Conventional and advanced MR imaging in infantile Refsum disease

We report magnetic resonance (MR) imaging findings including diffusion-weighted imaging and proton MR spectroscopy findings in a patient with infantile Refsum disease. The initial diagnosis was made on the basis of history, clinical findings and biochemical studies. Bilateral and symmetrical...

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Main Authors: Mustafa Kılıç, Kader Karlı-Oğuz, Göknur Haliloğlu, Meral Topçu, Ronald James Wanders, Turgay Coşkun
Format: Article
Language:English
Published: Hacettepe University Institute of Child Health 2015-06-01
Series:The Turkish Journal of Pediatrics
Online Access:https://turkjpediatr.org/article/view/1241
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author Mustafa Kılıç
Kader Karlı-Oğuz
Göknur Haliloğlu
Meral Topçu
Ronald James Wanders
Turgay Coşkun
author_facet Mustafa Kılıç
Kader Karlı-Oğuz
Göknur Haliloğlu
Meral Topçu
Ronald James Wanders
Turgay Coşkun
author_sort Mustafa Kılıç
collection DOAJ
description We report magnetic resonance (MR) imaging findings including diffusion-weighted imaging and proton MR spectroscopy findings in a patient with infantile Refsum disease. The initial diagnosis was made on the basis of history, clinical findings and biochemical studies. Bilateral and symmetrical involvement of the peritrigonal white matter, centrum semiovale, thalami, corpus callosum and corticospinal tracts as assessed by increased T2 signal was highly suggestive of a peroxisomal disorder. Facilitated diffusion was observed in diseased parenchyma. Long echo-time (TE: 270 ms) MRS showed decreased N-acetyl-aspartate/creatine and elevated choline/creatine and lactate; short echo-time MRS (TE: 30 ms) revealed increased myoinositol at 3.56 ppm and lipid peaks at 0.9 and 1.3 ppm. A major contribution to the differential diagnosis came from MR imaging and proton MRS, as discussed in this report.
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id doaj-art-b0de8a48224e489ab88f66d7dc9bf176
institution DOAJ
issn 0041-4301
2791-6421
language English
publishDate 2015-06-01
publisher Hacettepe University Institute of Child Health
record_format Article
series The Turkish Journal of Pediatrics
spelling doaj-art-b0de8a48224e489ab88f66d7dc9bf1762025-08-20T02:55:41ZengHacettepe University Institute of Child HealthThe Turkish Journal of Pediatrics0041-43012791-64212015-06-01573Conventional and advanced MR imaging in infantile Refsum diseaseMustafa Kılıç0Kader Karlı-OğuzGöknur HaliloğluMeral TopçuRonald James WandersTurgay CoşkunDivisions of Pediatric Nutrition and Metabolism, Department of Pediatrics, Hacettepe University Faculty of Medicine, Ankara, Turkey. kilickorkmaz@yahoo.com.tr. We report magnetic resonance (MR) imaging findings including diffusion-weighted imaging and proton MR spectroscopy findings in a patient with infantile Refsum disease. The initial diagnosis was made on the basis of history, clinical findings and biochemical studies. Bilateral and symmetrical involvement of the peritrigonal white matter, centrum semiovale, thalami, corpus callosum and corticospinal tracts as assessed by increased T2 signal was highly suggestive of a peroxisomal disorder. Facilitated diffusion was observed in diseased parenchyma. Long echo-time (TE: 270 ms) MRS showed decreased N-acetyl-aspartate/creatine and elevated choline/creatine and lactate; short echo-time MRS (TE: 30 ms) revealed increased myoinositol at 3.56 ppm and lipid peaks at 0.9 and 1.3 ppm. A major contribution to the differential diagnosis came from MR imaging and proton MRS, as discussed in this report. https://turkjpediatr.org/article/view/1241
spellingShingle Mustafa Kılıç
Kader Karlı-Oğuz
Göknur Haliloğlu
Meral Topçu
Ronald James Wanders
Turgay Coşkun
Conventional and advanced MR imaging in infantile Refsum disease
The Turkish Journal of Pediatrics
title Conventional and advanced MR imaging in infantile Refsum disease
title_full Conventional and advanced MR imaging in infantile Refsum disease
title_fullStr Conventional and advanced MR imaging in infantile Refsum disease
title_full_unstemmed Conventional and advanced MR imaging in infantile Refsum disease
title_short Conventional and advanced MR imaging in infantile Refsum disease
title_sort conventional and advanced mr imaging in infantile refsum disease
url https://turkjpediatr.org/article/view/1241
work_keys_str_mv AT mustafakılıc conventionalandadvancedmrimagingininfantilerefsumdisease
AT kaderkarlıoguz conventionalandadvancedmrimagingininfantilerefsumdisease
AT goknurhaliloglu conventionalandadvancedmrimagingininfantilerefsumdisease
AT meraltopcu conventionalandadvancedmrimagingininfantilerefsumdisease
AT ronaldjameswanders conventionalandadvancedmrimagingininfantilerefsumdisease
AT turgaycoskun conventionalandadvancedmrimagingininfantilerefsumdisease