The rapidly evolving view of lysosomal storage diseases
Abstract Lysosomal storage diseases are a group of metabolic disorders caused by deficiencies of several components of lysosomal function. Most commonly affected are lysosomal hydrolases, which are involved in the breakdown and recycling of a variety of complex molecules and cellular structures. The...
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| Main Authors: | Giancarlo Parenti, Diego L Medina, Andrea Ballabio |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
Springer Nature
2021-01-01
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| Series: | EMBO Molecular Medicine |
| Subjects: | |
| Online Access: | https://doi.org/10.15252/emmm.202012836 |
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