Generation and characterization of human iPSC line SANi012-A from a patient with an inherited platelet disorder carrying the heterozygous ETV6 c.1105C > T variant

Germline mutations in ETV6, a transcription factor of the ETS family, are associated with autosomal dominant thrombocytopenia and an increased risk of leukemia. We generated a human iPSC line, SANi012-A, from a patient carrying a heterozygous ETV6 c.1105C > T missense mutation. Proerythroblasts f...

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Main Authors: Huan Zhang, Chantal C. Clark, Elise J. Huisman, Marieke von Lindern, Marjon H. Cnossen, Emile van den Akker, Eszter Varga
Format: Article
Language:English
Published: Elsevier 2025-09-01
Series:Stem Cell Research
Online Access:http://www.sciencedirect.com/science/article/pii/S1873506125001199
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author Huan Zhang
Chantal C. Clark
Elise J. Huisman
Marieke von Lindern
Marjon H. Cnossen
Emile van den Akker
Eszter Varga
author_facet Huan Zhang
Chantal C. Clark
Elise J. Huisman
Marieke von Lindern
Marjon H. Cnossen
Emile van den Akker
Eszter Varga
author_sort Huan Zhang
collection DOAJ
description Germline mutations in ETV6, a transcription factor of the ETS family, are associated with autosomal dominant thrombocytopenia and an increased risk of leukemia. We generated a human iPSC line, SANi012-A, from a patient carrying a heterozygous ETV6 c.1105C > T missense mutation. Proerythroblasts from the patient’s peripheral blood mononuclear cells (PBMCs) were reprogrammed using a lentiviral hOKSM polycistronic vector. The iPSC line showed normal karyotype and morphology, expressed pluripotency markers, and were able to differentiate into all three germ layers.
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publishDate 2025-09-01
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series Stem Cell Research
spelling doaj-art-aa2673ac46f842aa85fbf1bc70a1d7f72025-08-20T03:50:01ZengElsevierStem Cell Research1873-50612025-09-018710376910.1016/j.scr.2025.103769Generation and characterization of human iPSC line SANi012-A from a patient with an inherited platelet disorder carrying the heterozygous ETV6 c.1105C > T variantHuan Zhang0Chantal C. Clark1Elise J. Huisman2Marieke von Lindern3Marjon H. Cnossen4Emile van den Akker5Eszter Varga6Sanquin Research and Landsteiner Laboratory, Amsterdam UMC, University of Amsterdam, Amsterdam, The NetherlandsSanquin Research and Landsteiner Laboratory, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands; Center for Benign Hematology, Thrombosis and Hemostasis - Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, The NetherlandsDepartment of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center, Rotterdam, The NetherlandsSanquin Research and Landsteiner Laboratory, Amsterdam UMC, University of Amsterdam, Amsterdam, The NetherlandsDepartment of Pediatric Hematology and Oncology, Erasmus MC Sophia Children’s Hospital, University Medical Center, Rotterdam, The NetherlandsSanquin Research and Landsteiner Laboratory, Amsterdam UMC, University of Amsterdam, Amsterdam, The NetherlandsSanquin Research and Landsteiner Laboratory, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands; Corresponding author.Germline mutations in ETV6, a transcription factor of the ETS family, are associated with autosomal dominant thrombocytopenia and an increased risk of leukemia. We generated a human iPSC line, SANi012-A, from a patient carrying a heterozygous ETV6 c.1105C > T missense mutation. Proerythroblasts from the patient’s peripheral blood mononuclear cells (PBMCs) were reprogrammed using a lentiviral hOKSM polycistronic vector. The iPSC line showed normal karyotype and morphology, expressed pluripotency markers, and were able to differentiate into all three germ layers.http://www.sciencedirect.com/science/article/pii/S1873506125001199
spellingShingle Huan Zhang
Chantal C. Clark
Elise J. Huisman
Marieke von Lindern
Marjon H. Cnossen
Emile van den Akker
Eszter Varga
Generation and characterization of human iPSC line SANi012-A from a patient with an inherited platelet disorder carrying the heterozygous ETV6 c.1105C > T variant
Stem Cell Research
title Generation and characterization of human iPSC line SANi012-A from a patient with an inherited platelet disorder carrying the heterozygous ETV6 c.1105C > T variant
title_full Generation and characterization of human iPSC line SANi012-A from a patient with an inherited platelet disorder carrying the heterozygous ETV6 c.1105C > T variant
title_fullStr Generation and characterization of human iPSC line SANi012-A from a patient with an inherited platelet disorder carrying the heterozygous ETV6 c.1105C > T variant
title_full_unstemmed Generation and characterization of human iPSC line SANi012-A from a patient with an inherited platelet disorder carrying the heterozygous ETV6 c.1105C > T variant
title_short Generation and characterization of human iPSC line SANi012-A from a patient with an inherited platelet disorder carrying the heterozygous ETV6 c.1105C > T variant
title_sort generation and characterization of human ipsc line sani012 a from a patient with an inherited platelet disorder carrying the heterozygous etv6 c 1105c t variant
url http://www.sciencedirect.com/science/article/pii/S1873506125001199
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