Silent but significant: Functional elucidation of a synonymous ATP7B mutation in Wilson’s disease pedigrees

IntroductionWilson’s disease (hepatolenticular degeneration) is a common hereditary neurological disorder. Early diagnosis, particularly the widespread implementation of genetic testing and timely intervention, is crucial for improving the prognosis of this disease. However, limited data exist on ge...

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Bibliographic Details
Main Authors: Qi Zhang, Xiaoming Xie, Hairong Li, Yulei Li, Hongyao Huang
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-06-01
Series:Frontiers in Genetics
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Online Access:https://www.frontiersin.org/articles/10.3389/fgene.2025.1604683/full
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