CRISPR-directed exon skipping; friend or foe (opportunity or warning sign)?

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Bibliographic Details
Main Authors: Kelly H. Banas, Eric B. Kmiec
Format: Article
Language:English
Published: Elsevier 2025-06-01
Series:Molecular Therapy: Nucleic Acids
Online Access:http://www.sciencedirect.com/science/article/pii/S2162253125000939
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