Gene therapy: A Revolution in Medicine or a Risky Game with our DNA?

Gene therapy: A Revolution in Medicine or a Risky Game with our DNA?

Introduction: The aim of this review is to provide an overview of the applications of gene therapies in various diseases and to highlight areas where further research is needed. Materials and methods: A review of chosen literature in the PubMed database was conducted, using the following keyword...

Full description

Saved in:

Bibliographic Details
Main Authors:	Julia Kozakiewicz, Aleksandra Okońska, Kamil Kościelecki, Agnieszka Kalisz, Iwona Skorulska, Klaudia Mączewska, Patrycja Długozima, Paulina Grzeszczuk, Weronika Grywińska, Aleksandra Głowacka
Format:	Article
Language:	English
Published:	Nicolaus Copernicus University in Toruń 2025-03-01
Series:	Quality in Sport
Subjects:	gene therapy SMA DMD Parkinson's disease Huntington's disease
Online Access:	https://apcz.umk.pl/QS/article/view/58956
Tags:	Add Tag No Tags, Be the first to tag this record!

Similar Items

Cast Syndrome: Breaking Self-Perpetuating Circle through Increased Medical Awareness
by: Agnieszka Kalisz, et al.
Published: (2025-04-01)

When pulmonary embolism is not an obvious diagnosis - pathophysiology, risk factors, diagnosis, treatment and a review of the most unusual cases
by: Julia Kozakiewicz, et al.
Published: (2025-03-01)

Schnitzler Syndrome - Unraveling the Mystery of a Complex Condition
by: Paulina Grzeszczuk, et al.
Published: (2025-04-01)

Alpha 1 Antitrypsin Deficiency Pathophysiology, Symptoms, Diagnosis, Treatment
by: Kamil Kościelecki, et al.
Published: (2025-04-01)

Exploring the Potential of Virtual Reality in Eating Disorder Treatment
by: Weronika Barbara Grywińska, et al.
Published: (2025-03-01)

Optune in Glioblastoma: Revolutionizing Treatment with Tumor Treating Fields
by: Patrycja Długozima, et al.
Published: (2025-05-01)

Detecting Sleep Apnea with Smart-tech: Scientific Breakthrough or Overhyped Technology?
by: Aleksandra Głowacka, et al.
Published: (2025-04-01)

Treating neuromuscular diseases: unveiling gene therapy breakthroughs and pioneering future applications
by: Yu-Fu Wu, et al.
Published: (2025-02-01)

Malestar psicológico en portadores y no portadores de la mutación causante de enfermedad de Huntington y su relación con la carga de la enfermedad
by: Y. Rodríguez-Agudelo, et al.
Published: (2025-01-01)

Recognizing familial Huntington's disease in an Asian cohort: Insights from the Philippines
by: Jao Jarro B. Garcia, et al.
Published: (2025-03-01)

Significance of gene therapy in neurodegenerative diseases
by: Lingling Wang, et al.
Published: (2025-05-01)

Phase II trial of intravenous human dental pulp stem cell therapy for Huntington’s disease: a randomized, double-blind, placebo-controlled study
by: Joyce Macedo Sanches Fernandes, et al.
Published: (2025-08-01)

Diffusion tensor imaging of brain white matter in Huntington gene mutation individuals
by: Roberta Arb Saba, et al.

Juvenile Huntington's disease confirmed by genetic examination in twins Doença de Huntington juvenil confirmada por exame genético em gêmeas
by: GILBERTO LEVY, et al.
Published: (1999-09-01)

Internal consistency of a Brazilian version of the unified Huntington's disease rating scale Consistência interna da versão brasileira da escala unificada para avaliação da doença da Huntington
by: Vitor Tumas, et al.
Published: (2004-12-01)

Theory of mind impairment in Huntington's disease patients and their relatives
by: Leo Bayliss, et al.

Altered huntingtin−chromatin interactions predict transcriptional and epigenetic changes in Huntington's disease
by: Jocelynn R. Pearl, et al.
Published: (2025-05-01)

Varenicline improves motor and cognitive symptoms in early Huntington&rsquo;s disease
by: McGregor A, et al.
Published: (2016-09-01)

In Vitro Efficacy of PEI-Derived Lipopolymers in Silencing of Toxic Proteins in a Neuronal Model of Huntington’s Disease
by: Luis C. Morales, et al.
Published: (2025-05-01)

Navigating the neuronal recycling bin: Another look at huntingtin in coordinating autophagy
by: Thomas J. Krzystek, et al.
Published: (2025-12-01)

Problems with the Care of a Patient with Huntington’s Disease Hospitalised in a Psychiatric Ward — Case Report
by: Katarzyna Gołębiewska, et al.
Published: (2020-06-01)

“I don't have Huntington's disease”: the boundaries between acceptance and understanding
by: Gustavo Leite Franklin, et al.
Published: (2023-07-01)

Genomic insights into Duchene muscular dystrophy: Analysis of 1250 patients reveals 30% novel genetic patterns and 6 novel variants
by: Khalda Amr, et al.
Published: (2024-12-01)

Preliminary observations of glucose metabolism dysregulation in pediatric Huntington’s disease
by: Federica Graziola, et al.
Published: (2025-08-01)

Non-choreic movement disorders as initial manifestations of Huntington's disease Distúrbios do movimento não-coreicos como manifestação inicial da doença de Huntington
by: Nilson Becker, et al.
Published: (2007-06-01)

Two Decades of Huntington’s Disease in Varna, Bulgaria: A Retrospective Single-Centre Study of Clinical Trends and Challenges
by: Mariya Levkova, et al.
Published: (2025-06-01)

Striatal infusion of cholesterol promotes dose‐dependent behavioral benefits and exerts disease‐modifying effects in Huntington's disease mice
by: Giulia Birolini, et al.
Published: (2020-09-01)

Cholesterol‐loaded nanoparticles ameliorate synaptic and cognitive function in Huntington's disease mice
by: Marta Valenza, et al.
Published: (2015-11-01)

Huntington’s disease modeling on HEK293 cell line
by: D. V. Sharipova, et al.
Published: (2017-12-01)

Neurexin1 level in Huntington’s Disease and decreased Neurexin1 in disease progression
by: Kyoungjoo Cho, et al.
Published: (2025-03-01)

Associations between Sleep Quality and Serum Levels of Neurofilament Light in Individuals with Premanifest Huntington Disease
by: Mitchell Turner, et al.
Published: (2024-06-01)

The impact of COVID-19 pandemic on patients with Huntington's disease and care-givers: A French survey
by: Sara Meoni, et al.
Published: (2024-09-01)

Navigating competing needs: a qualitative study on parenthood with a partner with Huntington’s disease
by: Kristin J. Billaud Feragen, et al.
Published: (2025-12-01)

Abnormal eye movements in three types of chorea
by: Tiago Attoni, et al.

The mechanism of super-enhancer regulation of gene expression and research progress in neurodegenerative diseases
by: Shaofei Zhao, et al.
Published: (2025-04-01)

A collaborative network analysis for the interpretation of transcriptomics data in Huntington’s disease
by: Ozan Ozisik, et al.
Published: (2025-01-01)

Role of Asleep Surgery for Supplementary Motor Area Tumors
by: Krishna Kumar G, et al.
Published: (2023-08-01)

Huntington disease: DNA analysis in brazilian population
by: RASKIN SALMO, et al.
Published: (2000-01-01)

Longitudinal Treatment Patterns of Chorea in North American Patients with Huntington’s Disease: Data from Enroll-HD
by: Erin Furr Stimming, et al.
Published: (2025-01-01)

Metabolic dysregulation in Huntington's disease: Neuronal and glial perspectives
by: Ching-Pang Chang, et al.
Published: (2024-10-01)