Efficacy and safety of hematopoietic stem cell transplantation vs. immunosuppressive therapy in patients with hepatitis-associated aplastic anemia: a systematic review and meta-analysis

The present study aimed to compare the efficacy and safety of hematopoietic stem cell transplantation (HSCT) and immunosuppressive therapy (IST) for hepatitis-associated aplastic anemia (HAAA). Studies comparing HSCT with IST in HAAA were retrieved from inception to July 22, 2024, including 12 studi...

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Main Authors: Yaonan Hong, Qi Liu, Zhuonan Sun, Peicheng Wang, Xu Wang, Ziying Su, Yuzhu Li, Wenbin Liu, Huijin Hu, Yingying Shen, Baodong Ye, Yuhong Zhou, Shan Liu, Dijiong Wu
Format: Article
Language:English
Published: Taylor & Francis Group 2025-12-01
Series:Hematology
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Online Access:https://www.tandfonline.com/doi/10.1080/16078454.2025.2548990
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author Yaonan Hong
Qi Liu
Zhuonan Sun
Peicheng Wang
Xu Wang
Ziying Su
Yuzhu Li
Wenbin Liu
Huijin Hu
Yingying Shen
Baodong Ye
Yuhong Zhou
Shan Liu
Dijiong Wu
author_facet Yaonan Hong
Qi Liu
Zhuonan Sun
Peicheng Wang
Xu Wang
Ziying Su
Yuzhu Li
Wenbin Liu
Huijin Hu
Yingying Shen
Baodong Ye
Yuhong Zhou
Shan Liu
Dijiong Wu
author_sort Yaonan Hong
collection DOAJ
description The present study aimed to compare the efficacy and safety of hematopoietic stem cell transplantation (HSCT) and immunosuppressive therapy (IST) for hepatitis-associated aplastic anemia (HAAA). Studies comparing HSCT with IST in HAAA were retrieved from inception to July 22, 2024, including 12 studies with a total of 544 cases for meta-analysis. Meta-analysis demonstrated significantly superior outcomes in the HSCT group versus IST, which was manifested as lower overall mortality (P < 0.01), higher overall response rate (P < 0.001), and improved five-year overall survival (P < 0.05), yielding a pooled RR of 1.67 (95% CI: 1.15–2.44), 0.75 (95% CI: 0.66–0.86) and 0.88 (95% CI: 0.78–0.99), respectively. However, no benefit was observed in one-year survival (P = 0.08). Further subgroup analysis indicated that the advantage of mortality (P < 0.05, RR = 1.67, 95% CI: 1.10–2.55) and five-year overall survival (P = 0.05, RR = 0.84, 95% CI: 0.71–1.00) only achieved in patients under 20 years old. There was no significant difference in the overall response and one-year overall survival for each age group. Additionally, for the IST selection, a combination of cyclosporine (CSA) and antithymocyte globulin/antilymphocyte globulin (ATG/ALG) was preferred over the CSA-only regimen (effectiveness of 78.57% vs. 50.00%), although the difference was not statistically significant (P = 0.10, RR = 1.56, 95% CI: 0.92–2.66). This study showed that HSCT had a higher effective rate, greater long-term survival and lower mortality compared to IST, especially for patients under 20 years old, who should receive HSCT treatment as possible.
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spelling doaj-art-98356f39911f4b62bb8a7fecbdc9e8a22025-08-26T08:28:44ZengTaylor & Francis GroupHematology1607-84542025-12-0130110.1080/16078454.2025.2548990Efficacy and safety of hematopoietic stem cell transplantation vs. immunosuppressive therapy in patients with hepatitis-associated aplastic anemia: a systematic review and meta-analysisYaonan Hong0Qi Liu1Zhuonan Sun2Peicheng Wang3Xu Wang4Ziying Su5Yuzhu Li6Wenbin Liu7Huijin Hu8Yingying Shen9Baodong Ye10Yuhong Zhou11Shan Liu12Dijiong Wu13The First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe First School of Clinical Medicine, Zhejiang Chinese Medical University, Hangzhou, People’s Republic of ChinaThe present study aimed to compare the efficacy and safety of hematopoietic stem cell transplantation (HSCT) and immunosuppressive therapy (IST) for hepatitis-associated aplastic anemia (HAAA). Studies comparing HSCT with IST in HAAA were retrieved from inception to July 22, 2024, including 12 studies with a total of 544 cases for meta-analysis. Meta-analysis demonstrated significantly superior outcomes in the HSCT group versus IST, which was manifested as lower overall mortality (P < 0.01), higher overall response rate (P < 0.001), and improved five-year overall survival (P < 0.05), yielding a pooled RR of 1.67 (95% CI: 1.15–2.44), 0.75 (95% CI: 0.66–0.86) and 0.88 (95% CI: 0.78–0.99), respectively. However, no benefit was observed in one-year survival (P = 0.08). Further subgroup analysis indicated that the advantage of mortality (P < 0.05, RR = 1.67, 95% CI: 1.10–2.55) and five-year overall survival (P = 0.05, RR = 0.84, 95% CI: 0.71–1.00) only achieved in patients under 20 years old. There was no significant difference in the overall response and one-year overall survival for each age group. Additionally, for the IST selection, a combination of cyclosporine (CSA) and antithymocyte globulin/antilymphocyte globulin (ATG/ALG) was preferred over the CSA-only regimen (effectiveness of 78.57% vs. 50.00%), although the difference was not statistically significant (P = 0.10, RR = 1.56, 95% CI: 0.92–2.66). This study showed that HSCT had a higher effective rate, greater long-term survival and lower mortality compared to IST, especially for patients under 20 years old, who should receive HSCT treatment as possible.https://www.tandfonline.com/doi/10.1080/16078454.2025.2548990Hepatitis-associated aplastic anemiaHematopoietic stem cell transplantationImmunosuppressive therapyMeta-analysis
spellingShingle Yaonan Hong
Qi Liu
Zhuonan Sun
Peicheng Wang
Xu Wang
Ziying Su
Yuzhu Li
Wenbin Liu
Huijin Hu
Yingying Shen
Baodong Ye
Yuhong Zhou
Shan Liu
Dijiong Wu
Efficacy and safety of hematopoietic stem cell transplantation vs. immunosuppressive therapy in patients with hepatitis-associated aplastic anemia: a systematic review and meta-analysis
Hematology
Hepatitis-associated aplastic anemia
Hematopoietic stem cell transplantation
Immunosuppressive therapy
Meta-analysis
title Efficacy and safety of hematopoietic stem cell transplantation vs. immunosuppressive therapy in patients with hepatitis-associated aplastic anemia: a systematic review and meta-analysis
title_full Efficacy and safety of hematopoietic stem cell transplantation vs. immunosuppressive therapy in patients with hepatitis-associated aplastic anemia: a systematic review and meta-analysis
title_fullStr Efficacy and safety of hematopoietic stem cell transplantation vs. immunosuppressive therapy in patients with hepatitis-associated aplastic anemia: a systematic review and meta-analysis
title_full_unstemmed Efficacy and safety of hematopoietic stem cell transplantation vs. immunosuppressive therapy in patients with hepatitis-associated aplastic anemia: a systematic review and meta-analysis
title_short Efficacy and safety of hematopoietic stem cell transplantation vs. immunosuppressive therapy in patients with hepatitis-associated aplastic anemia: a systematic review and meta-analysis
title_sort efficacy and safety of hematopoietic stem cell transplantation vs immunosuppressive therapy in patients with hepatitis associated aplastic anemia a systematic review and meta analysis
topic Hepatitis-associated aplastic anemia
Hematopoietic stem cell transplantation
Immunosuppressive therapy
Meta-analysis
url https://www.tandfonline.com/doi/10.1080/16078454.2025.2548990
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