Profiling of Circulating Tumor Cells for Screening of Selective Inhibitors of Tumor‐Initiating Stem‐Like Cells

Abstract A critical barrier to effective cancer therapy is the improvement of drug selectivity, toxicity, and reduced recurrence of tumors expanded from tumor‐initiating stem‐like cells (TICs). The aim is to identify circulating tumor cell (CTC)‐biomarkers and to identify an effective combination of...

Full description

Saved in:
Bibliographic Details
Main Authors: Chia‐Lin Chen, Juan Carlos Hernandez, Dinesh Babu Uthaya Kumar, Tatsuya Machida, Stanley M. Tahara, Anthony El‐Khoueiry, Meng Li, Vasu Punj, Suresh Kumar Swaminathan, Ameya Kirtane, Yibu Chen, Jayanth Panyam, Keigo Machida
Format: Article
Language:English
Published: Wiley 2023-05-01
Series:Advanced Science
Subjects:
Online Access:https://doi.org/10.1002/advs.202206812
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849404580392075264
author Chia‐Lin Chen
Juan Carlos Hernandez
Dinesh Babu Uthaya Kumar
Tatsuya Machida
Stanley M. Tahara
Anthony El‐Khoueiry
Meng Li
Vasu Punj
Suresh Kumar Swaminathan
Ameya Kirtane
Yibu Chen
Jayanth Panyam
Keigo Machida
author_facet Chia‐Lin Chen
Juan Carlos Hernandez
Dinesh Babu Uthaya Kumar
Tatsuya Machida
Stanley M. Tahara
Anthony El‐Khoueiry
Meng Li
Vasu Punj
Suresh Kumar Swaminathan
Ameya Kirtane
Yibu Chen
Jayanth Panyam
Keigo Machida
author_sort Chia‐Lin Chen
collection DOAJ
description Abstract A critical barrier to effective cancer therapy is the improvement of drug selectivity, toxicity, and reduced recurrence of tumors expanded from tumor‐initiating stem‐like cells (TICs). The aim is to identify circulating tumor cell (CTC)‐biomarkers and to identify an effective combination of TIC‐specific, repurposed federal drug administration (FDA)‐approved drugs. Three different types of high‐throughput screens targeting the TIC population are employed: these include a CD133 (+) cell viability screen, a NANOG expression screen, and a drug combination screen. When combined in a refined secondary screening approach that targets Nanog expression with the same FDA‐approved drug library, histone deacetylase (HDAC) inhibitor(s) combined with all‐trans retinoic acid (ATRA) demonstrate the highest efficacy for inhibition of TIC growth in vitro and in vivo. Addition of immune checkpoint inhibitor further decreases recurrence and extends PDX mouse survival. RNA‐seq analysis of TICs reveals that combined drug treatment reduces many Toll‐like receptors (TLR) and stemness genes through repression of the lncRNA MIR22HG. This downregulation induces PTEN and TET2, leading to loss of the self‐renewal property of TICs. Thus, CTC biomarker analysis would predict the prognosis and therapy response to this drug combination. In general, biomarker‐guided stratification of HCC patients and TIC‐targeted therapy should eradicate TICs to extend HCC patient survival.
format Article
id doaj-art-999c7bce83734a00a201565cd6d18f4d
institution Kabale University
issn 2198-3844
language English
publishDate 2023-05-01
publisher Wiley
record_format Article
series Advanced Science
spelling doaj-art-999c7bce83734a00a201565cd6d18f4d2025-08-20T03:36:57ZengWileyAdvanced Science2198-38442023-05-011014n/an/a10.1002/advs.202206812Profiling of Circulating Tumor Cells for Screening of Selective Inhibitors of Tumor‐Initiating Stem‐Like CellsChia‐Lin Chen0Juan Carlos Hernandez1Dinesh Babu Uthaya Kumar2Tatsuya Machida3Stanley M. Tahara4Anthony El‐Khoueiry5Meng Li6Vasu Punj7Suresh Kumar Swaminathan8Ameya Kirtane9Yibu Chen10Jayanth Panyam11Keigo Machida12Departments of Molecular Microbiology and Immunology University of Southern California Los Angeles CA 90033 USADepartments of Molecular Microbiology and Immunology University of Southern California Los Angeles CA 90033 USADepartments of Molecular Microbiology and Immunology University of Southern California Los Angeles CA 90033 USADepartments of Molecular Microbiology and Immunology University of Southern California Los Angeles CA 90033 USADepartments of Molecular Microbiology and Immunology University of Southern California Los Angeles CA 90033 USANorris Comprehensive Cancer Center University of Southern California Keck School of Medicine Los Angeles CA 90033 USANorris Medical Library 2003 Zonal Ave Los Angeles CA 90089 USADepartment of Medicine University of Southern California Keck School of Medicine and Norris Comprehensive Cancer Center Los Angeles CA 90089 USADepartment of Pharmaceutics University of Minnesota Minneapolis MN 55455 USADepartment of Pharmaceutics University of Minnesota Minneapolis MN 55455 USANorris Medical Library 2003 Zonal Ave Los Angeles CA 90089 USADepartment of Pharmaceutics University of Minnesota Minneapolis MN 55455 USADepartments of Molecular Microbiology and Immunology University of Southern California Los Angeles CA 90033 USAAbstract A critical barrier to effective cancer therapy is the improvement of drug selectivity, toxicity, and reduced recurrence of tumors expanded from tumor‐initiating stem‐like cells (TICs). The aim is to identify circulating tumor cell (CTC)‐biomarkers and to identify an effective combination of TIC‐specific, repurposed federal drug administration (FDA)‐approved drugs. Three different types of high‐throughput screens targeting the TIC population are employed: these include a CD133 (+) cell viability screen, a NANOG expression screen, and a drug combination screen. When combined in a refined secondary screening approach that targets Nanog expression with the same FDA‐approved drug library, histone deacetylase (HDAC) inhibitor(s) combined with all‐trans retinoic acid (ATRA) demonstrate the highest efficacy for inhibition of TIC growth in vitro and in vivo. Addition of immune checkpoint inhibitor further decreases recurrence and extends PDX mouse survival. RNA‐seq analysis of TICs reveals that combined drug treatment reduces many Toll‐like receptors (TLR) and stemness genes through repression of the lncRNA MIR22HG. This downregulation induces PTEN and TET2, leading to loss of the self‐renewal property of TICs. Thus, CTC biomarker analysis would predict the prognosis and therapy response to this drug combination. In general, biomarker‐guided stratification of HCC patients and TIC‐targeted therapy should eradicate TICs to extend HCC patient survival.https://doi.org/10.1002/advs.202206812alcoholhepatocellular carcinoma (HCC)tumor‐initiating stem‐like cells (TIC)
spellingShingle Chia‐Lin Chen
Juan Carlos Hernandez
Dinesh Babu Uthaya Kumar
Tatsuya Machida
Stanley M. Tahara
Anthony El‐Khoueiry
Meng Li
Vasu Punj
Suresh Kumar Swaminathan
Ameya Kirtane
Yibu Chen
Jayanth Panyam
Keigo Machida
Profiling of Circulating Tumor Cells for Screening of Selective Inhibitors of Tumor‐Initiating Stem‐Like Cells
Advanced Science
alcohol
hepatocellular carcinoma (HCC)
tumor‐initiating stem‐like cells (TIC)
title Profiling of Circulating Tumor Cells for Screening of Selective Inhibitors of Tumor‐Initiating Stem‐Like Cells
title_full Profiling of Circulating Tumor Cells for Screening of Selective Inhibitors of Tumor‐Initiating Stem‐Like Cells
title_fullStr Profiling of Circulating Tumor Cells for Screening of Selective Inhibitors of Tumor‐Initiating Stem‐Like Cells
title_full_unstemmed Profiling of Circulating Tumor Cells for Screening of Selective Inhibitors of Tumor‐Initiating Stem‐Like Cells
title_short Profiling of Circulating Tumor Cells for Screening of Selective Inhibitors of Tumor‐Initiating Stem‐Like Cells
title_sort profiling of circulating tumor cells for screening of selective inhibitors of tumor initiating stem like cells
topic alcohol
hepatocellular carcinoma (HCC)
tumor‐initiating stem‐like cells (TIC)
url https://doi.org/10.1002/advs.202206812
work_keys_str_mv AT chialinchen profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT juancarloshernandez profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT dineshbabuuthayakumar profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT tatsuyamachida profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT stanleymtahara profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT anthonyelkhoueiry profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT mengli profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT vasupunj profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT sureshkumarswaminathan profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT ameyakirtane profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT yibuchen profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT jayanthpanyam profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells
AT keigomachida profilingofcirculatingtumorcellsforscreeningofselectiveinhibitorsoftumorinitiatingstemlikecells