Intravenous Pamidronate Therapy in Taiwanese Patients with Osteogenesis Imperfecta

Information on the long-term efficacy of intravenous pamidronate therapy in Asian patients with osteogenesis imperfecta (OI) is limited. We report our experience using pamidronate in Taiwanese patients with OI. Methods: Twenty-six patients with type I, III, or IV OI (eight males and 18 females; age...

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Main Authors: Hsiang-Yu Lin, Shuan-Pei Lin, Chih-Kuang Chuang, Ming-Ren Chen, Chia-Ying Chang
Format: Article
Language:English
Published: Elsevier 2008-10-01
Series:Pediatrics and Neonatology
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Online Access:http://www.sciencedirect.com/science/article/pii/S1875957209600024
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author Hsiang-Yu Lin
Shuan-Pei Lin
Chih-Kuang Chuang
Ming-Ren Chen
Chia-Ying Chang
author_facet Hsiang-Yu Lin
Shuan-Pei Lin
Chih-Kuang Chuang
Ming-Ren Chen
Chia-Ying Chang
author_sort Hsiang-Yu Lin
collection DOAJ
description Information on the long-term efficacy of intravenous pamidronate therapy in Asian patients with osteogenesis imperfecta (OI) is limited. We report our experience using pamidronate in Taiwanese patients with OI. Methods: Twenty-six patients with type I, III, or IV OI (eight males and 18 females; age range at last follow-up, 2.9-39.2 years) who received (or were currently receiving) intravenous pamidronate treatment (30 mg/m2/dose, every month) were retrospectively analyzed. Patients were followed for 1.0-7.3 years over the study period from February 2000 to October 2007. Results: The mean standard deviation score (SDS) for bone mineral density (BMD) had increased significantly from −4.72 to −3.37 (p < 0.005) after 1 year of treatment. In 16 patients evaluated after 4 years and eight after 6 years, the mean SDS continued to improve, to −2.69 (p < 0.001) and −1.54 (p < 0.005), respectively. The fracture rate decreased significantly (from 2.8 ± 1.1 to 0.6 ± 0.6, p < 0.001), and nine patients (35%) had no fractures while receiving treatment. The response to pamidronate was significantly better in patients with poorer initial BMD SDS (1 year: r = −0.71, p < 0.01; 4 years: r = −0.81, p < 0.01). Conclusion: This retrospective study suggests that Taiwanese patients with OI can benefit from pamidronate treatment, leading to a reduced incidence of fractures and increased BMD, especially in patients with poor baseline BMD.
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spelling doaj-art-72a5da9b7bec4fd48ffc789394ae30ea2025-08-20T03:49:04ZengElsevierPediatrics and Neonatology1875-95722008-10-0149516116510.1016/S1875-9572(09)60002-4Intravenous Pamidronate Therapy in Taiwanese Patients with Osteogenesis ImperfectaHsiang-Yu Lin0Shuan-Pei Lin1Chih-Kuang Chuang2Ming-Ren Chen3Chia-Ying Chang4Department of Pediatrics, Mackay Memorial Hospital, Taipei, TaiwanDepartment of Pediatrics, Mackay Memorial Hospital, Taipei, TaiwanDepartment of Medical Research, Mackay Memorial Hospital, Taipei, TaiwanDepartment of Pediatrics, Mackay Memorial Hospital, Taipei, TaiwanDepartment of Pediatrics, Mackay Memorial Hospital, Taipei, TaiwanInformation on the long-term efficacy of intravenous pamidronate therapy in Asian patients with osteogenesis imperfecta (OI) is limited. We report our experience using pamidronate in Taiwanese patients with OI. Methods: Twenty-six patients with type I, III, or IV OI (eight males and 18 females; age range at last follow-up, 2.9-39.2 years) who received (or were currently receiving) intravenous pamidronate treatment (30 mg/m2/dose, every month) were retrospectively analyzed. Patients were followed for 1.0-7.3 years over the study period from February 2000 to October 2007. Results: The mean standard deviation score (SDS) for bone mineral density (BMD) had increased significantly from −4.72 to −3.37 (p < 0.005) after 1 year of treatment. In 16 patients evaluated after 4 years and eight after 6 years, the mean SDS continued to improve, to −2.69 (p < 0.001) and −1.54 (p < 0.005), respectively. The fracture rate decreased significantly (from 2.8 ± 1.1 to 0.6 ± 0.6, p < 0.001), and nine patients (35%) had no fractures while receiving treatment. The response to pamidronate was significantly better in patients with poorer initial BMD SDS (1 year: r = −0.71, p < 0.01; 4 years: r = −0.81, p < 0.01). Conclusion: This retrospective study suggests that Taiwanese patients with OI can benefit from pamidronate treatment, leading to a reduced incidence of fractures and increased BMD, especially in patients with poor baseline BMD.http://www.sciencedirect.com/science/article/pii/S1875957209600024bisphosphonatesbone mineral densityfractureosteogenesis imperfectapamidronate
spellingShingle Hsiang-Yu Lin
Shuan-Pei Lin
Chih-Kuang Chuang
Ming-Ren Chen
Chia-Ying Chang
Intravenous Pamidronate Therapy in Taiwanese Patients with Osteogenesis Imperfecta
Pediatrics and Neonatology
bisphosphonates
bone mineral density
fracture
osteogenesis imperfecta
pamidronate
title Intravenous Pamidronate Therapy in Taiwanese Patients with Osteogenesis Imperfecta
title_full Intravenous Pamidronate Therapy in Taiwanese Patients with Osteogenesis Imperfecta
title_fullStr Intravenous Pamidronate Therapy in Taiwanese Patients with Osteogenesis Imperfecta
title_full_unstemmed Intravenous Pamidronate Therapy in Taiwanese Patients with Osteogenesis Imperfecta
title_short Intravenous Pamidronate Therapy in Taiwanese Patients with Osteogenesis Imperfecta
title_sort intravenous pamidronate therapy in taiwanese patients with osteogenesis imperfecta
topic bisphosphonates
bone mineral density
fracture
osteogenesis imperfecta
pamidronate
url http://www.sciencedirect.com/science/article/pii/S1875957209600024
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AT chihkuangchuang intravenouspamidronatetherapyintaiwanesepatientswithosteogenesisimperfecta
AT mingrenchen intravenouspamidronatetherapyintaiwanesepatientswithosteogenesisimperfecta
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