Managing Children with Gaucher Disease: Modern Clinical Recommendations

The focus of this article is Gaucher disease — a rare enough hereditary pathology. The authors present the most up-to-date epidemiological data and features of Gaucher disease etiopathogenesis. They offer clinical characteristics for the various types of this disease. The algorithm and crucial steps...

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Main Authors: A. A. Baranov, L. S. Namazova-Baranova, O. S. Gundobina, E. A. Lukina, A. K. Gevorkyan, K. V. Savostyanov, A. A. Pushkov, E. A. Vishnyova, G. B. Movsisyan
Format: Article
Language:Russian
Published: Union of pediatricians of Russia 2016-08-01
Series:Педиатрическая фармакология
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Online Access:https://www.pedpharma.ru/jour/article/view/1423
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author A. A. Baranov
L. S. Namazova-Baranova
O. S. Gundobina
E. A. Lukina
A. K. Gevorkyan
K. V. Savostyanov
A. A. Pushkov
E. A. Vishnyova
G. B. Movsisyan
author_facet A. A. Baranov
L. S. Namazova-Baranova
O. S. Gundobina
E. A. Lukina
A. K. Gevorkyan
K. V. Savostyanov
A. A. Pushkov
E. A. Vishnyova
G. B. Movsisyan
author_sort A. A. Baranov
collection DOAJ
description The focus of this article is Gaucher disease — a rare enough hereditary pathology. The authors present the most up-to-date epidemiological data and features of Gaucher disease etiopathogenesis. They offer clinical characteristics for the various types of this disease. The algorithm and crucial steps of differential diagnosis are described in detail. Also, the tactic and algorithms of enzymereplacing therapy (pathogenetic treatement of this hereditary enzymopathy) are carefully presented, together with the modern scheme of managing patients according to the corresponding health care delivery stages.
format Article
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institution Kabale University
issn 1727-5776
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language Russian
publishDate 2016-08-01
publisher Union of pediatricians of Russia
record_format Article
series Педиатрическая фармакология
spelling doaj-art-83d96af2192e4d659928b9f95e6ea4232025-08-20T03:39:29ZrusUnion of pediatricians of RussiaПедиатрическая фармакология1727-57762500-30892016-08-0113324425010.15690/pf.v13i3.15741408Managing Children with Gaucher Disease: Modern Clinical RecommendationsA. A. Baranov0L. S. Namazova-Baranova1O. S. Gundobina2E. A. Lukina3A. K. Gevorkyan4K. V. Savostyanov5A. A. Pushkov6E. A. Vishnyova7G. B. Movsisyan8Scientific Center of Children’s Health, Moscow, Russian Federation Sechenov First Moscow State Medical University, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian Federation Sechenov First Moscow State Medical University, Moscow, Russian Federation Pirogov Russian National Research Medical University, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian FederationHematology Scientific Center, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian Federation Sechenov First Moscow State Medical University, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian Federation Pirogov Russian National Research Medical University, Moscow, Russian FederationThe focus of this article is Gaucher disease — a rare enough hereditary pathology. The authors present the most up-to-date epidemiological data and features of Gaucher disease etiopathogenesis. They offer clinical characteristics for the various types of this disease. The algorithm and crucial steps of differential diagnosis are described in detail. Also, the tactic and algorithms of enzymereplacing therapy (pathogenetic treatement of this hereditary enzymopathy) are carefully presented, together with the modern scheme of managing patients according to the corresponding health care delivery stages.https://www.pedpharma.ru/jour/article/view/1423gaucher diseasestorage diseaseslipid metabolismetiologypathogenesisdifferential diagnosisclinical coursetreatmentenzyme-replacing therapychildren
spellingShingle A. A. Baranov
L. S. Namazova-Baranova
O. S. Gundobina
E. A. Lukina
A. K. Gevorkyan
K. V. Savostyanov
A. A. Pushkov
E. A. Vishnyova
G. B. Movsisyan
Managing Children with Gaucher Disease: Modern Clinical Recommendations
Педиатрическая фармакология
gaucher disease
storage diseases
lipid metabolism
etiology
pathogenesis
differential diagnosis
clinical course
treatment
enzyme-replacing therapy
children
title Managing Children with Gaucher Disease: Modern Clinical Recommendations
title_full Managing Children with Gaucher Disease: Modern Clinical Recommendations
title_fullStr Managing Children with Gaucher Disease: Modern Clinical Recommendations
title_full_unstemmed Managing Children with Gaucher Disease: Modern Clinical Recommendations
title_short Managing Children with Gaucher Disease: Modern Clinical Recommendations
title_sort managing children with gaucher disease modern clinical recommendations
topic gaucher disease
storage diseases
lipid metabolism
etiology
pathogenesis
differential diagnosis
clinical course
treatment
enzyme-replacing therapy
children
url https://www.pedpharma.ru/jour/article/view/1423
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