiesi, Parma - ItalyDipartimento di Diagnostica e Sanità Pubblica, Università degli Studi di Verona, Verona - Italy Introduction: Real-World Data (RWD) are data relating to patient health status and/or the delivery of health care routinely collected from a variety of sources such as Electronic Health Records (EHRs), data from product and disease Registries, patient generated data, etc. Real-World Evidence (RWE) is the clinical evidence about the usage and potential benefits and/or risks of a medical product derived from the analysis of Real-World Data. This document illustrates the results of a discussion of a multi-disciplinary expert Panel on the role of RWE with specific regard to both the post-marketing (re)evaluation of the benefit-risk profile of drugs in the real-world setting and the management of uncertainty about efficacy and safety at the time of their marketing, through Managed Entry Agreements (MEAs). Method: The debate took place during the 7th edition of the Seminari di Mogliano Veneto, attended by experts working in different organizations. Results: The experts have emphasized the need (i) to introduce outcome-based MEA for drugs with high uncertainty in outcomes and a high impact on spending, (ii) to evaluate the opportunity to define any secondary objectives in order to be able to carry out additional evaluations when establishing a new Registry, and (iii) to use other data sources through linkage and interoperability of the information systems involved (e.g., administrative databases, disease Registries). The Panel also agreed on a general need to define guidelines at national level on how to generate RWE to support the various regulatory processes including evaluation for the purposes of applying MEA and price renegotiation. https://journals.aboutscience.eu/index.php/grhta/article/view/3563Managed Entry AgreementsReal-World DataReal-World EvidenceRegistry
spellingShingle Silvia Adami
Cosetta Bianchi
Elisa Crovato
Gianluca Trifirò
Real-World Evidence and Managed Entry Agreements
Global & Regional Health Technology Assessment
Managed Entry Agreements
Real-World Data
Real-World Evidence
Registry
title Real-World Evidence and Managed Entry Agreements
title_full Real-World Evidence and Managed Entry Agreements
title_fullStr Real-World Evidence and Managed Entry Agreements
title_full_unstemmed Real-World Evidence and Managed Entry Agreements
title_short Real-World Evidence and Managed Entry Agreements
title_sort real world evidence and managed entry agreements
topic Managed Entry Agreements
Real-World Data
Real-World Evidence
Registry
url https://journals.aboutscience.eu/index.php/grhta/article/view/3563
work_keys_str_mv AT silviaadami realworldevidenceandmanagedentryagreements
AT cosettabianchi realworldevidenceandmanagedentryagreements
AT elisacrovato realworldevidenceandmanagedentryagreements
AT gianlucatrifiro realworldevidenceandmanagedentryagreements