Targeted protein degradation by KLHDC2 ligands identified by high-throughput screening

Proteolysis-targeting chimeras (PROTACs) enable the selective and sub-stoichiometric elimination of pathological proteins, yet only two E3 ligases are routinely used for this purpose. Here, we expand the repertoire of PROTAC-compatible E3 ligases by identifying a novel small molecule scaffold target...

Full description

Saved in:
Bibliographic Details
Main Authors: Han Zhou, Tonglian Zhou, Wenli Yu, Liping Liu, Yeonjin Ko, Kristen A Johnson, Ian A Wilson, Peter G Schultz, Michael J Bollong
Format: Article
Language:English
Published: eLife Sciences Publications Ltd 2025-06-01
Series:eLife
Subjects:
Online Access:https://elifesciences.org/articles/106844
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849335437027442688
author Han Zhou
Tonglian Zhou
Wenli Yu
Liping Liu
Yeonjin Ko
Kristen A Johnson
Ian A Wilson
Peter G Schultz
Michael J Bollong
author_facet Han Zhou
Tonglian Zhou
Wenli Yu
Liping Liu
Yeonjin Ko
Kristen A Johnson
Ian A Wilson
Peter G Schultz
Michael J Bollong
author_sort Han Zhou
collection DOAJ
description Proteolysis-targeting chimeras (PROTACs) enable the selective and sub-stoichiometric elimination of pathological proteins, yet only two E3 ligases are routinely used for this purpose. Here, we expand the repertoire of PROTAC-compatible E3 ligases by identifying a novel small molecule scaffold targeting the ubiquitin E3 ligase KLHDC2 using a fluorescence polarization-based high-throughput screen. We highlight the utility of this ligand with the synthesis of PROTACs capable of potently degrading BRD4 in cells. This work affords additional chemical matter for targeting KLHDC2 and suggests a practical approach for identifying novel E3 binders by high-throughput screening.
format Article
id doaj-art-adffac5b7d8b4036a17ab14a91fc110c
institution Kabale University
issn 2050-084X
language English
publishDate 2025-06-01
publisher eLife Sciences Publications Ltd
record_format Article
series eLife
spelling doaj-art-adffac5b7d8b4036a17ab14a91fc110c2025-08-20T03:45:15ZengeLife Sciences Publications LtdeLife2050-084X2025-06-011410.7554/eLife.106844Targeted protein degradation by KLHDC2 ligands identified by high-throughput screeningHan Zhou0Tonglian Zhou1Wenli Yu2Liping Liu3Yeonjin Ko4Kristen A Johnson5Ian A Wilson6Peter G Schultz7Michael J Bollong8https://orcid.org/0000-0001-9439-1476Department of Chemistry, Scripps Research, La Jolla, United StatesDepartment of Chemistry, Scripps Research, La Jolla, United StatesDepartment of Integrative Structural and Computational Biology, Scripps Research, La Jolla, United StatesDepartment of Chemistry, Scripps Research, La Jolla, United StatesChemical & Biological Integrative Research Center, Korea Institute of Science and Technology, Seoul, Republic of KoreaDepartment of Biology, Calibr-Skaggs at Scripps Research, La Jolla, United StatesDepartment of Integrative Structural and Computational Biology, Scripps Research, La Jolla, United StatesDepartment of Chemistry, Scripps Research, La Jolla, United StatesDepartment of Chemistry, Scripps Research, La Jolla, United StatesProteolysis-targeting chimeras (PROTACs) enable the selective and sub-stoichiometric elimination of pathological proteins, yet only two E3 ligases are routinely used for this purpose. Here, we expand the repertoire of PROTAC-compatible E3 ligases by identifying a novel small molecule scaffold targeting the ubiquitin E3 ligase KLHDC2 using a fluorescence polarization-based high-throughput screen. We highlight the utility of this ligand with the synthesis of PROTACs capable of potently degrading BRD4 in cells. This work affords additional chemical matter for targeting KLHDC2 and suggests a practical approach for identifying novel E3 binders by high-throughput screening.https://elifesciences.org/articles/106844KLHDC2PROTACE3 ligasehigh-throughput screening
spellingShingle Han Zhou
Tonglian Zhou
Wenli Yu
Liping Liu
Yeonjin Ko
Kristen A Johnson
Ian A Wilson
Peter G Schultz
Michael J Bollong
Targeted protein degradation by KLHDC2 ligands identified by high-throughput screening
eLife
KLHDC2
PROTAC
E3 ligase
high-throughput screening
title Targeted protein degradation by KLHDC2 ligands identified by high-throughput screening
title_full Targeted protein degradation by KLHDC2 ligands identified by high-throughput screening
title_fullStr Targeted protein degradation by KLHDC2 ligands identified by high-throughput screening
title_full_unstemmed Targeted protein degradation by KLHDC2 ligands identified by high-throughput screening
title_short Targeted protein degradation by KLHDC2 ligands identified by high-throughput screening
title_sort targeted protein degradation by klhdc2 ligands identified by high throughput screening
topic KLHDC2
PROTAC
E3 ligase
high-throughput screening
url https://elifesciences.org/articles/106844
work_keys_str_mv AT hanzhou targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening
AT tonglianzhou targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening
AT wenliyu targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening
AT lipingliu targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening
AT yeonjinko targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening
AT kristenajohnson targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening
AT ianawilson targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening
AT petergschultz targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening
AT michaeljbollong targetedproteindegradationbyklhdc2ligandsidentifiedbyhighthroughputscreening