Selective activation of antioxidant resources and energy deficiency in Marinesco–Sjögren syndrome fibroblasts as an adaptive biological response to Sil1 loss

Abstract Marinesco–Sjögren syndrome (MSS) is a neuromuscular disease which presents with ataxia, muscle weakness and cataracts. This syndrome is typically caused by mutations in SIL1 gene, an ER co-chaperone that disrupts protein folding. Although it is known that accumulation of misfolded proteins...

Full description

Saved in:
Bibliographic Details
Main Authors: Valeria Panella, Francesca Potenza, Carla Tatone, Lorenza Speranza, Fernanda Amicarelli, Michele Sallese
Format: Article
Language:English
Published: Nature Portfolio 2025-04-01
Series:Scientific Reports
Subjects:
Online Access:https://doi.org/10.1038/s41598-025-96467-9
Tags: Add Tag
No Tags, Be the first to tag this record!