Gene therapy breakthroughs in ALS: a beacon of hope for 20% of ALS patients

Gene therapy breakthroughs in ALS: a beacon of hope for 20% of ALS patients

Abstract Amyotrophic lateral sclerosis (ALS) is a fatal motor neuron disease that remains incurable. Although the etiologies of ALS are diverse and the precise pathogenic mechanisms are not fully understood, approximately 20% of ALS cases are caused by genetic factors. Therefore, advancing targeted...

Full description

Saved in:
Bibliographic Details
Main Authors: Qingjian Xie, Kezheng Li, Yinuo Chen, Yaojia Li, Wenhua Jiang, Wen Cao, Huan Yu, Dongsheng Fan, Binbin Deng
Format: Article
Language:English
Published: BMC 2025-04-01
Series:Translational Neurodegeneration
Subjects:
Amyotrophic lateral sclerosis
Gene therapy
Gene therapy vectors
Gene targeting sites
Online Access:https://doi.org/10.1186/s40035-025-00477-6
Tags: Add Tag
No Tags, Be the first to tag this record!

Similar Items

Similar Items