P311: Clinical responses to off-label use of phenylbutyrate for STXBP1 and SLC6A1

P311: Clinical responses to off-label use of phenylbutyrate for STXBP1 and SLC6A1

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Bibliographic Details
Main Authors:	Kristen Barbour, Tommy Stӧdberg, Anna Larsson, Zachary Grinspan
Format:	Article
Language:	English
Published:	Elsevier 2025-01-01
Series:	Genetics in Medicine Open
Online Access:	http://www.sciencedirect.com/science/article/pii/S2949774425003152
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