TARGETING PRC2 ENHANCES THE ANTITUMOR CYTOTOXIC CAPACITY OF ANTI-CD19 CAR-T CELLS AGAINST HEMATOLOGICAL MALIGNANCIES

Chimeric Antigen Receptor (CAR) T cell therapy was adopted as a clinical modality for patients with relapsed/refractory hematological malignancies. Despite the clinical efficacy of CAR-T cell therapy, a considerable fraction of patients still relapses during the first months following CAR-T cell inf...

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Main Authors: MLR Carvalho, CO Andrade, MP Cabral-Piccin, GS Kinker, GAF Vitiello, L Abdo, RAG Cambui, MH Bonamino, TS Medina
Format: Article
Language:English
Published: Elsevier 2024-10-01
Series:Hematology, Transfusion and Cell Therapy
Online Access:http://www.sciencedirect.com/science/article/pii/S2531137924019989
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author MLR Carvalho
CO Andrade
MP Cabral-Piccin
GS Kinker
GAF Vitiello
L Abdo
RAG Cambui
MH Bonamino
TS Medina
author_facet MLR Carvalho
CO Andrade
MP Cabral-Piccin
GS Kinker
GAF Vitiello
L Abdo
RAG Cambui
MH Bonamino
TS Medina
author_sort MLR Carvalho
collection DOAJ
description Chimeric Antigen Receptor (CAR) T cell therapy was adopted as a clinical modality for patients with relapsed/refractory hematological malignancies. Despite the clinical efficacy of CAR-T cell therapy, a considerable fraction of patients still relapses during the first months following CAR-T cell infusion. The limited CAR-T cell efficiency is thought to relate to epigenetic mechanisms involved in T-cell suppression and dysfunction. Here, screening of multiple epigenetic inhibitors revealed that targeting PRC2 consistently enhanced the cytotoxic/effector phenotype of CD8 T-cells. Notably, PRC2 inhibition promoted the differentiation of GZMB+ effector memory 19BBζ CAR-T cells and enhanced their antitumor activity both in vitro and in vivo. Consistent with their long-lasting antitumor activity, PRC2-inhibited 19BBζ CAR-T cells did not exhibit any signs of dysfunctionality/exhaustion. Furthermore, TCR restimulation along with PRC2 inhibition of patient-derived anti-CD19 CAR-T cells also induced the development of GZMB+ effector memory cells and elicited potent antitumor responses against CD19+ Daudi cells. In line with this, thegene signature derived from in-house PRC2-inhibited 19BBζ CAR-T cells was enriched in tisagenlecleucel (tisa-cel) BBζCAR-T cell therapy responders with large B-cell lymphoma. Collectively, our results demonstrated that targeting PRC2 may be a promising approach to enhance a functional effector program in CAR-T cells against hematological malignancies.
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spelling doaj-art-a3c90adc916c4e98af573a04f9b095c82025-08-20T02:17:45ZengElsevierHematology, Transfusion and Cell Therapy2531-13792024-10-0146S97910.1016/j.htct.2024.09.1665TARGETING PRC2 ENHANCES THE ANTITUMOR CYTOTOXIC CAPACITY OF ANTI-CD19 CAR-T CELLS AGAINST HEMATOLOGICAL MALIGNANCIESMLR Carvalho0CO Andrade1MP Cabral-Piccin2GS Kinker3GAF Vitiello4L Abdo5RAG Cambui6MH Bonamino7TS Medina8International Research Center, A.C.Camargo Cancer Center, São Paulo, SP, BrazilCell and Gene Therapy Program – Research Coordination, Instituto Nacional de Câncer (INCA), Rio de Janeiro, RJ, BrazilInternational Research Center, A.C.Camargo Cancer Center, São Paulo, SP, BrazilInternational Research Center, A.C.Camargo Cancer Center, São Paulo, SP, BrazilInternational Research Center, A.C.Camargo Cancer Center, São Paulo, SP, BrazilCell and Gene Therapy Program – Research Coordination, Instituto Nacional de Câncer (INCA), Rio de Janeiro, RJ, BrazilInternational Research Center, A.C.Camargo Cancer Center, São Paulo, SP, BrazilCell and Gene Therapy Program – Research Coordination, Instituto Nacional de Câncer (INCA), Rio de Janeiro, RJ, BrazilInternational Research Center, A.C.Camargo Cancer Center, São Paulo, SP, BrazilChimeric Antigen Receptor (CAR) T cell therapy was adopted as a clinical modality for patients with relapsed/refractory hematological malignancies. Despite the clinical efficacy of CAR-T cell therapy, a considerable fraction of patients still relapses during the first months following CAR-T cell infusion. The limited CAR-T cell efficiency is thought to relate to epigenetic mechanisms involved in T-cell suppression and dysfunction. Here, screening of multiple epigenetic inhibitors revealed that targeting PRC2 consistently enhanced the cytotoxic/effector phenotype of CD8 T-cells. Notably, PRC2 inhibition promoted the differentiation of GZMB+ effector memory 19BBζ CAR-T cells and enhanced their antitumor activity both in vitro and in vivo. Consistent with their long-lasting antitumor activity, PRC2-inhibited 19BBζ CAR-T cells did not exhibit any signs of dysfunctionality/exhaustion. Furthermore, TCR restimulation along with PRC2 inhibition of patient-derived anti-CD19 CAR-T cells also induced the development of GZMB+ effector memory cells and elicited potent antitumor responses against CD19+ Daudi cells. In line with this, thegene signature derived from in-house PRC2-inhibited 19BBζ CAR-T cells was enriched in tisagenlecleucel (tisa-cel) BBζCAR-T cell therapy responders with large B-cell lymphoma. Collectively, our results demonstrated that targeting PRC2 may be a promising approach to enhance a functional effector program in CAR-T cells against hematological malignancies.http://www.sciencedirect.com/science/article/pii/S2531137924019989
spellingShingle MLR Carvalho
CO Andrade
MP Cabral-Piccin
GS Kinker
GAF Vitiello
L Abdo
RAG Cambui
MH Bonamino
TS Medina
TARGETING PRC2 ENHANCES THE ANTITUMOR CYTOTOXIC CAPACITY OF ANTI-CD19 CAR-T CELLS AGAINST HEMATOLOGICAL MALIGNANCIES
Hematology, Transfusion and Cell Therapy
title TARGETING PRC2 ENHANCES THE ANTITUMOR CYTOTOXIC CAPACITY OF ANTI-CD19 CAR-T CELLS AGAINST HEMATOLOGICAL MALIGNANCIES
title_full TARGETING PRC2 ENHANCES THE ANTITUMOR CYTOTOXIC CAPACITY OF ANTI-CD19 CAR-T CELLS AGAINST HEMATOLOGICAL MALIGNANCIES
title_fullStr TARGETING PRC2 ENHANCES THE ANTITUMOR CYTOTOXIC CAPACITY OF ANTI-CD19 CAR-T CELLS AGAINST HEMATOLOGICAL MALIGNANCIES
title_full_unstemmed TARGETING PRC2 ENHANCES THE ANTITUMOR CYTOTOXIC CAPACITY OF ANTI-CD19 CAR-T CELLS AGAINST HEMATOLOGICAL MALIGNANCIES
title_short TARGETING PRC2 ENHANCES THE ANTITUMOR CYTOTOXIC CAPACITY OF ANTI-CD19 CAR-T CELLS AGAINST HEMATOLOGICAL MALIGNANCIES
title_sort targeting prc2 enhances the antitumor cytotoxic capacity of anti cd19 car t cells against hematological malignancies
url http://www.sciencedirect.com/science/article/pii/S2531137924019989
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