Modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacy

Abstract Hepatocellular carcinoma (HCC) is the third most common cause of cancer-related death worldwide. Treating HCC is challenging because of the poor drug effectiveness and the lack of tools to predict patient responses. To resolve these issues, we established a patient-centric spheroid model us...

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Main Authors: Sara Cherradi, Salomé Roux, Marie Dupuy, Séverine Tabone-Eglinger, Edouard Tuaillon, Marianne Ziol, Eric Assenat, Hong Tuan Duong
Format: Article
Language:English
Published: Nature Portfolio 2025-01-01
Series:Scientific Reports
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Online Access:https://doi.org/10.1038/s41598-024-84304-4
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author Sara Cherradi
Salomé Roux
Marie Dupuy
Séverine Tabone-Eglinger
Edouard Tuaillon
Marianne Ziol
Eric Assenat
Hong Tuan Duong
author_facet Sara Cherradi
Salomé Roux
Marie Dupuy
Séverine Tabone-Eglinger
Edouard Tuaillon
Marianne Ziol
Eric Assenat
Hong Tuan Duong
author_sort Sara Cherradi
collection DOAJ
description Abstract Hepatocellular carcinoma (HCC) is the third most common cause of cancer-related death worldwide. Treating HCC is challenging because of the poor drug effectiveness and the lack of tools to predict patient responses. To resolve these issues, we established a patient-centric spheroid model using HepG2, TWNT-1, and THP-1 co-culture, that mimics HCC phenotype. We developed a target-independent cell killing (TICK) exclusion strategy to monitor the therapeutic response. We demonstrated that our model reproduced the Barcelona Clinic Liver Cancer (BCLC) molecular classification, displayed known alterations of epigenetic players, and responded to tyrosine kinase inhibitors (TKIs) such as sorafenib, cabozantinib, and lenvatinib in a patient-dependent manner. Importantly, we reported for the first time that our model correctly predicted 34 clinical outcomes to TKIs out of 37 case studies on 32 HCC patients confirming that patient-centric spheroids, combined with our TICK exclusion strategy, are valuable models for drug discovery and opening a near perspective to personalized care.
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issn 2045-2322
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spelling doaj-art-7767c6e24ec94dcf9df7a92178bca3752025-08-20T02:36:34ZengNature PortfolioScientific Reports2045-23222025-01-0115111110.1038/s41598-024-84304-4Modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacySara Cherradi0Salomé Roux1Marie Dupuy2Séverine Tabone-Eglinger3Edouard Tuaillon4Marianne Ziol5Eric Assenat6Hong Tuan Duong7PredictCan Biotechnologies SAS, Biopôle EuromédecinePredictCan Biotechnologies SAS, Biopôle EuromédecineService d’Oncologie Médicale, Hôpital Saint Eloi, Centre Hospitalier Universitaire de MontpellierPlateforme de Gestion des Echantillons Biologiques, Centre Léon Bérard, Cancer Research Center of Lyon, Université de Lyon, Université Claude Bernard Lyon 1, INSERM 1052, CNRS 5286Centre de Ressources Biologiques (CRB), Centre Hospitalier Universitaire de MontpellierCentre de Ressources Biologiques du Groupe hospitalier Paris Seine Saint-DenisService d’Oncologie Médicale, Hôpital Saint Eloi, Centre Hospitalier Universitaire de MontpellierPredictCan Biotechnologies SAS, Biopôle EuromédecineAbstract Hepatocellular carcinoma (HCC) is the third most common cause of cancer-related death worldwide. Treating HCC is challenging because of the poor drug effectiveness and the lack of tools to predict patient responses. To resolve these issues, we established a patient-centric spheroid model using HepG2, TWNT-1, and THP-1 co-culture, that mimics HCC phenotype. We developed a target-independent cell killing (TICK) exclusion strategy to monitor the therapeutic response. We demonstrated that our model reproduced the Barcelona Clinic Liver Cancer (BCLC) molecular classification, displayed known alterations of epigenetic players, and responded to tyrosine kinase inhibitors (TKIs) such as sorafenib, cabozantinib, and lenvatinib in a patient-dependent manner. Importantly, we reported for the first time that our model correctly predicted 34 clinical outcomes to TKIs out of 37 case studies on 32 HCC patients confirming that patient-centric spheroids, combined with our TICK exclusion strategy, are valuable models for drug discovery and opening a near perspective to personalized care.https://doi.org/10.1038/s41598-024-84304-4Patient-centric spheroid modelHepatocellular carcinomaTargeted therapyTyrosine kinase inhibitorsPrediction of clinical outcomes
spellingShingle Sara Cherradi
Salomé Roux
Marie Dupuy
Séverine Tabone-Eglinger
Edouard Tuaillon
Marianne Ziol
Eric Assenat
Hong Tuan Duong
Modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacy
Scientific Reports
Patient-centric spheroid model
Hepatocellular carcinoma
Targeted therapy
Tyrosine kinase inhibitors
Prediction of clinical outcomes
title Modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacy
title_full Modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacy
title_fullStr Modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacy
title_full_unstemmed Modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacy
title_short Modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacy
title_sort modelling hepatocellular carcinoma microenvironment phenotype to evaluate drug efficacy
topic Patient-centric spheroid model
Hepatocellular carcinoma
Targeted therapy
Tyrosine kinase inhibitors
Prediction of clinical outcomes
url https://doi.org/10.1038/s41598-024-84304-4
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