Economics, externalities and rare disease

Special combined efforts addressing rare diseases should apply economic principles and methods to maximize returns to research and investment. Four opportunities exist: (1) exploiting treatment spillovers; (2) encouraging institutional networking and knowledge-sharing; (3) recognizing shared molecul...

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Main Authors: Carlisle Ford Runge, James Campbell, Carlisle P. Runge, Reena V. Kartha
Format: Article
Language:English
Published: Elsevier 2024-01-01
Series:Rare
Subjects:
Online Access:http://www.sciencedirect.com/science/article/pii/S295000872400019X
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author Carlisle Ford Runge
James Campbell
Carlisle P. Runge
Reena V. Kartha
author_facet Carlisle Ford Runge
James Campbell
Carlisle P. Runge
Reena V. Kartha
author_sort Carlisle Ford Runge
collection DOAJ
description Special combined efforts addressing rare diseases should apply economic principles and methods to maximize returns to research and investment. Four opportunities exist: (1) exploiting treatment spillovers; (2) encouraging institutional networking and knowledge-sharing; (3) recognizing shared molecular and genetic etiologies; (4) organizing resulting clusters and baskets for scaling trials, research, diagnosis and treatment.
format Article
id doaj-art-a390b86b96844f728b9acde21497902e
institution OA Journals
issn 2950-0087
language English
publishDate 2024-01-01
publisher Elsevier
record_format Article
series Rare
spelling doaj-art-a390b86b96844f728b9acde21497902e2025-08-20T02:37:02ZengElsevierRare2950-00872024-01-01210003610.1016/j.rare.2024.100036Economics, externalities and rare diseaseCarlisle Ford Runge0James Campbell1Carlisle P. Runge2Reena V. Kartha3Department of Applied Economics and Law, University of Minnesota, Twin Cities, USA; Corresponding author.School of Public Health, University of Minnesota, Twin Cities, USABinera, Inc. consulting for Biomedical Advanced Research and Development Authority (BARDA), U. S. Department of Health and Human Services, Washington DC, USACollege of Pharmacy, Center for Orphan Drug Research. Department of Experimental and Clinical Pharmacology, University of Minnesota, Twin Cities, USASpecial combined efforts addressing rare diseases should apply economic principles and methods to maximize returns to research and investment. Four opportunities exist: (1) exploiting treatment spillovers; (2) encouraging institutional networking and knowledge-sharing; (3) recognizing shared molecular and genetic etiologies; (4) organizing resulting clusters and baskets for scaling trials, research, diagnosis and treatment.http://www.sciencedirect.com/science/article/pii/S295000872400019XSpilloversAffinity clustersBasket trialsInvestment, orphan drugs
spellingShingle Carlisle Ford Runge
James Campbell
Carlisle P. Runge
Reena V. Kartha
Economics, externalities and rare disease
Rare
Spillovers
Affinity clusters
Basket trials
Investment, orphan drugs
title Economics, externalities and rare disease
title_full Economics, externalities and rare disease
title_fullStr Economics, externalities and rare disease
title_full_unstemmed Economics, externalities and rare disease
title_short Economics, externalities and rare disease
title_sort economics externalities and rare disease
topic Spillovers
Affinity clusters
Basket trials
Investment, orphan drugs
url http://www.sciencedirect.com/science/article/pii/S295000872400019X
work_keys_str_mv AT carlislefordrunge economicsexternalitiesandraredisease
AT jamescampbell economicsexternalitiesandraredisease
AT carlisleprunge economicsexternalitiesandraredisease
AT reenavkartha economicsexternalitiesandraredisease