Exacerbating and reversing lysosomal storage diseases: from yeast to humans
Lysosomal storage diseases (LSDs) arise from monogenic deficiencies in lysosomal proteins and pathways and are characterized by a tissue-wide accumulation of a vast variety of macromolecules, normally specific to each genetic lesion. Strategies for treatment of LSDs commonly depend on reduction of t...
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| Main Authors: | Tamayanthi Rajakumar, Andrew B. Munkacsi, Stephen L. Sturley |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
Shared Science Publishers OG
2017-08-01
|
| Series: | Microbial Cell |
| Subjects: | |
| Online Access: | http://microbialcell.com/researcharticles/exacerbating-and-reversing-lysosomal-storage-diseases-from-yeast-to-humans/ |
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