Neonatal form of biotin-thiamine-responsive basal ganglia disease. Clues to diagnosis

Biotin-thiamine-responsive basal ganglia disease is characterized by seizures, dystonia and encephalopathy attacks, with an acute-subacute onset in childhood. It causes cerebral damage especially with caudate head and putamen involvement and may lead to severe sequelae and even death if left untrea...

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Main Authors: Aydan Değerliyurt, Mehmet Gündüz, Serdar Ceylaner, Özlem Ünal, Sevim Ünal
Format: Article
Language:English
Published: Hacettepe University Institute of Child Health 2019-04-01
Series:The Turkish Journal of Pediatrics
Subjects:
Online Access:https://turkjpediatr.org/article/view/683
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author Aydan Değerliyurt
Mehmet Gündüz
Serdar Ceylaner
Özlem Ünal
Sevim Ünal
author_facet Aydan Değerliyurt
Mehmet Gündüz
Serdar Ceylaner
Özlem Ünal
Sevim Ünal
author_sort Aydan Değerliyurt
collection DOAJ
description Biotin-thiamine-responsive basal ganglia disease is characterized by seizures, dystonia and encephalopathy attacks, with an acute-subacute onset in childhood. It causes cerebral damage especially with caudate head and putamen involvement and may lead to severe sequelae and even death if left untreated. We report a patient with the neonatal form of biotin-thiamine-responsive basal ganglia disease who presented with encephalopathy and lactic acidosis in the neonatal period together with the diagnostic magnetic resonance imaging (MRI) clues. MRI in the neonatal period revealed bilateral involvement of the putamen, thalamus, and perirolandic cortical regions. However, MRI obtained at 32 months revealed involvement of the caudate nuclei in addition to the putamen and thalami. The neuroimaging findings of our patient and relevant literature indicate that patients with biotin-thiamine-responsive basal ganglia disease who are symptomatic in the neonatal period have putamen, thalami, and perirolandic cortical involvement. However, these patients do not have caudate involvement, unlike the patients who present in childhood.
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publishDate 2019-04-01
publisher Hacettepe University Institute of Child Health
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series The Turkish Journal of Pediatrics
spelling doaj-art-b377de3d35c546e6bd3971141fa9e6412025-08-20T03:16:22ZengHacettepe University Institute of Child HealthThe Turkish Journal of Pediatrics0041-43012791-64212019-04-0161210.24953/turkjped.2019.02.016Neonatal form of biotin-thiamine-responsive basal ganglia disease. Clues to diagnosisAydan Değerliyurt0Mehmet Gündüz1Serdar Ceylaner2Özlem Ünal3Sevim Ünal4Departments of Pediatric Neurology, Ankara Pediatrics, Hematology- Oncology Training and Research Hospital.Pediatric Metabolism and Nutrition, Ankara Pediatrics, Hematology- Oncology Training and Research Hospital.Intergen Genetics Centre, Ankara, Turkey.Pediatric Metabolism and Nutrition, Ankara Pediatrics, Hematology- Oncology Training and Research Hospital.Departments of Neonatology, Ankara Pediatrics, Hematology- Oncology Training and Research Hospital. Biotin-thiamine-responsive basal ganglia disease is characterized by seizures, dystonia and encephalopathy attacks, with an acute-subacute onset in childhood. It causes cerebral damage especially with caudate head and putamen involvement and may lead to severe sequelae and even death if left untreated. We report a patient with the neonatal form of biotin-thiamine-responsive basal ganglia disease who presented with encephalopathy and lactic acidosis in the neonatal period together with the diagnostic magnetic resonance imaging (MRI) clues. MRI in the neonatal period revealed bilateral involvement of the putamen, thalamus, and perirolandic cortical regions. However, MRI obtained at 32 months revealed involvement of the caudate nuclei in addition to the putamen and thalami. The neuroimaging findings of our patient and relevant literature indicate that patients with biotin-thiamine-responsive basal ganglia disease who are symptomatic in the neonatal period have putamen, thalami, and perirolandic cortical involvement. However, these patients do not have caudate involvement, unlike the patients who present in childhood. https://turkjpediatr.org/article/view/683Leigh syndromeSLC19A3basal gangliabiotin-thiamine-responsive basal ganglia diseasethiamine transporter 2
spellingShingle Aydan Değerliyurt
Mehmet Gündüz
Serdar Ceylaner
Özlem Ünal
Sevim Ünal
Neonatal form of biotin-thiamine-responsive basal ganglia disease. Clues to diagnosis
The Turkish Journal of Pediatrics
Leigh syndrome
SLC19A3
basal ganglia
biotin-thiamine-responsive basal ganglia disease
thiamine transporter 2
title Neonatal form of biotin-thiamine-responsive basal ganglia disease. Clues to diagnosis
title_full Neonatal form of biotin-thiamine-responsive basal ganglia disease. Clues to diagnosis
title_fullStr Neonatal form of biotin-thiamine-responsive basal ganglia disease. Clues to diagnosis
title_full_unstemmed Neonatal form of biotin-thiamine-responsive basal ganglia disease. Clues to diagnosis
title_short Neonatal form of biotin-thiamine-responsive basal ganglia disease. Clues to diagnosis
title_sort neonatal form of biotin thiamine responsive basal ganglia disease clues to diagnosis
topic Leigh syndrome
SLC19A3
basal ganglia
biotin-thiamine-responsive basal ganglia disease
thiamine transporter 2
url https://turkjpediatr.org/article/view/683
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