Intrahepatic cholangiocarcinoma trends and treatment lines: real-world evidence from the French National Hospital Discharge database

Background: Little is known about the therapeutic trajectory of patients treated in hospitals for intrahepatic cholangiocarcinoma (iCCA) and patterns of care in daily clinical practice. Patients and methods: An observational retrospective study was conducted on the French National Hospital Discharge...

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Main Authors: M. Delaye, B. Grenier, A. Lièvre, C. Neuzillet
Format: Article
Language:English
Published: Elsevier 2025-06-01
Series:ESMO Gastrointestinal Oncology
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Online Access:http://www.sciencedirect.com/science/article/pii/S2949819825000214
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author M. Delaye
B. Grenier
A. Lièvre
C. Neuzillet
author_facet M. Delaye
B. Grenier
A. Lièvre
C. Neuzillet
author_sort M. Delaye
collection DOAJ
description Background: Little is known about the therapeutic trajectory of patients treated in hospitals for intrahepatic cholangiocarcinoma (iCCA) and patterns of care in daily clinical practice. Patients and methods: An observational retrospective study was conducted on the French National Hospital Discharge Database. All patients with a new diagnosis of iCCA who had a first hospital stay (S1) from January 2016 to December 2021 were included. They were followed up until December 2021, or in-hospital death, whichever occurred first. Crude annual hospitalization rates were computed. Treatment lines were identified with an artificial intelligence algorithm [Analysis of Treatment Lines using Alignment of Sequences (ATLAS)]. A multistate model was used to compute the transition rates between lines. Results: Overall, 13 491 patients were included and the mean (standard deviation) follow-up duration was 13.1 months (17.9 months). The median age at S1 was 72.0 years and 55.9% were male. Nearly 20.7% were admitted via emergency services for S1, and 32.1% had metastases. Between 2016 and 2021, the crude annual rate of new iCCA cases increased from 3.08 [95% confidence interval (CI) 2.94-3.24] in 2016 (n = 1598) to 4.12 (95% CI 3.95-4.29) per 100 000 adult person-years in 2021 (n = 2188). Among 4855 patients receiving first-line systemic therapy (L1), 37.7% (95% CI 36.0% to 39.3%) received a second-line 2 (L2) during the follow-up. The median time between the start of L1 and the beginning of L2 was 7.0 months. Conclusions: This study provides up-to-date national real-world data on iCCA, revealing an increasing burden year by year in France, a poor outcome of patients with iCCA on L1 systemic therapy, and the low proportion of patients receiving an L2.
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spelling doaj-art-aa7e9a2f632b42f4b7d0cb331ea220072025-08-20T02:39:31ZengElsevierESMO Gastrointestinal Oncology2949-81982025-06-01810015210.1016/j.esmogo.2025.100152Intrahepatic cholangiocarcinoma trends and treatment lines: real-world evidence from the French National Hospital Discharge databaseM. Delaye0B. Grenier1A. Lièvre2C. Neuzillet3Department of Medical Oncology, Gastrointestinal Oncology, Institut Curie, Université Versailles Saint-Quentin-Université Paris-Saclay, Saint-Cloud, France; Association pour l'étude des Cancers et Affections des voies Biliaires (ACABi), Paris, France; Correspondence to: Dr Matthieu Delaye, Department of Medical Oncology, Gastrointestinal Oncology, Institut Curie, Université Versailles Saint-Quentin-Université Paris-Saclay, 35 rue, Saint-Cloud 92210, France. Tel: +33147111515Epidemiology Department, Heva, Lyon, FranceDepartment of Gastroenterology, University Hospital Pontchaillou, Rennes 1 University, INSERM U1242 “Chemistry Oncogenesis Stress Signalling”, Rennes, FranceDepartment of Medical Oncology, Gastrointestinal Oncology, Institut Curie, Université Versailles Saint-Quentin-Université Paris-Saclay, Saint-Cloud, France; Association pour l'étude des Cancers et Affections des voies Biliaires (ACABi), Paris, FranceBackground: Little is known about the therapeutic trajectory of patients treated in hospitals for intrahepatic cholangiocarcinoma (iCCA) and patterns of care in daily clinical practice. Patients and methods: An observational retrospective study was conducted on the French National Hospital Discharge Database. All patients with a new diagnosis of iCCA who had a first hospital stay (S1) from January 2016 to December 2021 were included. They were followed up until December 2021, or in-hospital death, whichever occurred first. Crude annual hospitalization rates were computed. Treatment lines were identified with an artificial intelligence algorithm [Analysis of Treatment Lines using Alignment of Sequences (ATLAS)]. A multistate model was used to compute the transition rates between lines. Results: Overall, 13 491 patients were included and the mean (standard deviation) follow-up duration was 13.1 months (17.9 months). The median age at S1 was 72.0 years and 55.9% were male. Nearly 20.7% were admitted via emergency services for S1, and 32.1% had metastases. Between 2016 and 2021, the crude annual rate of new iCCA cases increased from 3.08 [95% confidence interval (CI) 2.94-3.24] in 2016 (n = 1598) to 4.12 (95% CI 3.95-4.29) per 100 000 adult person-years in 2021 (n = 2188). Among 4855 patients receiving first-line systemic therapy (L1), 37.7% (95% CI 36.0% to 39.3%) received a second-line 2 (L2) during the follow-up. The median time between the start of L1 and the beginning of L2 was 7.0 months. Conclusions: This study provides up-to-date national real-world data on iCCA, revealing an increasing burden year by year in France, a poor outcome of patients with iCCA on L1 systemic therapy, and the low proportion of patients receiving an L2.http://www.sciencedirect.com/science/article/pii/S2949819825000214biliary tract cancerreal-world dataCisGemFOLFOXartificial intelligence
spellingShingle M. Delaye
B. Grenier
A. Lièvre
C. Neuzillet
Intrahepatic cholangiocarcinoma trends and treatment lines: real-world evidence from the French National Hospital Discharge database
ESMO Gastrointestinal Oncology
biliary tract cancer
real-world data
CisGem
FOLFOX
artificial intelligence
title Intrahepatic cholangiocarcinoma trends and treatment lines: real-world evidence from the French National Hospital Discharge database
title_full Intrahepatic cholangiocarcinoma trends and treatment lines: real-world evidence from the French National Hospital Discharge database
title_fullStr Intrahepatic cholangiocarcinoma trends and treatment lines: real-world evidence from the French National Hospital Discharge database
title_full_unstemmed Intrahepatic cholangiocarcinoma trends and treatment lines: real-world evidence from the French National Hospital Discharge database
title_short Intrahepatic cholangiocarcinoma trends and treatment lines: real-world evidence from the French National Hospital Discharge database
title_sort intrahepatic cholangiocarcinoma trends and treatment lines real world evidence from the french national hospital discharge database
topic biliary tract cancer
real-world data
CisGem
FOLFOX
artificial intelligence
url http://www.sciencedirect.com/science/article/pii/S2949819825000214
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AT alievre intrahepaticcholangiocarcinomatrendsandtreatmentlinesrealworldevidencefromthefrenchnationalhospitaldischargedatabase
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