Similar burden of rare genetic variants in ischemic and non-ischemic dilated cardiomyopathy

BackgroundThe aim of the study was to determine the prevalence of rare disease-causing variants in cardiomyopathy-associated genes in a cohort of patients with ischemic and non-ischemic dilated cardiomyopathy undergoing heart transplant.MethodsWe conducted a single-center cohort study of 60 adult pa...

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Main Authors: Louie Cao, Joshua Rushakoff, Ian Williamson, Anja Karlstaedt, Michelle Kittleson, Lawrence Czer, Evan P. Kransdorf
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-04-01
Series:Frontiers in Cardiovascular Medicine
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Online Access:https://www.frontiersin.org/articles/10.3389/fcvm.2025.1542653/full
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author Louie Cao
Joshua Rushakoff
Ian Williamson
Anja Karlstaedt
Michelle Kittleson
Lawrence Czer
Evan P. Kransdorf
author_facet Louie Cao
Joshua Rushakoff
Ian Williamson
Anja Karlstaedt
Michelle Kittleson
Lawrence Czer
Evan P. Kransdorf
author_sort Louie Cao
collection DOAJ
description BackgroundThe aim of the study was to determine the prevalence of rare disease-causing variants in cardiomyopathy-associated genes in a cohort of patients with ischemic and non-ischemic dilated cardiomyopathy undergoing heart transplant.MethodsWe conducted a single-center cohort study of 60 adult patients with left ventricular ejection fraction ≤50% and left ventricular end-diastolic dimension ≥95th percentile for sex/height who underwent heart transplant between January 2017 and December 2023 and consented to participate in a cardiac tissue biobank. We evaluated the prevalence of rare (minor allele frequency <0.1%) disease-causing (pathogenic or likely pathogenic by American College of Genetics and Genomics criteria) variants in cardiomyopathy-associated genes.ResultsA total of 60 individuals fulfilled the inclusion criteria: 16 with ischemic dilated cardiomyopathy [88% men, median age 65 years, interquartile range (IQR) 64–68 years] and 44 with non-ischemic dilated cardiomyopathy (80% men, median age 53 years, IQR 39–65 years). We found that the prevalence of disease-causing variants was similar between patients with ischemic dilated cardiomyopathy (3/16 or 19%; 95% credible interval 6%–36%) and those with non-ischemic dilated cardiomyopathy (10/44 or 23%; 95% credible interval 12%–33%). Variants in the ischemic dilated cardiomyopathy group were found in the TTN and DMD genes. Variants in the non-ischemic dilated cardiomyopathy group were found in the TTN, FLNC, LMNA, MYH7, and RBM20 genes.ConclusionsPatients with ischemic dilated cardiomyopathy undergoing heart transplant possessed a similar burden of rare disease-causing variants as those with non-ischemic dilated cardiomyopathy. Our results suggest that genetic testing may be beneficial in patients with advanced heart failure requiring heart transplant due to ischemic dilated cardiomyopathy to detect disease-causing variants in cardiomyopathy-associated genes.
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spelling doaj-art-b401979a7e8042d6b067eb8aac8e71482025-08-20T03:53:27ZengFrontiers Media S.A.Frontiers in Cardiovascular Medicine2297-055X2025-04-011210.3389/fcvm.2025.15426531542653Similar burden of rare genetic variants in ischemic and non-ischemic dilated cardiomyopathyLouie CaoJoshua RushakoffIan WilliamsonAnja KarlstaedtMichelle KittlesonLawrence CzerEvan P. KransdorfBackgroundThe aim of the study was to determine the prevalence of rare disease-causing variants in cardiomyopathy-associated genes in a cohort of patients with ischemic and non-ischemic dilated cardiomyopathy undergoing heart transplant.MethodsWe conducted a single-center cohort study of 60 adult patients with left ventricular ejection fraction ≤50% and left ventricular end-diastolic dimension ≥95th percentile for sex/height who underwent heart transplant between January 2017 and December 2023 and consented to participate in a cardiac tissue biobank. We evaluated the prevalence of rare (minor allele frequency <0.1%) disease-causing (pathogenic or likely pathogenic by American College of Genetics and Genomics criteria) variants in cardiomyopathy-associated genes.ResultsA total of 60 individuals fulfilled the inclusion criteria: 16 with ischemic dilated cardiomyopathy [88% men, median age 65 years, interquartile range (IQR) 64–68 years] and 44 with non-ischemic dilated cardiomyopathy (80% men, median age 53 years, IQR 39–65 years). We found that the prevalence of disease-causing variants was similar between patients with ischemic dilated cardiomyopathy (3/16 or 19%; 95% credible interval 6%–36%) and those with non-ischemic dilated cardiomyopathy (10/44 or 23%; 95% credible interval 12%–33%). Variants in the ischemic dilated cardiomyopathy group were found in the TTN and DMD genes. Variants in the non-ischemic dilated cardiomyopathy group were found in the TTN, FLNC, LMNA, MYH7, and RBM20 genes.ConclusionsPatients with ischemic dilated cardiomyopathy undergoing heart transplant possessed a similar burden of rare disease-causing variants as those with non-ischemic dilated cardiomyopathy. Our results suggest that genetic testing may be beneficial in patients with advanced heart failure requiring heart transplant due to ischemic dilated cardiomyopathy to detect disease-causing variants in cardiomyopathy-associated genes.https://www.frontiersin.org/articles/10.3389/fcvm.2025.1542653/fullischemic cardiomyopathydilated cardiomyopathyheart transplantationgenetic testingischemic dilated cardiomyopathy
spellingShingle Louie Cao
Joshua Rushakoff
Ian Williamson
Anja Karlstaedt
Michelle Kittleson
Lawrence Czer
Evan P. Kransdorf
Similar burden of rare genetic variants in ischemic and non-ischemic dilated cardiomyopathy
Frontiers in Cardiovascular Medicine
ischemic cardiomyopathy
dilated cardiomyopathy
heart transplantation
genetic testing
ischemic dilated cardiomyopathy
title Similar burden of rare genetic variants in ischemic and non-ischemic dilated cardiomyopathy
title_full Similar burden of rare genetic variants in ischemic and non-ischemic dilated cardiomyopathy
title_fullStr Similar burden of rare genetic variants in ischemic and non-ischemic dilated cardiomyopathy
title_full_unstemmed Similar burden of rare genetic variants in ischemic and non-ischemic dilated cardiomyopathy
title_short Similar burden of rare genetic variants in ischemic and non-ischemic dilated cardiomyopathy
title_sort similar burden of rare genetic variants in ischemic and non ischemic dilated cardiomyopathy
topic ischemic cardiomyopathy
dilated cardiomyopathy
heart transplantation
genetic testing
ischemic dilated cardiomyopathy
url https://www.frontiersin.org/articles/10.3389/fcvm.2025.1542653/full
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