A database study of the safety and effectiveness of daily growth hormone in treating more than 80,000 children with growth disorders worldwide: a plain language summary of publication

Summary Researchers looked at data from the largest and longest-running database of children with growth disorders who were treated with daily injections of a brand of growth hormone called Genotropin . The researchers used these data to better understand the safety and effectiveness of daily growth...

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Main Authors: Mohamad Maghnie, Michael B. Ranke, Mitchell E. Geffner, Elpis Vlachopapadopoulou, Lourdes Ibáñez, Martin Carlsson, Wayne Cutfield, Raoul Rooman, Roy Gomez, Michael P. Wajnrajch, Agnès Linglart, Renata Stawerska, Peter E. Clayton, Feyza Darendeliler, Anita C. S. Hokken-Koelega, Reiko Horikawa, Toshiaki Tanaka, Helmuth-Günther Dörr, Michel Polak, Adda Grimberg
Format: Article
Language:English
Published: SAGE Publishing 2025-08-01
Series:Therapeutic Advances in Endocrinology and Metabolism
Online Access:https://doi.org/10.1177/20420188251345556
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author Mohamad Maghnie
Michael B. Ranke
Mitchell E. Geffner
Elpis Vlachopapadopoulou
Lourdes Ibáñez
Martin Carlsson
Wayne Cutfield
Raoul Rooman
Roy Gomez
Michael P. Wajnrajch
Agnès Linglart
Renata Stawerska
Peter E. Clayton
Feyza Darendeliler
Anita C. S. Hokken-Koelega
Reiko Horikawa
Toshiaki Tanaka
Helmuth-Günther Dörr
Michel Polak
Adda Grimberg
author_facet Mohamad Maghnie
Michael B. Ranke
Mitchell E. Geffner
Elpis Vlachopapadopoulou
Lourdes Ibáñez
Martin Carlsson
Wayne Cutfield
Raoul Rooman
Roy Gomez
Michael P. Wajnrajch
Agnès Linglart
Renata Stawerska
Peter E. Clayton
Feyza Darendeliler
Anita C. S. Hokken-Koelega
Reiko Horikawa
Toshiaki Tanaka
Helmuth-Günther Dörr
Michel Polak
Adda Grimberg
author_sort Mohamad Maghnie
collection DOAJ
description Summary Researchers looked at data from the largest and longest-running database of children with growth disorders who were treated with daily injections of a brand of growth hormone called Genotropin . The researchers used these data to better understand the safety and effectiveness of daily growth hormone treatment. Researchers showed that daily growth hormone treatment: ○ Increased the children’s heights, measured after 1 year of treatment. This was seen for all of the growth disorders studied. ○ Increased growth in children of different ages, with higher growth seen in children who had begun treatment before they started puberty. ○ Allowed short children to reach an adult height within the normal range. This was true even for children who did not begin treatment until early adolescence. ○ Was safe. Only a very small percentage (3%) of children had any side effects related to growth hormone treatment, the most common of which was headaches. When children reach the end of puberty, their growth plates close and they are unable to grow any taller. Once this happens, growth hormone treatment cannot increase their growth further and treatment should be stopped. The purpose of this plain language summary is to help you to understand the findings from recent research. Somatropin is used to treat the conditions under study that are discussed in this summary. Approval varies by country; please check with your local healthcare provider for more details. The results of this study may differ from those of other studies. Health professionals should make treatment decisions based on all available evidence and not on the results of a single study.
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spelling doaj-art-8eec64e7de474c5ab070a48cbf71fdbe2025-08-20T04:03:12ZengSAGE PublishingTherapeutic Advances in Endocrinology and Metabolism2042-01962025-08-011610.1177/20420188251345556A database study of the safety and effectiveness of daily growth hormone in treating more than 80,000 children with growth disorders worldwide: a plain language summary of publicationMohamad Maghnie0Michael B. Ranke1Mitchell E. Geffner2Elpis Vlachopapadopoulou3Lourdes Ibáñez4Martin Carlsson5Wayne Cutfield6Raoul Rooman7Roy Gomez8Michael P. Wajnrajch9Agnès Linglart10Renata Stawerska11Peter E. Clayton12Feyza Darendeliler13Anita C. S. Hokken-Koelega14Reiko Horikawa15Toshiaki Tanaka16Helmuth-Günther Dörr17Michel Polak18Adda Grimberg19Department of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genova, Genova, ItalyDepartment of Pediatric Endocrinology, University Children’s Hospital, Tübingen, GermanyDepartment of Pediatrics, The Saban Research Institute, Children’s Hospital Los Angeles, Keck School of Medicine of the University of Southern California, Los Angeles, CA, USADepartment of Endocrinology, Growth and Development, Children’s Hospital P. & A. Kyriakou, Athens, GreeceCentro de Investigación Biomédica en Red de Diabetes y Enfermedades Metabólicas Asociadas, Instituto de Salud Carlos III (Biomedical Research Center for Diabetes and Associated Metabolic Diseases, Carlos III Health Institute), Madrid, SpainInflammation and Immunology, Pfizer Inc., New York, NY, USAPaediatric Endocrinology, Liggins Institute, University of Auckland, Auckland, New ZealandPendoCon, Putte, BelgiumPfizer Biopharmaceuticals Group, Pfizer Pte Ltd, Singapore, SingaporeDepartment of Pediatrics, New York University Grossman School of Medicine, New York, NY, USAAPHP, Reference Center for Rare Diseases of Calcium and Phosphate Metabolism, and Filière OSCAR, endo ERN and ERN BOND, Paris, FranceDepartment of Paediatric Endocrinology, Medical University of Lodz, Lodz, PolandDevelopmental Biology and Medicine, Faculty of Biology, Medicine and Health, University of Manchester, Manchester, UKPediatric Endocrinology Unit, İstanbul Faculty of Medicine, İstanbul, TurkeyDepartment of Pediatrics, Subdivision of Endocrinology, Erasmus University Medical Center, Rotterdam, The NetherlandsDivision of Endocrinology and Metabolism, National Center for Child Health and Development, Tokyo, JapanTanaka Growth Clinic, Tokyo, JapanDivision of Pediatric Endocrinology, Department of Pediatrics and Adolescent Medicine, Friedrich-Alexander University of Erlangen-Nürnberg, Erlangen, GermanyPaediatric Endocrinology, Gynaecology and Diabetology Department, Hôpital Universitaire Necker Enfants Malades, Université de Paris Cité (Necker Children’s University Hospital, University of Paris City), Paris, FranceDivision of Pediatric Endocrinology and Diabetes, Children’s Hospital of Philadelphia, Philadelphia, PA, USASummary Researchers looked at data from the largest and longest-running database of children with growth disorders who were treated with daily injections of a brand of growth hormone called Genotropin . The researchers used these data to better understand the safety and effectiveness of daily growth hormone treatment. Researchers showed that daily growth hormone treatment: ○ Increased the children’s heights, measured after 1 year of treatment. This was seen for all of the growth disorders studied. ○ Increased growth in children of different ages, with higher growth seen in children who had begun treatment before they started puberty. ○ Allowed short children to reach an adult height within the normal range. This was true even for children who did not begin treatment until early adolescence. ○ Was safe. Only a very small percentage (3%) of children had any side effects related to growth hormone treatment, the most common of which was headaches. When children reach the end of puberty, their growth plates close and they are unable to grow any taller. Once this happens, growth hormone treatment cannot increase their growth further and treatment should be stopped. The purpose of this plain language summary is to help you to understand the findings from recent research. Somatropin is used to treat the conditions under study that are discussed in this summary. Approval varies by country; please check with your local healthcare provider for more details. The results of this study may differ from those of other studies. Health professionals should make treatment decisions based on all available evidence and not on the results of a single study.https://doi.org/10.1177/20420188251345556
spellingShingle Mohamad Maghnie
Michael B. Ranke
Mitchell E. Geffner
Elpis Vlachopapadopoulou
Lourdes Ibáñez
Martin Carlsson
Wayne Cutfield
Raoul Rooman
Roy Gomez
Michael P. Wajnrajch
Agnès Linglart
Renata Stawerska
Peter E. Clayton
Feyza Darendeliler
Anita C. S. Hokken-Koelega
Reiko Horikawa
Toshiaki Tanaka
Helmuth-Günther Dörr
Michel Polak
Adda Grimberg
A database study of the safety and effectiveness of daily growth hormone in treating more than 80,000 children with growth disorders worldwide: a plain language summary of publication
Therapeutic Advances in Endocrinology and Metabolism
title A database study of the safety and effectiveness of daily growth hormone in treating more than 80,000 children with growth disorders worldwide: a plain language summary of publication
title_full A database study of the safety and effectiveness of daily growth hormone in treating more than 80,000 children with growth disorders worldwide: a plain language summary of publication
title_fullStr A database study of the safety and effectiveness of daily growth hormone in treating more than 80,000 children with growth disorders worldwide: a plain language summary of publication
title_full_unstemmed A database study of the safety and effectiveness of daily growth hormone in treating more than 80,000 children with growth disorders worldwide: a plain language summary of publication
title_short A database study of the safety and effectiveness of daily growth hormone in treating more than 80,000 children with growth disorders worldwide: a plain language summary of publication
title_sort database study of the safety and effectiveness of daily growth hormone in treating more than 80 000 children with growth disorders worldwide a plain language summary of publication
url https://doi.org/10.1177/20420188251345556
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