Transplantation of Human Peripheral Stem and Progenitor Cells to Humanized Mouse Model for Systemic Lupus Erythematosus

Syahrul Chilmi, Dina Fauziah, Matthew Brian Khrisna, Ifa Fauziah, Friska Supriyanto, Kusworini Handono, Kevin Reinaldo Sunjaya, Wimardy Leonard Wijaya, Mustofa Aidid, Hani Susianti Clinical Pathology Department, Faculty of Medicine Brawijaya University/Dr. Saiful Anwar General Hospital, Malang, Indo...

Full description

Saved in:
Bibliographic Details
Main Authors: Chilmi S, Fauziah D, Khrisna MB, Fauziah I, Supriyanto F, Handono K, Sunjaya KR, Wijaya WL, Aidid M, Susianti H
Format: Article
Language:English
Published: Dove Medical Press 2025-06-01
Series:Journal of Blood Medicine
Subjects:
Online Access:https://www.dovepress.com/transplantation-of-human-peripheral-stem-and-progenitor-cells-to-human-peer-reviewed-fulltext-article-JBM
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849433549818560512
author Chilmi S
Fauziah D
Khrisna MB
Fauziah I
Supriyanto F
Handono K
Sunjaya KR
Wijaya WL
Aidid M
Susianti H
author_facet Chilmi S
Fauziah D
Khrisna MB
Fauziah I
Supriyanto F
Handono K
Sunjaya KR
Wijaya WL
Aidid M
Susianti H
author_sort Chilmi S
collection DOAJ
description Syahrul Chilmi, Dina Fauziah, Matthew Brian Khrisna, Ifa Fauziah, Friska Supriyanto, Kusworini Handono, Kevin Reinaldo Sunjaya, Wimardy Leonard Wijaya, Mustofa Aidid, Hani Susianti Clinical Pathology Department, Faculty of Medicine Brawijaya University/Dr. Saiful Anwar General Hospital, Malang, IndonesiaCorrespondence: Hani Susianti, Clinical Pathology Department, Faculty of Medicine Brawijaya University/Dr. Saiful Anwar General Hospital, Jaksa Agung Suprapto Street Number 2, Malang, East Java, 65111, Indonesia, Tel +6281334760295, Email hanisusianti.fk@ub.ac.idIntroduction: Systemic Lupus Erythematosus (SLE) is an autoimmune disease characterized by damaged and dysregulated immune system due to breakdown in the selection process during clonal growth of immune cells. Studies have shown that patients with systemic lupus erythematosus (SLE) display altered gene expression patterns and increased double-stranded DNA breaks within their hematopoietic stem and progenitor cells (HSPC). However, the current animal models for SLE found in the existing literature predominantly emphasize the use of peripheral blood mononuclear cells (PBMC) over HSPC for the creation of humanized mouse models. Nevertheless, these prior models were constrained by the limited efficiency of human cell engraftment and limited PBMC ability to replicate the capacity of HSPC to generate human SLE cells that can engraft host mice, thus making the transplant protocol inadequate.Patients and Methods: Transplantation was initiated by extracting HSPC from stable SLE patients by leukapheresis. The collected cells were assessed for purity before storage at − 80 °C. Humanized mice were conditioned with cyclophosphamide and total-body irradiation before receiving the HSPC transplant. After transplantation, the mice were administered human granulocyte-colony stimulating factor and sacrificed to evaluate autoantibodies and HSPC in their bone marrow and blood samples. Statistical analysis was performed using Student’s t-test and one-way ANOVA.Results: Upon human stem cells engravement into mice, we found a noteworthy presence of HSPC, as evidenced by the positive expression of hCD45, hCD34, and/or hCD44, and the production of human antinuclear antibodies. The results indicated that the transplanted mice generated reactive autoantibodies against human cells, similar to that observed in the human donor patient. These findings shed light on the survival and behavior of transplanted human stem cells in a mouse model.Conclusion: In this study, we successfully induced immunodeficiency in mice for xenotransplantation with human peripheral stem cells.Keywords: autoimmune, experimental, humanized mouse, stem cells
format Article
id doaj-art-8f5e2bd3b33f430e8970cca9533fe1b6
institution Kabale University
issn 1179-2736
language English
publishDate 2025-06-01
publisher Dove Medical Press
record_format Article
series Journal of Blood Medicine
spelling doaj-art-8f5e2bd3b33f430e8970cca9533fe1b62025-08-20T03:27:00ZengDove Medical PressJournal of Blood Medicine1179-27362025-06-01Volume 16Issue 1269277103569Transplantation of Human Peripheral Stem and Progenitor Cells to Humanized Mouse Model for Systemic Lupus ErythematosusChilmi S0Fauziah D1Khrisna MB2Fauziah I3Supriyanto F4Handono K5Sunjaya KR6Wijaya WL7Aidid M8Susianti H9Clinical Pathology and Laboratory MedicineClinical pathologyClinical Pathology DepartmentClinical Pathology DepartmentClinical Pathology DepartmentDepartment of Clinical Pathology, Faculty of MedicineClinical Pathology DepartmentClinical Pathology DepartmentClinical Pathology DepartmentClinical Pathology DepartmentSyahrul Chilmi, Dina Fauziah, Matthew Brian Khrisna, Ifa Fauziah, Friska Supriyanto, Kusworini Handono, Kevin Reinaldo Sunjaya, Wimardy Leonard Wijaya, Mustofa Aidid, Hani Susianti Clinical Pathology Department, Faculty of Medicine Brawijaya University/Dr. Saiful Anwar General Hospital, Malang, IndonesiaCorrespondence: Hani Susianti, Clinical Pathology Department, Faculty of Medicine Brawijaya University/Dr. Saiful Anwar General Hospital, Jaksa Agung Suprapto Street Number 2, Malang, East Java, 65111, Indonesia, Tel +6281334760295, Email hanisusianti.fk@ub.ac.idIntroduction: Systemic Lupus Erythematosus (SLE) is an autoimmune disease characterized by damaged and dysregulated immune system due to breakdown in the selection process during clonal growth of immune cells. Studies have shown that patients with systemic lupus erythematosus (SLE) display altered gene expression patterns and increased double-stranded DNA breaks within their hematopoietic stem and progenitor cells (HSPC). However, the current animal models for SLE found in the existing literature predominantly emphasize the use of peripheral blood mononuclear cells (PBMC) over HSPC for the creation of humanized mouse models. Nevertheless, these prior models were constrained by the limited efficiency of human cell engraftment and limited PBMC ability to replicate the capacity of HSPC to generate human SLE cells that can engraft host mice, thus making the transplant protocol inadequate.Patients and Methods: Transplantation was initiated by extracting HSPC from stable SLE patients by leukapheresis. The collected cells were assessed for purity before storage at − 80 °C. Humanized mice were conditioned with cyclophosphamide and total-body irradiation before receiving the HSPC transplant. After transplantation, the mice were administered human granulocyte-colony stimulating factor and sacrificed to evaluate autoantibodies and HSPC in their bone marrow and blood samples. Statistical analysis was performed using Student’s t-test and one-way ANOVA.Results: Upon human stem cells engravement into mice, we found a noteworthy presence of HSPC, as evidenced by the positive expression of hCD45, hCD34, and/or hCD44, and the production of human antinuclear antibodies. The results indicated that the transplanted mice generated reactive autoantibodies against human cells, similar to that observed in the human donor patient. These findings shed light on the survival and behavior of transplanted human stem cells in a mouse model.Conclusion: In this study, we successfully induced immunodeficiency in mice for xenotransplantation with human peripheral stem cells.Keywords: autoimmune, experimental, humanized mouse, stem cellshttps://www.dovepress.com/transplantation-of-human-peripheral-stem-and-progenitor-cells-to-human-peer-reviewed-fulltext-article-JBMAutoimmuneExperimentalHumanized MouseStem cells
spellingShingle Chilmi S
Fauziah D
Khrisna MB
Fauziah I
Supriyanto F
Handono K
Sunjaya KR
Wijaya WL
Aidid M
Susianti H
Transplantation of Human Peripheral Stem and Progenitor Cells to Humanized Mouse Model for Systemic Lupus Erythematosus
Journal of Blood Medicine
Autoimmune
Experimental
Humanized Mouse
Stem cells
title Transplantation of Human Peripheral Stem and Progenitor Cells to Humanized Mouse Model for Systemic Lupus Erythematosus
title_full Transplantation of Human Peripheral Stem and Progenitor Cells to Humanized Mouse Model for Systemic Lupus Erythematosus
title_fullStr Transplantation of Human Peripheral Stem and Progenitor Cells to Humanized Mouse Model for Systemic Lupus Erythematosus
title_full_unstemmed Transplantation of Human Peripheral Stem and Progenitor Cells to Humanized Mouse Model for Systemic Lupus Erythematosus
title_short Transplantation of Human Peripheral Stem and Progenitor Cells to Humanized Mouse Model for Systemic Lupus Erythematosus
title_sort transplantation of human peripheral stem and progenitor cells to humanized mouse model for systemic lupus erythematosus
topic Autoimmune
Experimental
Humanized Mouse
Stem cells
url https://www.dovepress.com/transplantation-of-human-peripheral-stem-and-progenitor-cells-to-human-peer-reviewed-fulltext-article-JBM
work_keys_str_mv AT chilmis transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT fauziahd transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT khrisnamb transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT fauziahi transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT supriyantof transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT handonok transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT sunjayakr transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT wijayawl transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT aididm transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus
AT susiantih transplantationofhumanperipheralstemandprogenitorcellstohumanizedmousemodelforsystemiclupuserythematosus