O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 study

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Main Authors: Ravi Savarirayan, Elena Muslimova, Josep Bergua, Paul Arundel, Jean Salles, Vrinda Saraff, Borja Delgado, Antonio Leiva-Gea, Helen McDevitt, Marc Nicolino, Massimiliano Rossi, Maria Salcedo, Valerie Cormier-Daire, Mars Skael, Peter Kannu, John Phillips, Howard Saal, Paul Harmatz, Toby Candler, Richard Weng, Yun Bai, Supriya Raj, Julie Hoover-Fong, Melita Irving, Daniela Rogoff
Format: Article
Language:English
Published: Elsevier 2025-01-01
Series:Genetics in Medicine Open
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774425001281
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author Ravi Savarirayan
Elena Muslimova
Josep Bergua
Paul Arundel
Jean Salles
Vrinda Saraff
Borja Delgado
Antonio Leiva-Gea
Helen McDevitt
Marc Nicolino
Massimiliano Rossi
Maria Salcedo
Valerie Cormier-Daire
Mars Skael
Peter Kannu
John Phillips
Howard Saal
Paul Harmatz
Toby Candler
Richard Weng
Yun Bai
Supriya Raj
Julie Hoover-Fong
Melita Irving
Daniela Rogoff
author_facet Ravi Savarirayan
Elena Muslimova
Josep Bergua
Paul Arundel
Jean Salles
Vrinda Saraff
Borja Delgado
Antonio Leiva-Gea
Helen McDevitt
Marc Nicolino
Massimiliano Rossi
Maria Salcedo
Valerie Cormier-Daire
Mars Skael
Peter Kannu
John Phillips
Howard Saal
Paul Harmatz
Toby Candler
Richard Weng
Yun Bai
Supriya Raj
Julie Hoover-Fong
Melita Irving
Daniela Rogoff
author_sort Ravi Savarirayan
collection DOAJ
format Article
id doaj-art-b4f5cc626b4a4c478f664f88a1a2d595
institution DOAJ
issn 2949-7744
language English
publishDate 2025-01-01
publisher Elsevier
record_format Article
series Genetics in Medicine Open
spelling doaj-art-b4f5cc626b4a4c478f664f88a1a2d5952025-08-20T03:14:31ZengElsevierGenetics in Medicine Open2949-77442025-01-01310208910.1016/j.gimo.2025.102089O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 studyRavi Savarirayan0Elena Muslimova1Josep Bergua2Paul Arundel3Jean Salles4Vrinda Saraff5Borja Delgado6Antonio Leiva-Gea7Helen McDevitt8Marc Nicolino9Massimiliano Rossi10Maria Salcedo11Valerie Cormier-Daire12Mars Skael13Peter Kannu14John Phillips15Howard Saal16Paul Harmatz17Toby Candler18Richard Weng19Yun Bai20Supriya Raj21Julie Hoover-Fong22Melita Irving23Daniela Rogoff24Murdoch Children’s Research Institute, Melbourne, AustraliaBridgeBio Pharma, San Francisco, CAHospital Vithas San José, Vitoria-Gasteiz, SpainSheffield Children’s NHS Foundation Trust, Sheffield, UKHôpital des Enfants – Toulouse, Toulouse, FranceBirmingham Women’s and Children’s NHS Foundation Trust, Birmingham, UKHospital Universitario Virgen de la Victoria, Malaga, SpainHospital Universitario Virgen de la Victoria, Malaga, SpainNHS Greater Glasgow and Clyde, Glasgow, UKHôpital Femme Mère Enfant, Hospices Civils de Lyon, Lyon, FranceHôpital Femme Mère Enfant, Hospices Civils de Lyon, Lyon, FranceHospital Universitario La Paz, Madrid, SpainHôpital Necker-Enfants Malades, Paris, FranceManchester University NHS Foundation Trust, Manchester, UKUniversity of Alberta – Stollery Children’s Hospital, Edmonton, CanadaVanderbilt University Medical Center, Nashville, TN15Cincinnati Children’s Hospital Medical Center, Cincinnati, OHBenioff Children’s Hospital Oakland, Oakland, CAUniversity Hospitals Bristol and Weston NHS Foundation Trust, Bristol, UKBridgeBio Pharma, San Francisco, CABridgeBio Pharma, San Francisco, CAMurdoch Children’s Research Institute, Melbourne, AustraliaJohns Hopkins, Department of PediatricsGuy’s and St Thomas’ NHS Foundation Trust, London, UKBridgeBio Pharma, San Francisco, CAhttp://www.sciencedirect.com/science/article/pii/S2949774425001281
spellingShingle Ravi Savarirayan
Elena Muslimova
Josep Bergua
Paul Arundel
Jean Salles
Vrinda Saraff
Borja Delgado
Antonio Leiva-Gea
Helen McDevitt
Marc Nicolino
Massimiliano Rossi
Maria Salcedo
Valerie Cormier-Daire
Mars Skael
Peter Kannu
John Phillips
Howard Saal
Paul Harmatz
Toby Candler
Richard Weng
Yun Bai
Supriya Raj
Julie Hoover-Fong
Melita Irving
Daniela Rogoff
O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 study
Genetics in Medicine Open
title O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 study
title_full O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 study
title_fullStr O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 study
title_full_unstemmed O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 study
title_short O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 study
title_sort o13 oral infigratinib for children with achondroplasia month 18 results from the propel 2 study
url http://www.sciencedirect.com/science/article/pii/S2949774425001281
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