RBM4-mediated intron excision of Hsf1 induces BDNF for cerebellar foliation

Abstract Brain-derived neurotrophic factor (BDNF) plays important roles in brain development and neural function. Constitutive knockout of the splicing regulator RBM4 reduces BDNF expression in the developing brain and causes cerebellar hypoplasia, an autism-like feature. Here, we show that Rbm4 kno...

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Main Authors: Chiu-Lun Shen, Yu-Young Tsai, Shen-Ju Chou, Yao-Ming Chang, Woan-Yuh Tarn
Format: Article
Language:English
Published: Nature Portfolio 2024-12-01
Series:Communications Biology
Online Access:https://doi.org/10.1038/s42003-024-07328-6
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author Chiu-Lun Shen
Yu-Young Tsai
Shen-Ju Chou
Yao-Ming Chang
Woan-Yuh Tarn
author_facet Chiu-Lun Shen
Yu-Young Tsai
Shen-Ju Chou
Yao-Ming Chang
Woan-Yuh Tarn
author_sort Chiu-Lun Shen
collection DOAJ
description Abstract Brain-derived neurotrophic factor (BDNF) plays important roles in brain development and neural function. Constitutive knockout of the splicing regulator RBM4 reduces BDNF expression in the developing brain and causes cerebellar hypoplasia, an autism-like feature. Here, we show that Rbm4 knockout induced intron 6 retention of Hsf1, leading to downregulation of HSF1 protein and its downstream target BDNF. RBM4-mediated Hsf1 intron excision regulated BDNF expression in cultured granule cells. Ectopic expression of HSF1 restored cerebellar foliation and motor learning of Rbm4-knockout mice, indicating a critical role for RBM4-HSF1-BDNF in cerebellar foliation. Moreover, N-methyl-D-aspartate receptor (NMDAR) signaling promoted the expression and nuclear translocation of RBM4, and hence increased the expression of both HSF and BDNF. A short CU-rich motif was responsible for NMDAR- and RBM4-mediated intron excision. Finally, RBM4 and polypyrimidine tract binding (PTB) proteins play antagonistic roles in intron excision, suggesting a role for splicing regulation in BDNF expression.
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issn 2399-3642
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spelling doaj-art-99a62d99c6994b66a253aa925e160c192025-08-20T02:53:48ZengNature PortfolioCommunications Biology2399-36422024-12-017111310.1038/s42003-024-07328-6RBM4-mediated intron excision of Hsf1 induces BDNF for cerebellar foliationChiu-Lun Shen0Yu-Young Tsai1Shen-Ju Chou2Yao-Ming Chang3Woan-Yuh Tarn4Institute of Biomedical Sciences, Academia SinicaInstitute of Biomedical Sciences, Academia SinicaInstitute of Cellular and Organismic Biology, Academia SinicaInstitute of Biomedical Sciences, Academia SinicaInstitute of Biomedical Sciences, Academia SinicaAbstract Brain-derived neurotrophic factor (BDNF) plays important roles in brain development and neural function. Constitutive knockout of the splicing regulator RBM4 reduces BDNF expression in the developing brain and causes cerebellar hypoplasia, an autism-like feature. Here, we show that Rbm4 knockout induced intron 6 retention of Hsf1, leading to downregulation of HSF1 protein and its downstream target BDNF. RBM4-mediated Hsf1 intron excision regulated BDNF expression in cultured granule cells. Ectopic expression of HSF1 restored cerebellar foliation and motor learning of Rbm4-knockout mice, indicating a critical role for RBM4-HSF1-BDNF in cerebellar foliation. Moreover, N-methyl-D-aspartate receptor (NMDAR) signaling promoted the expression and nuclear translocation of RBM4, and hence increased the expression of both HSF and BDNF. A short CU-rich motif was responsible for NMDAR- and RBM4-mediated intron excision. Finally, RBM4 and polypyrimidine tract binding (PTB) proteins play antagonistic roles in intron excision, suggesting a role for splicing regulation in BDNF expression.https://doi.org/10.1038/s42003-024-07328-6
spellingShingle Chiu-Lun Shen
Yu-Young Tsai
Shen-Ju Chou
Yao-Ming Chang
Woan-Yuh Tarn
RBM4-mediated intron excision of Hsf1 induces BDNF for cerebellar foliation
Communications Biology
title RBM4-mediated intron excision of Hsf1 induces BDNF for cerebellar foliation
title_full RBM4-mediated intron excision of Hsf1 induces BDNF for cerebellar foliation
title_fullStr RBM4-mediated intron excision of Hsf1 induces BDNF for cerebellar foliation
title_full_unstemmed RBM4-mediated intron excision of Hsf1 induces BDNF for cerebellar foliation
title_short RBM4-mediated intron excision of Hsf1 induces BDNF for cerebellar foliation
title_sort rbm4 mediated intron excision of hsf1 induces bdnf for cerebellar foliation
url https://doi.org/10.1038/s42003-024-07328-6
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AT shenjuchou rbm4mediatedintronexcisionofhsf1inducesbdnfforcerebellarfoliation
AT yaomingchang rbm4mediatedintronexcisionofhsf1inducesbdnfforcerebellarfoliation
AT woanyuhtarn rbm4mediatedintronexcisionofhsf1inducesbdnfforcerebellarfoliation