A phase 2 study of spartalizumab (PDR001) among patients with recurrent or metastatic esophageal squamous cell carcinoma (KCSG HN18-17, K-MASTER project 12)

Spartalizumab (PDR001) is a humanized IgG4 monoclonal antibody targeting programmed cell death protein 1 (PD-1). We conducted a single-arm, phase 2 trial to investigate the efficacy and safety of spartalizumab in patients with refractory esophageal squamous cell carcinoma (ESCC). Patients with histo...

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Main Authors: Dong Ki Lee, Sook Ryun Park, Yeul Hong Kim, Yun-Gyoo Lee, Su-Jin Shin, Beung-Chul Ahn, Sung Sook Lee, Sun Min Lim, Hye Ryun Kim, Byoung Chul Cho, Min Hee Hong
Format: Article
Language:English
Published: Taylor & Francis Group 2024-12-01
Series:OncoImmunology
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Online Access:https://www.tandfonline.com/doi/10.1080/2162402X.2024.2371563
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author Dong Ki Lee
Sook Ryun Park
Yeul Hong Kim
Yun-Gyoo Lee
Su-Jin Shin
Beung-Chul Ahn
Sung Sook Lee
Sun Min Lim
Hye Ryun Kim
Byoung Chul Cho
Min Hee Hong
author_facet Dong Ki Lee
Sook Ryun Park
Yeul Hong Kim
Yun-Gyoo Lee
Su-Jin Shin
Beung-Chul Ahn
Sung Sook Lee
Sun Min Lim
Hye Ryun Kim
Byoung Chul Cho
Min Hee Hong
author_sort Dong Ki Lee
collection DOAJ
description Spartalizumab (PDR001) is a humanized IgG4 monoclonal antibody targeting programmed cell death protein 1 (PD-1). We conducted a single-arm, phase 2 trial to investigate the efficacy and safety of spartalizumab in patients with refractory esophageal squamous cell carcinoma (ESCC). Patients with histologically confirmed ESCC who experienced disease progression after platinum-based chemotherapy received 300 mg of intravenous spartalizumab every three weeks until disease progression or occurrence of unacceptable toxicity. The primary endpoint was centrally assessed objective response according to the Response Evaluation Criteria in Solid Tumors, version 1.1. Adverse events were closely monitored throughout the study. From March 2020 through April 2021, 44 patients with ESCC were enrolled. Of the 44 patients, the objective response rate was 20.5% (95% confidence interval: 8.5–32.4). With a median follow-up of 10.9 months, median progression-free survival and overall survival were 3.2 months and 11.2 months, respectively. In addition, the median duration of response was 24.7 months. The most common grade 3 or 4 adverse event was grade 3 dysphagia (eight [18%] patients). Biomarker analyses explored programmed cell death ligand 1 and CD20 as potential predictive markers for PD-1 blockade. Spartalizumab showed promising activity with a manageable safety profile, indicating its potential as a new treatment option for patients with refractory ESCC.Trial registration The trial was registered at ClinicalTrials.gov under the identifier NCT03785496.
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spelling doaj-art-7b1070c787db4a9e95ccef4e558415732024-12-03T13:49:34ZengTaylor & Francis GroupOncoImmunology2162-402X2024-12-0113110.1080/2162402X.2024.2371563A phase 2 study of spartalizumab (PDR001) among patients with recurrent or metastatic esophageal squamous cell carcinoma (KCSG HN18-17, K-MASTER project 12)Dong Ki Lee0Sook Ryun Park1Yeul Hong Kim2Yun-Gyoo Lee3Su-Jin Shin4Beung-Chul Ahn5Sung Sook Lee6Sun Min Lim7Hye Ryun Kim8Byoung Chul Cho9Min Hee Hong10Department of Pharmacology, Yonsei University College of Medicine, Seoul, KoreaDepartment of Oncology, Asan Medical Center, University of Ulsan College of Medicine, Seoul, KoreaDivision of Medical Oncology, Department of Internal Medicine, Korea University College of Medicine, Seoul, KoreaDepartment of Internal Medicine, Kangbuk Samsung Hospital, Sungkyunkwan University School of Medicine, Seoul, KoreaDepartment of Pathology, Gangnam Severance Hospital, Yonsei University College of Medicine, Seoul, KoreaCenter for Lung Cancer, National Cancer Center, Goyang-si, South KoreaInje University Haeundae Paik Hospital, Inje University College of Medicine, Busan, South KoreaDivision of Medical Oncology, Department of Internal Medicine, Yonsei Cancer Center, Severance Hospital, Yonsei University College of Medicine, Seoul, KoreaDivision of Medical Oncology, Department of Internal Medicine, Yonsei Cancer Center, Severance Hospital, Yonsei University College of Medicine, Seoul, KoreaDivision of Medical Oncology, Department of Internal Medicine, Yonsei Cancer Center, Severance Hospital, Yonsei University College of Medicine, Seoul, KoreaDivision of Medical Oncology, Department of Internal Medicine, Yonsei Cancer Center, Severance Hospital, Yonsei University College of Medicine, Seoul, KoreaSpartalizumab (PDR001) is a humanized IgG4 monoclonal antibody targeting programmed cell death protein 1 (PD-1). We conducted a single-arm, phase 2 trial to investigate the efficacy and safety of spartalizumab in patients with refractory esophageal squamous cell carcinoma (ESCC). Patients with histologically confirmed ESCC who experienced disease progression after platinum-based chemotherapy received 300 mg of intravenous spartalizumab every three weeks until disease progression or occurrence of unacceptable toxicity. The primary endpoint was centrally assessed objective response according to the Response Evaluation Criteria in Solid Tumors, version 1.1. Adverse events were closely monitored throughout the study. From March 2020 through April 2021, 44 patients with ESCC were enrolled. Of the 44 patients, the objective response rate was 20.5% (95% confidence interval: 8.5–32.4). With a median follow-up of 10.9 months, median progression-free survival and overall survival were 3.2 months and 11.2 months, respectively. In addition, the median duration of response was 24.7 months. The most common grade 3 or 4 adverse event was grade 3 dysphagia (eight [18%] patients). Biomarker analyses explored programmed cell death ligand 1 and CD20 as potential predictive markers for PD-1 blockade. Spartalizumab showed promising activity with a manageable safety profile, indicating its potential as a new treatment option for patients with refractory ESCC.Trial registration The trial was registered at ClinicalTrials.gov under the identifier NCT03785496.https://www.tandfonline.com/doi/10.1080/2162402X.2024.2371563CD20-positive immune cellEsophageal squamous cell carcinomaimmune checkpoint inhibitorPD-L1 expressionspartalizumab
spellingShingle Dong Ki Lee
Sook Ryun Park
Yeul Hong Kim
Yun-Gyoo Lee
Su-Jin Shin
Beung-Chul Ahn
Sung Sook Lee
Sun Min Lim
Hye Ryun Kim
Byoung Chul Cho
Min Hee Hong
A phase 2 study of spartalizumab (PDR001) among patients with recurrent or metastatic esophageal squamous cell carcinoma (KCSG HN18-17, K-MASTER project 12)
OncoImmunology
CD20-positive immune cell
Esophageal squamous cell carcinoma
immune checkpoint inhibitor
PD-L1 expression
spartalizumab
title A phase 2 study of spartalizumab (PDR001) among patients with recurrent or metastatic esophageal squamous cell carcinoma (KCSG HN18-17, K-MASTER project 12)
title_full A phase 2 study of spartalizumab (PDR001) among patients with recurrent or metastatic esophageal squamous cell carcinoma (KCSG HN18-17, K-MASTER project 12)
title_fullStr A phase 2 study of spartalizumab (PDR001) among patients with recurrent or metastatic esophageal squamous cell carcinoma (KCSG HN18-17, K-MASTER project 12)
title_full_unstemmed A phase 2 study of spartalizumab (PDR001) among patients with recurrent or metastatic esophageal squamous cell carcinoma (KCSG HN18-17, K-MASTER project 12)
title_short A phase 2 study of spartalizumab (PDR001) among patients with recurrent or metastatic esophageal squamous cell carcinoma (KCSG HN18-17, K-MASTER project 12)
title_sort phase 2 study of spartalizumab pdr001 among patients with recurrent or metastatic esophageal squamous cell carcinoma kcsg hn18 17 k master project 12
topic CD20-positive immune cell
Esophageal squamous cell carcinoma
immune checkpoint inhibitor
PD-L1 expression
spartalizumab
url https://www.tandfonline.com/doi/10.1080/2162402X.2024.2371563
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