Yeast NDI1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex I deficiency.

Mutations in subunits of the mitochondrial NADH dehydrogenase cause mitochondrial complex I deficiency, a group of severe neurological diseases that can result in death in infancy. The pathogenesis of complex I deficiency remain poorly understood, and as a result there are currently no available tre...

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Main Authors: Lucy Granat, Debbra Y Knorr, Daniel C Ranson, Emma L Hamer, Ram Prosad Chakrabarty, Francesca Mattedi, Laura Fort-Aznar, Frank Hirth, Sean T Sweeney, Alessio Vagnoni, Navdeep S Chandel, Joseph M Bateman
Format: Article
Language:English
Published: Public Library of Science (PLoS) 2023-07-01
Series:PLoS Genetics
Online Access:https://journals.plos.org/plosgenetics/article/file?id=10.1371/journal.pgen.1010793&type=printable
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author Lucy Granat
Debbra Y Knorr
Daniel C Ranson
Emma L Hamer
Ram Prosad Chakrabarty
Francesca Mattedi
Laura Fort-Aznar
Frank Hirth
Sean T Sweeney
Alessio Vagnoni
Navdeep S Chandel
Joseph M Bateman
author_facet Lucy Granat
Debbra Y Knorr
Daniel C Ranson
Emma L Hamer
Ram Prosad Chakrabarty
Francesca Mattedi
Laura Fort-Aznar
Frank Hirth
Sean T Sweeney
Alessio Vagnoni
Navdeep S Chandel
Joseph M Bateman
author_sort Lucy Granat
collection DOAJ
description Mutations in subunits of the mitochondrial NADH dehydrogenase cause mitochondrial complex I deficiency, a group of severe neurological diseases that can result in death in infancy. The pathogenesis of complex I deficiency remain poorly understood, and as a result there are currently no available treatments. To better understand the underlying mechanisms, we modelled complex I deficiency in Drosophila using knockdown of the mitochondrial complex I subunit ND-75 (NDUFS1) specifically in neurons. Neuronal complex I deficiency causes locomotor defects, seizures and reduced lifespan. At the cellular level, complex I deficiency does not affect ATP levels but leads to mitochondrial morphology defects, reduced endoplasmic reticulum-mitochondria contacts and activation of the endoplasmic reticulum unfolded protein response (UPR) in neurons. Multi-omic analysis shows that complex I deficiency dramatically perturbs mitochondrial metabolism in the brain. We find that expression of the yeast non-proton translocating NADH dehydrogenase NDI1, which reinstates mitochondrial NADH oxidation but not ATP production, restores levels of several key metabolites in the brain in complex I deficiency. Remarkably, NDI1 expression also reinstates endoplasmic reticulum-mitochondria contacts, prevents UPR activation and rescues the behavioural and lifespan phenotypes caused by complex I deficiency. Together, these data show that metabolic disruption due to loss of neuronal NADH dehydrogenase activity cause UPR activation and drive pathogenesis in complex I deficiency.
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issn 1553-7390
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language English
publishDate 2023-07-01
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record_format Article
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spelling doaj-art-720dde159eb94f2e9971e386d99fd3c02025-08-20T03:46:20ZengPublic Library of Science (PLoS)PLoS Genetics1553-73901553-74042023-07-01197e101079310.1371/journal.pgen.1010793Yeast NDI1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex I deficiency.Lucy GranatDebbra Y KnorrDaniel C RansonEmma L HamerRam Prosad ChakrabartyFrancesca MattediLaura Fort-AznarFrank HirthSean T SweeneyAlessio VagnoniNavdeep S ChandelJoseph M BatemanMutations in subunits of the mitochondrial NADH dehydrogenase cause mitochondrial complex I deficiency, a group of severe neurological diseases that can result in death in infancy. The pathogenesis of complex I deficiency remain poorly understood, and as a result there are currently no available treatments. To better understand the underlying mechanisms, we modelled complex I deficiency in Drosophila using knockdown of the mitochondrial complex I subunit ND-75 (NDUFS1) specifically in neurons. Neuronal complex I deficiency causes locomotor defects, seizures and reduced lifespan. At the cellular level, complex I deficiency does not affect ATP levels but leads to mitochondrial morphology defects, reduced endoplasmic reticulum-mitochondria contacts and activation of the endoplasmic reticulum unfolded protein response (UPR) in neurons. Multi-omic analysis shows that complex I deficiency dramatically perturbs mitochondrial metabolism in the brain. We find that expression of the yeast non-proton translocating NADH dehydrogenase NDI1, which reinstates mitochondrial NADH oxidation but not ATP production, restores levels of several key metabolites in the brain in complex I deficiency. Remarkably, NDI1 expression also reinstates endoplasmic reticulum-mitochondria contacts, prevents UPR activation and rescues the behavioural and lifespan phenotypes caused by complex I deficiency. Together, these data show that metabolic disruption due to loss of neuronal NADH dehydrogenase activity cause UPR activation and drive pathogenesis in complex I deficiency.https://journals.plos.org/plosgenetics/article/file?id=10.1371/journal.pgen.1010793&type=printable
spellingShingle Lucy Granat
Debbra Y Knorr
Daniel C Ranson
Emma L Hamer
Ram Prosad Chakrabarty
Francesca Mattedi
Laura Fort-Aznar
Frank Hirth
Sean T Sweeney
Alessio Vagnoni
Navdeep S Chandel
Joseph M Bateman
Yeast NDI1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex I deficiency.
PLoS Genetics
title Yeast NDI1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex I deficiency.
title_full Yeast NDI1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex I deficiency.
title_fullStr Yeast NDI1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex I deficiency.
title_full_unstemmed Yeast NDI1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex I deficiency.
title_short Yeast NDI1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex I deficiency.
title_sort yeast ndi1 reconfigures neuronal metabolism and prevents the unfolded protein response in mitochondrial complex i deficiency
url https://journals.plos.org/plosgenetics/article/file?id=10.1371/journal.pgen.1010793&type=printable
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