O36: Lentiviral gene therapy for Fabry disease in the Canadian FACTS trial: 5 year end of study results
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| Main Authors: | , , , , , , , , , , , |
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| Format: | Article |
| Language: | English |
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Elsevier
2025-01-01
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| Series: | Genetics in Medicine Open |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2949774425001517 |
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| _version_ | 1849711960637046784 |
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| author | Aneal Khan Dwayne Barber William McKillop Anthony Rupar Christiane Auray-Blais Graeme Fraser Daniel Fowler Alexandra Berger Ronan Foley Armand Keating Michael West Jeffrey Medin |
| author_facet | Aneal Khan Dwayne Barber William McKillop Anthony Rupar Christiane Auray-Blais Graeme Fraser Daniel Fowler Alexandra Berger Ronan Foley Armand Keating Michael West Jeffrey Medin |
| author_sort | Aneal Khan |
| collection | DOAJ |
| format | Article |
| id | doaj-art-7257db364edd4fe9bd1216b3c7dee5e1 |
| institution | DOAJ |
| issn | 2949-7744 |
| language | English |
| publishDate | 2025-01-01 |
| publisher | Elsevier |
| record_format | Article |
| series | Genetics in Medicine Open |
| spelling | doaj-art-7257db364edd4fe9bd1216b3c7dee5e12025-08-20T03:14:28ZengElsevierGenetics in Medicine Open2949-77442025-01-01310211210.1016/j.gimo.2025.102112O36: Lentiviral gene therapy for Fabry disease in the Canadian FACTS trial: 5 year end of study resultsAneal Khan0Dwayne Barber1William McKillop2Anthony Rupar3Christiane Auray-Blais4Graeme Fraser5Daniel Fowler6Alexandra Berger7Ronan Foley8Armand Keating9Michael West10Jeffrey Medin11M.A.G.I.C. Clinic (Metabolics and Genetics in Canada)Department of Laboratory Medicine and Pathobiology, University of TorontoDepartment of Pediatrics, Medical College of WisconsinDepartment of Pathology and Laboratory Medicine, Western UniversityDepartment of Pediatrics, Division of Medical Genetics, CIUSS de l’Estrie-CHUS Hospital FleurimontDepartment of Oncology, McMaster University and Juravinski Hospital and Cancer CentreRapa TherapeuticsPrincess Margaret Cancer Centre, University Health NetworkDepartment of Pathology and Molecular Medicine, McMaster University and Juravinski Hospital and Cancer CentreDepartment of Laboratory Medicine and Pathobiology, University of Toronto, Princess Margaret Cancer CentreDivision of Nephrology, Department of Medicine, Dalhousie UniversityDepartment of Biochemistry, Medical College of Wisconsinhttp://www.sciencedirect.com/science/article/pii/S2949774425001517 |
| spellingShingle | Aneal Khan Dwayne Barber William McKillop Anthony Rupar Christiane Auray-Blais Graeme Fraser Daniel Fowler Alexandra Berger Ronan Foley Armand Keating Michael West Jeffrey Medin O36: Lentiviral gene therapy for Fabry disease in the Canadian FACTS trial: 5 year end of study results Genetics in Medicine Open |
| title | O36: Lentiviral gene therapy for Fabry disease in the Canadian FACTS trial: 5 year end of study results |
| title_full | O36: Lentiviral gene therapy for Fabry disease in the Canadian FACTS trial: 5 year end of study results |
| title_fullStr | O36: Lentiviral gene therapy for Fabry disease in the Canadian FACTS trial: 5 year end of study results |
| title_full_unstemmed | O36: Lentiviral gene therapy for Fabry disease in the Canadian FACTS trial: 5 year end of study results |
| title_short | O36: Lentiviral gene therapy for Fabry disease in the Canadian FACTS trial: 5 year end of study results |
| title_sort | o36 lentiviral gene therapy for fabry disease in the canadian facts trial 5 year end of study results |
| url | http://www.sciencedirect.com/science/article/pii/S2949774425001517 |
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