Global consensus from the PHITT consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma, hepatocellular neoplasm – not otherwise specified (HCN-NOS), hepatocellular carcinoma and fibrolamellar carcinoma after trial closure

Malignant liver tumors affecting children and adolescents are rare. In order to adequately study liver tumors occurring in this patient population and establish a more uniform approach to therapy, the three primary liver tumor consortia, SIOPEL (mainly European), COG (mainly North American) and JCCG...

Full description

Saved in:
Bibliographic Details
Main Authors: Irene Schmid, Allison F. O’Neill, Kenichiro Watanabe, Isabelle Aerts, Sophie Branchereau, Penelope R. Brock, Madhumita Dandapani, Brice Fresneau, Jim Geller, Tomoro Hishiki, Danielle Ingham, Kathelijne Kraal, Milind Ronghe, Greg Tiao, Angela Trobaugh-Lotrario, Arun Rangaswami, Michael J. Sullivan, Jozsef Zsiros, Eiso Hiyama, Marcio Malogolowkin, Marc Ansari
Format: Article
Language:English
Published: Elsevier 2025-06-01
Series:EJC Paediatric Oncology
Subjects:
Online Access:http://www.sciencedirect.com/science/article/pii/S2772610X25000236
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849422513345396736
author Irene Schmid
Allison F. O’Neill
Kenichiro Watanabe
Isabelle Aerts
Sophie Branchereau
Penelope R. Brock
Madhumita Dandapani
Brice Fresneau
Jim Geller
Tomoro Hishiki
Danielle Ingham
Kathelijne Kraal
Milind Ronghe
Greg Tiao
Angela Trobaugh-Lotrario
Arun Rangaswami
Michael J. Sullivan
Jozsef Zsiros
Eiso Hiyama
Marcio Malogolowkin
Marc Ansari
author_facet Irene Schmid
Allison F. O’Neill
Kenichiro Watanabe
Isabelle Aerts
Sophie Branchereau
Penelope R. Brock
Madhumita Dandapani
Brice Fresneau
Jim Geller
Tomoro Hishiki
Danielle Ingham
Kathelijne Kraal
Milind Ronghe
Greg Tiao
Angela Trobaugh-Lotrario
Arun Rangaswami
Michael J. Sullivan
Jozsef Zsiros
Eiso Hiyama
Marcio Malogolowkin
Marc Ansari
author_sort Irene Schmid
collection DOAJ
description Malignant liver tumors affecting children and adolescents are rare. In order to adequately study liver tumors occurring in this patient population and establish a more uniform approach to therapy, the three primary liver tumor consortia, SIOPEL (mainly European), COG (mainly North American) and JCCG (Japan), in concert, designed an international prospective clinical trial [PHITT (Paediatric Hepatic International Tumour Trial)/COGAHEP1531/JPLT4 – to be referred to as PHITT from this point forth] for the study of hepatoblastoma and hepatocellular carcinoma in children and adolescents. Recruitment to PHITT has recently concluded. The major results from this trial will be published in the next 2–3 years, therefore in the interim, we sought to provide a consensus statement on evidence-based chemotherapy guidance for hepatoblastoma and hepatocellular carcinoma of all stages.
format Article
id doaj-art-9b3f06cc83fa41528a530fa49f9868c7
institution Kabale University
issn 2772-610X
language English
publishDate 2025-06-01
publisher Elsevier
record_format Article
series EJC Paediatric Oncology
spelling doaj-art-9b3f06cc83fa41528a530fa49f9868c72025-08-20T03:31:05ZengElsevierEJC Paediatric Oncology2772-610X2025-06-01510023510.1016/j.ejcped.2025.100235Global consensus from the PHITT consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma, hepatocellular neoplasm – not otherwise specified (HCN-NOS), hepatocellular carcinoma and fibrolamellar carcinoma after trial closureIrene Schmid0Allison F. O’Neill1Kenichiro Watanabe2Isabelle Aerts3Sophie Branchereau4Penelope R. Brock5Madhumita Dandapani6Brice Fresneau7Jim Geller8Tomoro Hishiki9Danielle Ingham10Kathelijne Kraal11Milind Ronghe12Greg Tiao13Angela Trobaugh-Lotrario14Arun Rangaswami15Michael J. Sullivan16Jozsef Zsiros17Eiso Hiyama18Marcio Malogolowkin19Marc Ansari20Department of Pediatric Hematology and Oncology, Dr. von Hauner Children`s Hospital, University of Munich, LMU Munich, Germany; Correspondence to: Dr. von Hauner Children`s Hospital, Department of Pediatric Hematology and Oncology, University of Munich, LMU Munich, Lindwurmstr, Munich, Germany.Department of Pediatric Oncology, Dana-Farber and Boston Children’s Cancer and Blood Disorder Center, and Harvard Medical School, Boston, MA, USADepartment of Hematology and Oncology, Shizuoka Children's Hospital, Shizuoka, JapanInstitut Curie, PSL Research University, Oncology Center SIREDO, Paris, FranceBicetre Hospital APHP, Paris Saclay University, FranceOncology Department, Great Ormond Street Hospital for Children, NHS Foundation Trust, London, United KingdomDepartment of Paediatric Oncology, Nottingham University Hospitals NHS Trust, Nottingham, UKDepartment of Children and Adolescent Oncology, Gustave Roussy, Paris-Saclay University, Villejuif, FranceDivision of Oncology, Cincinnati Children's Hospital Medical Center, University of Cincinnati, Cincinnati, OH, USAPediatric Surgery, Chiba University Hospital, Chiba, JapanDepartment of Paediatric Oncology & Haematology, Leeds Children's Hospital, Leeds, United KingdomPrincess Maxima Center for Pediatric Oncology, Utrecht, the NetherlandsDepartment of Paediatric Oncology, Royal Hospital for Children, Glasgow, United KingdomPediatric Surgery, University of Cincinnati, Cincinnati, USAProvidence Sacred Heart Children's Hospital, Spokane, WA, USADivision of Pediatric Hematology and Oncology, University of California San Francisco, San Francisco, California, USAThe Royal Children's Hospital, Melbourne, AustraliaPrincess Maxima Center for Pediatric Oncology, Utrecht, the NetherlandsDepartment of Pediatric Surgery, Hiroshima University Hospital, Hiroshima, JapanDivision of Pediatric Hematology-Oncology, Department of Pediatrics, US Davis Comprehensive Cancer Center, Sacramento, USACansearch Research platform for Pediatric =ncology and Hematology, Faculty of Medicine, Department of Pediatrics, Gynecology and Obstetrics, University of Geneva, Switzerland; Division of Pediatric Oncology and Hematology, Department of Women, Child and Adolescent, University Geneva Hospitals, Geneva, SwitzerlandMalignant liver tumors affecting children and adolescents are rare. In order to adequately study liver tumors occurring in this patient population and establish a more uniform approach to therapy, the three primary liver tumor consortia, SIOPEL (mainly European), COG (mainly North American) and JCCG (Japan), in concert, designed an international prospective clinical trial [PHITT (Paediatric Hepatic International Tumour Trial)/COGAHEP1531/JPLT4 – to be referred to as PHITT from this point forth] for the study of hepatoblastoma and hepatocellular carcinoma in children and adolescents. Recruitment to PHITT has recently concluded. The major results from this trial will be published in the next 2–3 years, therefore in the interim, we sought to provide a consensus statement on evidence-based chemotherapy guidance for hepatoblastoma and hepatocellular carcinoma of all stages.http://www.sciencedirect.com/science/article/pii/S2772610X25000236HepatoblastomaHepatocellular CarcinomaHepatocellular Neoplasm – Not Otherwise SpecifiedInterim guidanceChildrenChemotherapy
spellingShingle Irene Schmid
Allison F. O’Neill
Kenichiro Watanabe
Isabelle Aerts
Sophie Branchereau
Penelope R. Brock
Madhumita Dandapani
Brice Fresneau
Jim Geller
Tomoro Hishiki
Danielle Ingham
Kathelijne Kraal
Milind Ronghe
Greg Tiao
Angela Trobaugh-Lotrario
Arun Rangaswami
Michael J. Sullivan
Jozsef Zsiros
Eiso Hiyama
Marcio Malogolowkin
Marc Ansari
Global consensus from the PHITT consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma, hepatocellular neoplasm – not otherwise specified (HCN-NOS), hepatocellular carcinoma and fibrolamellar carcinoma after trial closure
EJC Paediatric Oncology
Hepatoblastoma
Hepatocellular Carcinoma
Hepatocellular Neoplasm – Not Otherwise Specified
Interim guidance
Children
Chemotherapy
title Global consensus from the PHITT consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma, hepatocellular neoplasm – not otherwise specified (HCN-NOS), hepatocellular carcinoma and fibrolamellar carcinoma after trial closure
title_full Global consensus from the PHITT consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma, hepatocellular neoplasm – not otherwise specified (HCN-NOS), hepatocellular carcinoma and fibrolamellar carcinoma after trial closure
title_fullStr Global consensus from the PHITT consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma, hepatocellular neoplasm – not otherwise specified (HCN-NOS), hepatocellular carcinoma and fibrolamellar carcinoma after trial closure
title_full_unstemmed Global consensus from the PHITT consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma, hepatocellular neoplasm – not otherwise specified (HCN-NOS), hepatocellular carcinoma and fibrolamellar carcinoma after trial closure
title_short Global consensus from the PHITT consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma, hepatocellular neoplasm – not otherwise specified (HCN-NOS), hepatocellular carcinoma and fibrolamellar carcinoma after trial closure
title_sort global consensus from the phitt consortium surrounding an interim chemotherapy guidance for the treatment of children with hepatoblastoma hepatocellular neoplasm not otherwise specified hcn nos hepatocellular carcinoma and fibrolamellar carcinoma after trial closure
topic Hepatoblastoma
Hepatocellular Carcinoma
Hepatocellular Neoplasm – Not Otherwise Specified
Interim guidance
Children
Chemotherapy
url http://www.sciencedirect.com/science/article/pii/S2772610X25000236
work_keys_str_mv AT ireneschmid globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT allisonfoneill globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT kenichirowatanabe globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT isabelleaerts globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT sophiebranchereau globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT peneloperbrock globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT madhumitadandapani globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT bricefresneau globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT jimgeller globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT tomorohishiki globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT danielleingham globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT kathelijnekraal globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT milindronghe globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT gregtiao globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT angelatrobaughlotrario globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT arunrangaswami globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT michaeljsullivan globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT jozsefzsiros globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT eisohiyama globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT marciomalogolowkin globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure
AT marcansari globalconsensusfromthephittconsortiumsurroundinganinterimchemotherapyguidanceforthetreatmentofchildrenwithhepatoblastomahepatocellularneoplasmnototherwisespecifiedhcnnoshepatocellularcarcinomaandfibrolamellarcarcinomaaftertrialclosure