Identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal disease

Abstract Identification of tissue‐specific renal stem/progenitor cells with nephrogenic potential is a critical step in developing cell‐based therapies for renal disease. In the human kidney, stem/progenitor cells are induced into the nephrogenic pathway to form nephrons until the 34 week of gestati...

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Main Authors: Orit Harari‐Steinberg, Sally Metsuyanim, Dorit Omer, Yehudit Gnatek, Rotem Gershon, Sara Pri‐Chen, Derya D. Ozdemir, Yaniv Lerenthal, Tzahi Noiman, Herzel Ben‐Hur, Zvi Vaknin, David F. Schneider, Bruce J. Aronow, Ronald S. Goldstein, Peter Hohenstein, Benjamin Dekel
Format: Article
Language:English
Published: Springer Nature 2013-09-01
Series:EMBO Molecular Medicine
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Online Access:https://doi.org/10.1002/emmm.201201584
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author Orit Harari‐Steinberg
Sally Metsuyanim
Dorit Omer
Yehudit Gnatek
Rotem Gershon
Sara Pri‐Chen
Derya D. Ozdemir
Yaniv Lerenthal
Tzahi Noiman
Herzel Ben‐Hur
Zvi Vaknin
David F. Schneider
Bruce J. Aronow
Ronald S. Goldstein
Peter Hohenstein
Benjamin Dekel
author_facet Orit Harari‐Steinberg
Sally Metsuyanim
Dorit Omer
Yehudit Gnatek
Rotem Gershon
Sara Pri‐Chen
Derya D. Ozdemir
Yaniv Lerenthal
Tzahi Noiman
Herzel Ben‐Hur
Zvi Vaknin
David F. Schneider
Bruce J. Aronow
Ronald S. Goldstein
Peter Hohenstein
Benjamin Dekel
author_sort Orit Harari‐Steinberg
collection DOAJ
description Abstract Identification of tissue‐specific renal stem/progenitor cells with nephrogenic potential is a critical step in developing cell‐based therapies for renal disease. In the human kidney, stem/progenitor cells are induced into the nephrogenic pathway to form nephrons until the 34 week of gestation, and no equivalent cell types can be traced in the adult kidney. Human nephron progenitor cells (hNPCs) have yet to be isolated. Here we show that growth of human foetal kidneys in serum‐free defined conditions and prospective isolation of NCAM1+ cells selects for nephron lineage that includes the SIX2‐positive cap mesenchyme cells identifying a mitotically active population with in vitro clonogenic and stem/progenitor properties. After transplantation in the chick embryo, these cells—but not differentiated counterparts—efficiently formed various nephron tubule types. hNPCs engrafted and integrated in diseased murine kidneys and treatment of renal failure in the 5/6 nephrectomy kidney injury model had beneficial effects on renal function halting disease progression. These findings constitute the first definition of an intrinsic nephron precursor population, with major potential for cell‐based therapeutic strategies and modelling of kidney disease.
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spelling doaj-art-b0a80b1c58cc4d72bc2064b920df87ed2025-08-20T02:11:29ZengSpringer NatureEMBO Molecular Medicine1757-46761757-46842013-09-015101556156810.1002/emmm.201201584Identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal diseaseOrit Harari‐Steinberg0Sally Metsuyanim1Dorit Omer2Yehudit Gnatek3Rotem Gershon4Sara Pri‐Chen5Derya D. Ozdemir6Yaniv Lerenthal7Tzahi Noiman8Herzel Ben‐Hur9Zvi Vaknin10David F. Schneider11Bruce J. Aronow12Ronald S. Goldstein13Peter Hohenstein14Benjamin Dekel15The Pediatric Stem Cell Research Institute, Edmond and Lily Safra Children's Hospital, Sheba Center for Regenerative Medicine, Sheba Medical CenterThe Pediatric Stem Cell Research Institute, Edmond and Lily Safra Children's Hospital, Sheba Center for Regenerative Medicine, Sheba Medical CenterThe Pediatric Stem Cell Research Institute, Edmond and Lily Safra Children's Hospital, Sheba Center for Regenerative Medicine, Sheba Medical CenterThe Pediatric Stem Cell Research Institute, Edmond and Lily Safra Children's Hospital, Sheba Center for Regenerative Medicine, Sheba Medical CenterThe Pediatric Stem Cell Research Institute, Edmond and Lily Safra Children's Hospital, Sheba Center for Regenerative Medicine, Sheba Medical CenterThe Pediatric Stem Cell Research Institute, Edmond and Lily Safra Children's Hospital, Sheba Center for Regenerative Medicine, Sheba Medical CenterThe Roslin Institute, University of Edinburgh, Easter Bush CampusCancer Research Center, Sheba Medical CenterMina and Everard Goodman Faculty of Life Sciences, Bar‐IlanUniversityL.E.M. Laboratory of Early DetectionDepartment of Obstet and Gynecology, Assaf HarofehDepartment of Obstet and Gynecology, Assaf HarofehDivision of Molecular and Developmental Biology, Department of Pediatrics, University of Cincinnati, Childrens Hospital Medical CenterMina and Everard Goodman Faculty of Life Sciences, Bar‐IlanUniversityThe Roslin Institute, University of Edinburgh, Easter Bush CampusThe Pediatric Stem Cell Research Institute, Edmond and Lily Safra Children's Hospital, Sheba Center for Regenerative Medicine, Sheba Medical CenterAbstract Identification of tissue‐specific renal stem/progenitor cells with nephrogenic potential is a critical step in developing cell‐based therapies for renal disease. In the human kidney, stem/progenitor cells are induced into the nephrogenic pathway to form nephrons until the 34 week of gestation, and no equivalent cell types can be traced in the adult kidney. Human nephron progenitor cells (hNPCs) have yet to be isolated. Here we show that growth of human foetal kidneys in serum‐free defined conditions and prospective isolation of NCAM1+ cells selects for nephron lineage that includes the SIX2‐positive cap mesenchyme cells identifying a mitotically active population with in vitro clonogenic and stem/progenitor properties. After transplantation in the chick embryo, these cells—but not differentiated counterparts—efficiently formed various nephron tubule types. hNPCs engrafted and integrated in diseased murine kidneys and treatment of renal failure in the 5/6 nephrectomy kidney injury model had beneficial effects on renal function halting disease progression. These findings constitute the first definition of an intrinsic nephron precursor population, with major potential for cell‐based therapeutic strategies and modelling of kidney disease.https://doi.org/10.1002/emmm.201201584developmentkidney stem cellsprogenitor cellsregenerationstem cells
spellingShingle Orit Harari‐Steinberg
Sally Metsuyanim
Dorit Omer
Yehudit Gnatek
Rotem Gershon
Sara Pri‐Chen
Derya D. Ozdemir
Yaniv Lerenthal
Tzahi Noiman
Herzel Ben‐Hur
Zvi Vaknin
David F. Schneider
Bruce J. Aronow
Ronald S. Goldstein
Peter Hohenstein
Benjamin Dekel
Identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal disease
EMBO Molecular Medicine
development
kidney stem cells
progenitor cells
regeneration
stem cells
title Identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal disease
title_full Identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal disease
title_fullStr Identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal disease
title_full_unstemmed Identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal disease
title_short Identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal disease
title_sort identification of human nephron progenitors capable of generation of kidney structures and functional repair of chronic renal disease
topic development
kidney stem cells
progenitor cells
regeneration
stem cells
url https://doi.org/10.1002/emmm.201201584
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