Structure-based discovery and experimental validation of HIT101481851 as a potential PKMYT1 inhibitor for pancreatic cancer

PKMYT1 is a validated therapeutic target in pancreatic cancer due to its critical role in controlling the G2/M transition of the cell cycle. In this study, a structure-based drug discovery pipeline was implemented to identify novel PKMYT1 inhibitors with high binding stability and anticancer potenti...

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Main Authors: Ting Wang, Jingyu Wang, Gongxiong Yao, Hongchao Zhang, Chenghui Song, Xueren Ao
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-06-01
Series:Frontiers in Pharmacology
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Online Access:https://www.frontiersin.org/articles/10.3389/fphar.2025.1605741/full
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author Ting Wang
Ting Wang
Jingyu Wang
Gongxiong Yao
Hongchao Zhang
Chenghui Song
Xueren Ao
author_facet Ting Wang
Ting Wang
Jingyu Wang
Gongxiong Yao
Hongchao Zhang
Chenghui Song
Xueren Ao
author_sort Ting Wang
collection DOAJ
description PKMYT1 is a validated therapeutic target in pancreatic cancer due to its critical role in controlling the G2/M transition of the cell cycle. In this study, a structure-based drug discovery pipeline was implemented to identify novel PKMYT1 inhibitors with high binding stability and anticancer potential. Pharmacophore models were constructed from four PKMYT1 co-crystal structures, and virtual screening was performed against a large compound library. Through molecular docking and intersection analysis, five consensus high-affinity compounds were identified, among which HIT101481851 demonstrated the most favorable binding characteristics. Molecular dynamics simulations confirmed its stable interactions with key residues such as CYS-190 and PHE-240 across multiple PKMYT1 conformations. ADMET predictions indicated good gastrointestinal absorption, acceptable drug-likeness, and low risk of off-target reactivity. Furthermore, in vivo experiments showed that HIT101481851 inhibited the viability of pancreatic cancer cell lines in a dose-dependent manner while exhibiting lower toxicity toward normal pancreatic epithelial cells. These results suggest that HIT101481851 is a promising lead compound for the development of PKMYT1-targeted therapeutics in pancreatic cancer.
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publisher Frontiers Media S.A.
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spelling doaj-art-9d534cd83bf74d61bddf61ef8dc4dcef2025-08-20T03:31:11ZengFrontiers Media S.A.Frontiers in Pharmacology1663-98122025-06-011610.3389/fphar.2025.16057411605741Structure-based discovery and experimental validation of HIT101481851 as a potential PKMYT1 inhibitor for pancreatic cancerTing Wang0Ting Wang1Jingyu Wang2Gongxiong Yao3Hongchao Zhang4Chenghui Song5Xueren Ao6The Third Clinical Medical College of Guangzhou University of Chinese Medicine, Guangzhou, ChinaThe Third Affiliated Hospital, Guangzhou University of Chinese Medicine, Guangzhou, ChinaThe Third Affiliated Hospital, Guangzhou University of Chinese Medicine, Guangzhou, ChinaThe Third Affiliated Hospital, Guangzhou University of Chinese Medicine, Guangzhou, ChinaThe Third Affiliated Hospital, Guangzhou University of Chinese Medicine, Guangzhou, ChinaThe Third Affiliated Hospital, Guangzhou University of Chinese Medicine, Guangzhou, ChinaThe Third Affiliated Hospital, Guangzhou University of Chinese Medicine, Guangzhou, ChinaPKMYT1 is a validated therapeutic target in pancreatic cancer due to its critical role in controlling the G2/M transition of the cell cycle. In this study, a structure-based drug discovery pipeline was implemented to identify novel PKMYT1 inhibitors with high binding stability and anticancer potential. Pharmacophore models were constructed from four PKMYT1 co-crystal structures, and virtual screening was performed against a large compound library. Through molecular docking and intersection analysis, five consensus high-affinity compounds were identified, among which HIT101481851 demonstrated the most favorable binding characteristics. Molecular dynamics simulations confirmed its stable interactions with key residues such as CYS-190 and PHE-240 across multiple PKMYT1 conformations. ADMET predictions indicated good gastrointestinal absorption, acceptable drug-likeness, and low risk of off-target reactivity. Furthermore, in vivo experiments showed that HIT101481851 inhibited the viability of pancreatic cancer cell lines in a dose-dependent manner while exhibiting lower toxicity toward normal pancreatic epithelial cells. These results suggest that HIT101481851 is a promising lead compound for the development of PKMYT1-targeted therapeutics in pancreatic cancer.https://www.frontiersin.org/articles/10.3389/fphar.2025.1605741/fullPKMYT1pancreatic cancervirtual screeningmolecular dynamicsexperimental validation
spellingShingle Ting Wang
Ting Wang
Jingyu Wang
Gongxiong Yao
Hongchao Zhang
Chenghui Song
Xueren Ao
Structure-based discovery and experimental validation of HIT101481851 as a potential PKMYT1 inhibitor for pancreatic cancer
Frontiers in Pharmacology
PKMYT1
pancreatic cancer
virtual screening
molecular dynamics
experimental validation
title Structure-based discovery and experimental validation of HIT101481851 as a potential PKMYT1 inhibitor for pancreatic cancer
title_full Structure-based discovery and experimental validation of HIT101481851 as a potential PKMYT1 inhibitor for pancreatic cancer
title_fullStr Structure-based discovery and experimental validation of HIT101481851 as a potential PKMYT1 inhibitor for pancreatic cancer
title_full_unstemmed Structure-based discovery and experimental validation of HIT101481851 as a potential PKMYT1 inhibitor for pancreatic cancer
title_short Structure-based discovery and experimental validation of HIT101481851 as a potential PKMYT1 inhibitor for pancreatic cancer
title_sort structure based discovery and experimental validation of hit101481851 as a potential pkmyt1 inhibitor for pancreatic cancer
topic PKMYT1
pancreatic cancer
virtual screening
molecular dynamics
experimental validation
url https://www.frontiersin.org/articles/10.3389/fphar.2025.1605741/full
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