MODERN APPROACHES TO THERAPY FOR CHILDREN WITH MUCOPOLYSACCHARIDOSIS

MODERN APPROACHES TO THERAPY FOR CHILDREN WITH MUCOPOLYSACCHARIDOSIS

Mucopolysaccharidosis is the group of hereditary metabolic disorders; it is characterized by accumulation of glycosaminoglycans owing to storage of specific lysosomal enzymes. Background: Research objective was to study the influence of enzyme replacement therapy on a somatic state and psychomotor d...

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Bibliographic Details
Main Authors:	N. V. Buchinskaya, I. А. Chikova, E. А. Isupova, О. V. Kalashnikova, М. М. Kostik, V. G. Chasnyk
Format:	Article
Language:	English
Published:	"Paediatrician" Publishers LLC 2014-05-01
Series:	Вопросы современной педиатрии
Subjects:	mucopolysaccharidosis enzyme replacement therapy implantable venous port systems
Online Access:	https://vsp.spr-journal.ru/jour/article/view/190
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