m276-SL-PBD eradicates tumors and instigates long-lasting tumor-free survival in Merkel cell carcinoma preclinical models

Summary: Merkel cell carcinoma (MCC) is a rare but aggressive neuroendocrine carcinoma, and immune checkpoint inhibitors (ICIs) are the only approved therapy; nonetheless, resistance is notable and there is a critical need for novel effective therapies. Recently, CD276 was identified as a promising...

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Main Authors: Mikaela D. Kunika, Aarthi Kannan, Graham J. Velasco, Yang Feng, Steven Seaman, Bhaba K. Das, Dillon Pham, Nils Lambrecht, Haibo Zhao, Brad St. Croix, Ling Gao
Format: Article
Language:English
Published: Elsevier 2025-05-01
Series:iScience
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Online Access:http://www.sciencedirect.com/science/article/pii/S2589004225006972
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author Mikaela D. Kunika
Aarthi Kannan
Graham J. Velasco
Yang Feng
Steven Seaman
Bhaba K. Das
Dillon Pham
Nils Lambrecht
Haibo Zhao
Brad St. Croix
Ling Gao
author_facet Mikaela D. Kunika
Aarthi Kannan
Graham J. Velasco
Yang Feng
Steven Seaman
Bhaba K. Das
Dillon Pham
Nils Lambrecht
Haibo Zhao
Brad St. Croix
Ling Gao
author_sort Mikaela D. Kunika
collection DOAJ
description Summary: Merkel cell carcinoma (MCC) is a rare but aggressive neuroendocrine carcinoma, and immune checkpoint inhibitors (ICIs) are the only approved therapy; nonetheless, resistance is notable and there is a critical need for novel effective therapies. Recently, CD276 was identified as a promising therapeutic target in human cancers. In preclinical studies, a modified CD276 antibody-drug conjugate (ADC) with pyrrolobenzodiazepine (m276-SL-PBD) elicited more potent anti-tumor effects than two CD276 ADCs currently in clinical trials. Here, we uncover notable CD276 expression in MCC patient tumors, and demonstrate m276-SL-PBD efficacy against MCC preclinical models. Complete eradication is observed in all xenografts bearing CD276 expression, with 82% achieving 180-day tumor-free survival after 4 or 5 weekly doses, and m276-SL-PBD remained efficacious against relapsed tumors. Of clinical relevance, m276-SL-PBD retains its potency in MCC-bearing humanized mice. Importantly, no detectable adverse effects were observed. Thus, m276-SL-PBD is a promising therapy for patients unsuitable or resistant to ICIs.
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spelling doaj-art-b143e85567dc4dce82f54c13ed7e3f8e2025-08-20T01:55:59ZengElsevieriScience2589-00422025-05-0128511243610.1016/j.isci.2025.112436m276-SL-PBD eradicates tumors and instigates long-lasting tumor-free survival in Merkel cell carcinoma preclinical modelsMikaela D. Kunika0Aarthi Kannan1Graham J. Velasco2Yang Feng3Steven Seaman4Bhaba K. Das5Dillon Pham6Nils Lambrecht7Haibo Zhao8Brad St. Croix9Ling Gao10Southern California Institute for Research and Education, Long Beach, CA 90822, USASouthern California Institute for Research and Education, Long Beach, CA 90822, USA; Department of Dermatology, University of California-Irvine, Irvine, CA 92697, USAPathology Department, Tibor Rubin VA Medical Center, VA Long Beach Healthcare System, Long Beach, CA 90822, USATumor Angiogenesis Unit, Mouse Cancer Genetics Program (MCGP), National Cancer Institute (NCI), NIH, Frederick, MD 21702, USATumor Angiogenesis Unit, Mouse Cancer Genetics Program (MCGP), National Cancer Institute (NCI), NIH, Frederick, MD 21702, USASouthern California Institute for Research and Education, Long Beach, CA 90822, USASouthern California Institute for Research and Education, Long Beach, CA 90822, USAPathology Department, Tibor Rubin VA Medical Center, VA Long Beach Healthcare System, Long Beach, CA 90822, USASouthern California Institute for Research and Education, Long Beach, CA 90822, USATumor Angiogenesis Unit, Mouse Cancer Genetics Program (MCGP), National Cancer Institute (NCI), NIH, Frederick, MD 21702, USASouthern California Institute for Research and Education, Long Beach, CA 90822, USA; Department of Dermatology, University of California-Irvine, Irvine, CA 92697, USA; Dermatology Section, Tibor Rubin VA Medical Center, VA Long Beach Healthcare System, Long Beach, CA 90822, USA; Corresponding authorSummary: Merkel cell carcinoma (MCC) is a rare but aggressive neuroendocrine carcinoma, and immune checkpoint inhibitors (ICIs) are the only approved therapy; nonetheless, resistance is notable and there is a critical need for novel effective therapies. Recently, CD276 was identified as a promising therapeutic target in human cancers. In preclinical studies, a modified CD276 antibody-drug conjugate (ADC) with pyrrolobenzodiazepine (m276-SL-PBD) elicited more potent anti-tumor effects than two CD276 ADCs currently in clinical trials. Here, we uncover notable CD276 expression in MCC patient tumors, and demonstrate m276-SL-PBD efficacy against MCC preclinical models. Complete eradication is observed in all xenografts bearing CD276 expression, with 82% achieving 180-day tumor-free survival after 4 or 5 weekly doses, and m276-SL-PBD remained efficacious against relapsed tumors. Of clinical relevance, m276-SL-PBD retains its potency in MCC-bearing humanized mice. Importantly, no detectable adverse effects were observed. Thus, m276-SL-PBD is a promising therapy for patients unsuitable or resistant to ICIs.http://www.sciencedirect.com/science/article/pii/S2589004225006972therapeutic procedurebiotechnologycancer
spellingShingle Mikaela D. Kunika
Aarthi Kannan
Graham J. Velasco
Yang Feng
Steven Seaman
Bhaba K. Das
Dillon Pham
Nils Lambrecht
Haibo Zhao
Brad St. Croix
Ling Gao
m276-SL-PBD eradicates tumors and instigates long-lasting tumor-free survival in Merkel cell carcinoma preclinical models
iScience
therapeutic procedure
biotechnology
cancer
title m276-SL-PBD eradicates tumors and instigates long-lasting tumor-free survival in Merkel cell carcinoma preclinical models
title_full m276-SL-PBD eradicates tumors and instigates long-lasting tumor-free survival in Merkel cell carcinoma preclinical models
title_fullStr m276-SL-PBD eradicates tumors and instigates long-lasting tumor-free survival in Merkel cell carcinoma preclinical models
title_full_unstemmed m276-SL-PBD eradicates tumors and instigates long-lasting tumor-free survival in Merkel cell carcinoma preclinical models
title_short m276-SL-PBD eradicates tumors and instigates long-lasting tumor-free survival in Merkel cell carcinoma preclinical models
title_sort m276 sl pbd eradicates tumors and instigates long lasting tumor free survival in merkel cell carcinoma preclinical models
topic therapeutic procedure
biotechnology
cancer
url http://www.sciencedirect.com/science/article/pii/S2589004225006972
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