Cystinosis symposium: a rare disease model for comprehensive care

The time to provide a forum for collaboration in cystinosis research underscored the recent Cystinosis Symposium: A Rare Disease Model for Comprehensive Care held at the New York Academy of Medicine, on 31 May 2024, an event sponsored by the Cystinosis Research Network and numerous corporate entitie...

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Main Authors: Ashley M. Gefen, Frederick J. Kaskel, Joshua J. Zaritsky
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-07-01
Series:Frontiers in Pediatrics
Subjects:
Online Access:https://www.frontiersin.org/articles/10.3389/fped.2025.1630897/full
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author Ashley M. Gefen
Frederick J. Kaskel
Frederick J. Kaskel
Joshua J. Zaritsky
author_facet Ashley M. Gefen
Frederick J. Kaskel
Frederick J. Kaskel
Joshua J. Zaritsky
author_sort Ashley M. Gefen
collection DOAJ
description The time to provide a forum for collaboration in cystinosis research underscored the recent Cystinosis Symposium: A Rare Disease Model for Comprehensive Care held at the New York Academy of Medicine, on 31 May 2024, an event sponsored by the Cystinosis Research Network and numerous corporate entities (Amgen and others). This conference was one of the first to address the glaring deficiencies in the care of children and adults with cystinosis by focusing on themes that are mutually applicable to multidisciplinary healthcare providers, educators, and families. The ultimate goal was to disseminate new information and awareness to all engaged in the cystinosis community and provide an algorithm to navigate more effectively the promising future toward a cure.
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spelling doaj-art-aaa84a16a2454f8f910bd613df16bc842025-08-20T03:32:20ZengFrontiers Media S.A.Frontiers in Pediatrics2296-23602025-07-011310.3389/fped.2025.16308971630897Cystinosis symposium: a rare disease model for comprehensive careAshley M. Gefen0Frederick J. Kaskel1Frederick J. Kaskel2Joshua J. Zaritsky3Division of Nephrology, Department of Pediatrics, Phoenix Children's Hospital, Phoenix, AZ, United StatesDivision of Nephrology, Department of Pediatrics, Children's Hospital at Montefiore, New York, NY, United StatesDivision of Nephrology, Department of Pediatrics, Albert Einstein College of Medicine, Bronx, NY, United StatesDivision of Nephrology, Department of Pediatrics, Phoenix Children's Hospital, Phoenix, AZ, United StatesThe time to provide a forum for collaboration in cystinosis research underscored the recent Cystinosis Symposium: A Rare Disease Model for Comprehensive Care held at the New York Academy of Medicine, on 31 May 2024, an event sponsored by the Cystinosis Research Network and numerous corporate entities (Amgen and others). This conference was one of the first to address the glaring deficiencies in the care of children and adults with cystinosis by focusing on themes that are mutually applicable to multidisciplinary healthcare providers, educators, and families. The ultimate goal was to disseminate new information and awareness to all engaged in the cystinosis community and provide an algorithm to navigate more effectively the promising future toward a cure.https://www.frontiersin.org/articles/10.3389/fped.2025.1630897/fullcystinosisrare diseasecomprehensive caretransitioncystinosis metabolic bone disease
spellingShingle Ashley M. Gefen
Frederick J. Kaskel
Frederick J. Kaskel
Joshua J. Zaritsky
Cystinosis symposium: a rare disease model for comprehensive care
Frontiers in Pediatrics
cystinosis
rare disease
comprehensive care
transition
cystinosis metabolic bone disease
title Cystinosis symposium: a rare disease model for comprehensive care
title_full Cystinosis symposium: a rare disease model for comprehensive care
title_fullStr Cystinosis symposium: a rare disease model for comprehensive care
title_full_unstemmed Cystinosis symposium: a rare disease model for comprehensive care
title_short Cystinosis symposium: a rare disease model for comprehensive care
title_sort cystinosis symposium a rare disease model for comprehensive care
topic cystinosis
rare disease
comprehensive care
transition
cystinosis metabolic bone disease
url https://www.frontiersin.org/articles/10.3389/fped.2025.1630897/full
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AT joshuajzaritsky cystinosissymposiumararediseasemodelforcomprehensivecare