Patients with rare diseases: from therapeutic orphans to pioneers of personalized treatments
Abstract Common diseases, such as cancer, diabetes mellitus, or Alzheimer's disease, affect a large segment of the population, which justifies the enormous financial allocations for translational and clinical research. In contrast, the ~5,000 known rare disorders affect only very few patients e...
Saved in:
| Main Authors: | Christoph Klein, William A Gahl |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
Springer Nature
2017-11-01
|
| Series: | EMBO Molecular Medicine |
| Online Access: | https://doi.org/10.15252/emmm.201708365 |
| Tags: |
Add Tag
No Tags, Be the first to tag this record!
|
Similar Items
-
Orphan diseases — rare but important!
by: article Editorial
Published: (2019-06-01) -
Pricing of orphan drugs in oncology and rare diseases
by: Mark Nuijten, et al.
Published: (2020-01-01) -
Drug Repurposing for Rare Orphan Diseases Using Machine Learning Techniques
by: Rajesh Manicavasaga, et al.
Published: (2022-05-01) -
Meeting abstracts from the 12th European Conference on Rare Diseases and Orphan Products
Published: (2024-12-01) -
Artificial intelligence in bioengineering: pioneering advances in medical robotics, imaging, and personalized therapeutics
by: Hang Su, et al.
Published: (2024-12-01)